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Clinical Trials/NL-OMON32439
NL-OMON32439
Completed
Phase 3

A PHASE III TRIAL OF ALD-101 ADUVANT THERAPY of UNRELATED UMBILICAL CORD BLOOD TRANSPLANTATION (UCBT) IN PATIENTS WITH INBORN ERRORS OF METABOLISM - UCBT-002

Aldagen, Inc.0 sites12 target enrollmentTBD

Overview

Phase
Phase 3
Intervention
Not specified
Conditions
Not specified
Sponsor
Aldagen, Inc.
Enrollment
12
Status
Completed
Last Updated
last year

Overview

Brief Summary

No summary available.

Registry
who.int
Start Date
TBD
End Date
TBD
Last Updated
last year
Study Type
Interventional

Investigators

Eligibility Criteria

Inclusion Criteria

  • Patients must have a confirmed diagnosis of inborn error of metabolism. Diagnosis to be confirmed by two appropriate tests (enzyme or mutation analysis) before study entry.
  • Patients must be \< 16 years of age at the time of study enrollment.
  • Patients must be \>\= 5 kg in weight.
  • Patients must have a good performance status (Lansky \>\= 80%).
  • Patients must have adequate function of other organ systems.
  • Patients must have a minimum life expectancy of at least 6 months.
  • Patient must be determined to be a good candidate for a standard UCBT according to the investigator and standard eligibility work\-up at the site.

Exclusion Criteria

  • Patients that are HIV, Hepatitis B and/or Hepatitis C positive.
  • Patients that are concurrently involved in any other clinical study that affects engraftment or immune reconstitution (e.g., other hematopoietic growth factors).
  • Patients with uncontrolled infections.
  • Patients with prior allogeneic stem cell transplant with cytoreduction preparative therapy within 12 months of enrollment.

Outcomes

Primary Outcomes

Not specified

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