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Pharmacogenetic sub-study within the research project „Structure Optimization for Children with Cancer after Therapy with Anthracyclines (LESS-Anthra)

Conditions
MedDRA - 10048610: Cardiotoxicity
C74
C64
Malignant neoplasm of adrenal gland
Malignant neoplasm of kidney, except renal pelvis
Registration Number
DRKS00015084
Lead Sponsor
Studienleiter des Late Effects Surveillance System (LESS)Klinik für Kinder- und Jugendmedizin, Universitätsklinikum Schleswig-Holstein, Campus Lübeck
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Enrolling by invitation
Sex
All
Target Recruitment
450
Inclusion Criteria

Patients are invited to participate if they: (a) were diagnosed with nephroblastoma or neuroblastoma between January 1990 and December 2012, (b) had the diagnosis before the age of 18, (c) were treated with anthracyclines, and (d) had participated in one of the nephroblastoma trials SIOP 9/GPOH, SIOP 93-01/GPOH, or SIOP 2001/GPOH or neuroblastoma trials NB 90, NB 97, or NB 2004.

Exclusion Criteria

Non-consent

Study & Design

Study Type
observational
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Comparison of high vs. moderate and low genetic risk of anthracycline-associated cardiotoxicity (according to RARG rs2229774, UGT1A6 rs17863783and SLC28A3 rs7853758 genotypes) with the incidence of anthracycline-associated cardiomyopathy, as confirmed by echocardiography. Echocardiography is performed as part of routine follow-up examinations within 12 months from inclusion of the patient.
Secondary Outcome Measures
NameTimeMethod
Comparison of the pharmacogenetic profile (candidate genes and genome-wide) between patients without and patients with anthracycline-associated cardiotoxicity, as confirmed by echocardiography. Echocardiography is performed as part of routine follow-up examinations within 12 months from inclusion of the patient.
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