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Study to Assess Safety and Efficacy of Filgotinib, Lanraplenib and Tirabrutinib in Adults With Active Sjogren's Syndrome

Registration Number
NCT03100942
Lead Sponsor
Gilead Sciences
Brief Summary

The primary objective of this study is to assess the efficacy of filgotinib, lanraplenib, and tirabrutinib in adults with active Sjogren's Syndrome (SjS).

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
152
Inclusion Criteria
  • Diagnosed with primary or secondary SjS according to the 2002 American European Consensus Group (AECG) classification
  • Active SjS as defined by an European League Against Rheumatism (EULAR) Sjogren's syndrome disease activity index (ESSDAI) ≥ 5
  • Seropositivity for antibodies to SjS-associated antigens A and/or B (anti-SSA or anti-SSB)

Key

Exclusion Criteria
  • Concurrent treatment with any biologic disease modifying antirheumatic drug (bDMARD) (prior bDMARD treatment allowed with appropriate washout as per study protocol)

Note: Other protocol defined Inclusion/Exclusion criteria may apply.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
TirabrutinibTirabrutinibTirabrutinib + filgotinib placebo + lanraplenib placebo for up to 50.3 weeks.
LanraplenibTirabrutinib placeboLanraplenib + filgotinib placebo + tirabrutinib placebo for up to 49.4 weeks.
FilgotinibLanraplenib placeboFilgotinib + lanraplenib placebo + tirabrutinib placebo for up to 50.4 weeks.
Placebo, then active treatmentLanraplenib placeboFilgotinib placebo + lanraplenib placebo + tirabrutinib placebo for 24 weeks. Following completion of the Week 24 assessments and procedures, participants will be rerandomized 1:1:1, in a blinded fashion and receive either of the following study drugs through Week 48: * filgotinib + lanraplenib placebo + tirabrutinib placebo * lanraplenib + filgotinib placebo + tirabrutinib placebo * tirabrutinib + filgotinib placebo + lanraplenib placebo
Placebo, then active treatmentTirabrutinib placeboFilgotinib placebo + lanraplenib placebo + tirabrutinib placebo for 24 weeks. Following completion of the Week 24 assessments and procedures, participants will be rerandomized 1:1:1, in a blinded fashion and receive either of the following study drugs through Week 48: * filgotinib + lanraplenib placebo + tirabrutinib placebo * lanraplenib + filgotinib placebo + tirabrutinib placebo * tirabrutinib + filgotinib placebo + lanraplenib placebo
TirabrutinibLanraplenib placeboTirabrutinib + filgotinib placebo + lanraplenib placebo for up to 50.3 weeks.
TirabrutinibFilgotinib placeboTirabrutinib + filgotinib placebo + lanraplenib placebo for up to 50.3 weeks.
Placebo, then active treatmentFilgotinib placeboFilgotinib placebo + lanraplenib placebo + tirabrutinib placebo for 24 weeks. Following completion of the Week 24 assessments and procedures, participants will be rerandomized 1:1:1, in a blinded fashion and receive either of the following study drugs through Week 48: * filgotinib + lanraplenib placebo + tirabrutinib placebo * lanraplenib + filgotinib placebo + tirabrutinib placebo * tirabrutinib + filgotinib placebo + lanraplenib placebo
LanraplenibFilgotinib placeboLanraplenib + filgotinib placebo + tirabrutinib placebo for up to 49.4 weeks.
FilgotinibTirabrutinib placeboFilgotinib + lanraplenib placebo + tirabrutinib placebo for up to 50.4 weeks.
LanraplenibLanraplenibLanraplenib + filgotinib placebo + tirabrutinib placebo for up to 49.4 weeks.
FilgotinibFilgotinibFilgotinib + lanraplenib placebo + tirabrutinib placebo for up to 50.4 weeks.
Placebo, then active treatmentFilgotinibFilgotinib placebo + lanraplenib placebo + tirabrutinib placebo for 24 weeks. Following completion of the Week 24 assessments and procedures, participants will be rerandomized 1:1:1, in a blinded fashion and receive either of the following study drugs through Week 48: * filgotinib + lanraplenib placebo + tirabrutinib placebo * lanraplenib + filgotinib placebo + tirabrutinib placebo * tirabrutinib + filgotinib placebo + lanraplenib placebo
Placebo, then active treatmentTirabrutinibFilgotinib placebo + lanraplenib placebo + tirabrutinib placebo for 24 weeks. Following completion of the Week 24 assessments and procedures, participants will be rerandomized 1:1:1, in a blinded fashion and receive either of the following study drugs through Week 48: * filgotinib + lanraplenib placebo + tirabrutinib placebo * lanraplenib + filgotinib placebo + tirabrutinib placebo * tirabrutinib + filgotinib placebo + lanraplenib placebo
Placebo, then active treatmentLanraplenibFilgotinib placebo + lanraplenib placebo + tirabrutinib placebo for 24 weeks. Following completion of the Week 24 assessments and procedures, participants will be rerandomized 1:1:1, in a blinded fashion and receive either of the following study drugs through Week 48: * filgotinib + lanraplenib placebo + tirabrutinib placebo * lanraplenib + filgotinib placebo + tirabrutinib placebo * tirabrutinib + filgotinib placebo + lanraplenib placebo
Primary Outcome Measures
NameTimeMethod
Percentage of Participants Fulfilling Protocol-Specified Response Criteria at Week 12, as Compared to BaselineWeek 12

Response was defined as: Improvement ≥ 20% in ≥ 3 of 5 participant-reported Sjogren's syndrome (SjS) related visual analogue score (VAS) measures (participant's assessment of global disease, pain, oral dryness, ocular dryness and fatigue), with no increase defined as \> 30 mm from baseline (Day 1) in any of the above 5 VAS measures, AND either ≥ 20% improvement in high sensitivity C-reactive protein (hsCRP) (if hsCRP ≥ 1.5 x upper limit of normal \[ULN\] on Day 1) or no increase in hsCRP to ≥ 1.5 x ULN (if hsCRP \< 1.5 x ULN on Day 1).

Secondary Outcome Measures
NameTimeMethod
Change From Baseline in European League Against Rheumatism (EULAR) Sjogren's Syndrome Disease Activity Index (ESSDAI) at Week 12Baseline; Week 12

The ESSDAI is a physician-administered tool designed to measure disease activity. It consists of 12 organ-specific 'domains' contributing to disease activity associated with the participant's Sjogren's Syndrome only (constitutional, lymphadenopathy, articular, muscular, cutaneous, glandular, pulmonary, renal, peripheral nervous system, central nervous system, hematological, biological). Each domain is assessed for activity level (i.e., no, low, moderate, high) and assigned a numerical score based on pre-determined weighting of each individual domain. Overall score (ranges from 0 (no activity) to 123 (worst activity)) is calculated as sum of all individual weighted domain scores. A negative change from baseline value indicates improvement.

Change From Baseline in ESSPRI at Week 24Baseline; Week 24

The ESSPRI is a participant-reported questionnaire to assess subjective participant symptoms and includes 3 domains (dryness, pain, and fatigue). Each domain is scored on scale of 0-10 (0 = no symptom at all and 10 = worst symptom imaginable), and an overall score is calculated as the mean of the three individual domains where all domains carry the same weight. Minimum score can be 0 and maximum score can be 10. A negative change from baseline value indicates improvement.

Change From Baseline in EULAR Sjogren's Syndrome Patient Reported Index (ESSPRI) at Week 12Baseline; Week 12

The ESSPRI is a participant-reported questionnaire to assess subjective participant symptoms and includes 3 domains (dryness, pain, and fatigue). Each domain is scored on scale of 0-10 (0 = no symptom at all and 10 = worst symptom imaginable), and an overall score is calculated as the mean of the three individual domains where all domains carry the same weight. Minimum score can be 0 and maximum score can be 10. A negative change from baseline value indicates improvement.

Change From Baseline in ESSDAI at Week 24Baseline; Week 24

The ESSDAI is a physician-administered tool designed to measure disease activity. It consists of 12 organ-specific 'domains' contributing to disease activity associated with the participant's Sjogren's Syndrome only (constitutional, lymphadenopathy, articular, muscular, cutaneous, glandular, pulmonary, renal, peripheral nervous system, central nervous system, hematological, biological). Each domain is assessed for activity level (i.e., no, low, moderate, high) and assigned a numerical score based on pre-determined weighting of each individual domain. Overall score (ranges from 0 (no activity) to 123 (worst activity)) is calculated as sum of all individual weighted domain scores. A negative change from baseline value indicates improvement.

Trial Locations

Locations (52)

Clinical Research of West Florida, Inc.

🇺🇸

Clearwater, Florida, United States

Center for Rheumatology Immunology and Arthritis

🇺🇸

Fort Lauderdale, Florida, United States

IRIS Research and Development, LLC

🇺🇸

Plantation, Florida, United States

June DO, PC

🇺🇸

Lansing, Michigan, United States

North Mississippi Medical Clinics, Inc. - Clinical Research

🇺🇸

Tupelo, Mississippi, United States

Accurate Clinical Research Inc.

🇺🇸

Houston, Texas, United States

AARR Arizona Arthritis & Rheumatology Research

🇺🇸

Phoenix, Arizona, United States

Intermedius

🇵🇱

Kościan, Poland

Centrum Kliniczno-Badawcze

🇵🇱

Elbląg, Poland

Centrum Badan Klinicznych S.C

🇵🇱

Poznan, Poland

Physician Research Collaboration, LLC

🇺🇸

Lincoln, Nebraska, United States

ClinSearch

🇺🇸

Chattanooga, Tennessee, United States

Centrum Medyczne Amed Warszawa Targowek

🇵🇱

Warszawa, Poland

Ramesh C. Gupta, MD

🇺🇸

Memphis, Tennessee, United States

Denver Arthritis Clinic

🇺🇸

Denver, Colorado, United States

Inland Rheumatology Clinical Trials, Inc.

🇺🇸

Upland, California, United States

Omega Research Consultants LLC

🇺🇸

DeBary, Florida, United States

Medvin Clinical Research

🇺🇸

Covina, California, United States

Suncoast Clinical Research, Inc.

🇺🇸

New Port Richey, Florida, United States

North Georgia Rheumatology Group, PC

🇺🇸

Lawrenceville, Georgia, United States

Springfield Clinic

🇺🇸

Springfield, Illinois, United States

Center for Arthritis & Osteoporosis

🇺🇸

Elizabethtown, Kentucky, United States

Clayton Medical Associates

🇺🇸

Saint Louis, Missouri, United States

Albuquerque Clinical Trials

🇺🇸

Albuquerque, New Mexico, United States

Joint and Muscle Research Institute

🇺🇸

Charlotte, North Carolina, United States

Cape Fear Arthritis Care, PLLC

🇺🇸

Leland, North Carolina, United States

Clinical Research Center of Reading, LLC

🇺🇸

Wyomissing, Pennsylvania, United States

Altoona Center for Clinical Research

🇺🇸

Duncansville, Pennsylvania, United States

East Penn Rheumatology Associates, P.C.

🇺🇸

Bethlehem, Pennsylvania, United States

Diagnostic Group Integrated Healthcare System, Pllc

🇺🇸

Beaumont, Texas, United States

Trinity Universal Research Associates

🇺🇸

Plano, Texas, United States

Southwest Rheumatology Research

🇺🇸

Mesquite, Texas, United States

Arthritis Northwest

🇺🇸

Spokane, Washington, United States

Wasatch Peak Family Practice

🇺🇸

Layton, Utah, United States

Arthritis & Osteoporosis Clinic

🇺🇸

Waco, Texas, United States

The Center for Arthritis and Rheumatic Diseases, PC

🇺🇸

Chesapeake, Virginia, United States

Ai Centrum Medyczne

🇵🇱

Poznan, Poland

Centrum Medyczne Oporow

🇵🇱

Wroclaw, Poland

Hospital de la Santa Creu i Sant Pau

🇪🇸

Barcelona, Spain

Hospital General Universitario De Elche

🇪🇸

Elche, Spain

Hospital Universitario de Fuenlabrada

🇪🇸

Fuenlabrada, Spain

Hospital Regional Universitario de Malaga

🇪🇸

Málaga, Spain

Corporacio Sanitaria Parc Taulí de Sabadell

🇪🇸

Sabadell, Spain

Hospital Clinico Universitario de Salamanca

🇪🇸

San Vicente, Spain

Hospital De Merida

🇪🇸

Mérida, Spain

Hospital Quironsalud Infanta Luisa

🇪🇸

Sevilla, Spain

Western General Hospital

🇬🇧

Edinburgh, United Kingdom

Doncaster Royal Infirmary

🇬🇧

Doncaster, United Kingdom

Princess Alexandra Hospital

🇬🇧

Harlow, United Kingdom

Great Western Hospital

🇬🇧

Swindon, United Kingdom

Warrington Hospital

🇬🇧

Warrington, United Kingdom

PMG Research of Salisbury

🇺🇸

Salisbury, North Carolina, United States

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