MedPath

Prospecive study for treatment of acute promyelocytic leukemia (APL) with all-trans retinoic acid (ATRA) and chemotherapy

Phase 3
Conditions
C92.4
Acute promyelocytic leukaemia [PML]
Registration Number
DRKS00004314
Lead Sponsor
niversitätsklinikum Münster
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Complete
Sex
All
Target Recruitment
189
Inclusion Criteria

Newly diagnosed APL, cytogenetically or molecularly confirmed, age over 16 years, written informed consent

Exclusion Criteria

Cardiac failure NYHA III und IV, chronic pumonary diasease with hypoxemia, severe treatment refractory hypertension, renal failure, if not explained by leukemia
(serum creatinine 2 mg/ 100 ml or more), severe chronic liver disease, uncontrolled pneumonia with hypoxemia, uncontrolled sepsis, uncontrolled life-threatening bleeding, psycatric disorder, frailty befor onset of leukemia, cachexia, pregnancy, secondary malignancy.

Study & Design

Study Type
interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Assessment of the effectiveness of the therapy<br>Main parameters:<br>Rate of complete remission<br>Overall survival at 6 years<br>Relapse free survival at 6 years<br>Event free survival at 6 years. <br>
Secondary Outcome Measures
NameTimeMethod
Rate of early death<br>Toxicity (in particular rate of infections WHO grade =3)<br>Monitoring of minimal residual disease by RT-PCR)<br>
© Copyright 2025. All Rights Reserved by MedPath