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A open-label study of M071754 in patients with infantile spasms

Phase 4
Conditions
infantile spasms
Registration Number
JPRN-jRCT2080222508
Lead Sponsor
Alfresa Pharma Corporation
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Sex
All
Target Recruitment
Not specified
Inclusion Criteria

Patients diagnosed with infantile spasms and who meet one of the following criteria
- Patients who have completed the maintenance phase of the preceding phase III clinical study and have been confirmed efficacy and there is no safety concern
- Patients who is taking Vigabatrin (in which case the frequency of spasms before the start of Vigabatrin and the cumulative dose of Vigabatrin must be confirmed)
- Patients who has experience to take Vigabatrin (in which case the frequency of spasms before the start of Vigabatrin and the cumulative dose of Vigabatrin must be confirmed)
- Patients who has no experience to take Vigabatrin.

Exclusion Criteria

- Patients who is taking Vigabatrin more than maximum dose (150mg/kg/day or 3g/day)
- Patients with concurrent severe liver/renal disease, cardiac disease, serious gastrointestinal disorder.
- Patients who received adrenocorticotropic hormone (ACTH) products or steroids within 4 weeks (28 days) prior to the formal registration of this study.
- Patients who have concurrent or a history of ophthalmological complication in whom possible aggravation of the symptoms with vigabatrin.
- Patients with concomitant Lennox-Gastaut syndrome.

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Safety, efficacy, blood taurine<br>Safety:<br>- Ophthalmologic examination, vital sign, height/weight, Laboratory test, ECG, MRI (head), adverse events<br>Efficacy:<br>- Frequency of spasms, disappearance of spasms in the maintenance phase.<br>- Disappearance of hypsarrhythmia
Secondary Outcome Measures
NameTimeMethod
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