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Clinical Trials/EUCTR2020-000067-23-FR
EUCTR2020-000067-23-FR
Active, not recruiting
Phase 1

First in Human Study to evaluate the safety, tolerability, pharmacokinetics, pharmacodynamics and preliminary efficacy of PPSGG in anti-MAG neuropathy patients

Polyneuron Pharmaceuticals AG0 sites48 target enrollmentMarch 13, 2020

Overview

Phase
Phase 1
Intervention
Not specified
Conditions
Not specified
Sponsor
Polyneuron Pharmaceuticals AG
Enrollment
48
Status
Active, not recruiting
Last Updated
5 years ago

Overview

Brief Summary

No summary available.

Registry
who.int
Start Date
March 13, 2020
End Date
TBD
Last Updated
5 years ago
Study Type
Interventional clinical trial of medicinal product
Sex
All

Investigators

Eligibility Criteria

Inclusion Criteria

  • Age between 18 and 80 years, male and female.
  • Patient with a confirmed diagnosis of monoclonal IgM associated with MGUS with anti\-MAG activity (titer of \> 10’000 BTU) and demyelinating neuropathy defined by electrophysiological criteria according to EFNS/PNS PDN guideline, 2010\.
  • Clear clinical signs of disability: with at least ONLS \= 2 in lower extremities.
  • Inflammatory Neuropathy Cause and Treatment (INCAT) sensory sum score \=2\.
  • Adequate hepatic and renal function
  • Are the trial subjects under 18? no
  • Number of subjects for this age range:
  • F.1\.2 Adults (18\-64 years) yes
  • F.1\.2\.1 Number of subjects for this age range 10
  • F.1\.3 Elderly (\>\=65 years) yes

Exclusion Criteria

  • Patients with total serum IgM levels \>30 g.
  • Hematological malignancy, prior malignancy of any organ system (except BCC)
  • Prior immunosuppression: No IVIG in previous 3 months, no previous cyclophosphamide or biologicals in prior 6/12\.
  • Other neurological, neuromuscular, rheumatologic or orthopedic condition with significant impact on the capabilities of walk preventing evaluation of neurological scores

Outcomes

Primary Outcomes

Not specified

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