Multicenter cohort study for Investigating Dystophinopathy-associated CArdiovascuLar Failure in Japa
Not Applicable
Recruiting
- Conditions
- Muscular dystrophy
- Registration Number
- JPRN-UMIN000013738
- Lead Sponsor
- The University of Tokyo
- Brief Summary
Not available
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- Recruiting
- Sex
- All
- Target Recruitment
- 700
Inclusion Criteria
Not provided
Exclusion Criteria
Patients without definitive diagnosis. Patients' refusal to participate.
Study & Design
- Study Type
- Observational
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method Prevalence, death, heart failure, arrhythmia, thromboembolism, hospitalization, speckle tracking strain imaging, cardiac enzymes and markers.
- Secondary Outcome Measures
Name Time Method Renal failure, stroke, activities of daily life, quality of life.