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Swiss Rare Disease Registry (SRDR)

Recruiting
Conditions
Rare Diseases
Registration Number
NCT05179863
Lead Sponsor
University of Bern
Brief Summary

The SRDR is a national registry that records rare diseases in people of any age who live in Switzerland. It serves as a platform for scientists, health professionals, affected people, and politicians.The SRDR aims to collect epidemiological data on rare diseases, and data on changes to the diagnosis over time. The SRDR will further serve as a research platform and facilitate patient participation in national and international studies. The SRDR will promote harmonization of data and method between the numerous existing disease-specific registries in Switzerland, will strengthen the exchange with international rare disease registries for research and policy, and will build a network for communication for patients and health care providers.

Detailed Description

Background: In Europe a disease is considered rare when fewer than one in 2'000 people are affected. Today, more than 7'000 rare diseases are known. Although scarce, rare diseases all together affect approximately 5-8% of the people around the world. In Switzerland, more than 500'000 people live with a rare disease. Clinical and epidemiological studies on rare diseases in Switzerland are lacking. Little is known about diagnostics, efficient treatment, and the course of rare diseases.

The cantonal Ethics Committee of Bern approved the SRDR project (project ID: 2017-02313, observational study, risk category A).

Objectives: The overall goal of the SRDR is to improve the care situation of people living with a rare disease in Switzerland. The development of a national registry to collect representative and complete data from children and adults with a rare disease in Switzerland helps to achieve this overall goal.

Primary objectives of the SRDR project:

1. Collect epidemiological data on rare diseases from all patients with rare diseases in Switzerland (incidence, prevalence, survival, mortality).

2. Collect data on quality of health care and outcomes (diagnosis, management, outcomes, quality indicators, treating institutions).

3. Setup a research platform for clinical, epidemiological, basic, and translational research on all rare diseases.

4. Facilitate patients to participate in national and international studies.

5. Promote harmonisation of data and methods between the numerous existing disease-specific registries in Switzerland.

6. Strengthen exchange with international rare disease registries for research and policy.

7. Build a network for communication, for patients and health care providers.

Procedure: After a person has been diagnosed with a rare disease, the medical staff inform the patient and/or the legal representative orally about the SRDR and its purpose during regular consultation. The medical staff will hand over the written age-appropriate patient information and the informed consent form. Patient organizations and the staff from the SRDR also have the possibility to inform people about the SRDR. Further, patients have the possibility to use a secure web-based application for self-notification.

The patient or/and the legal representative have 6 weeks to give or refuse the informed consent. Patients who wish to participate sign the consent form and are then registered in the SRDR. If a patient or/and legal representative do neither refuse registration nor sign informed consent within 6 weeks, the data will be registered. If a patient does not wish to participate, only a minimal anonymous data set is recorded.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
500000
Inclusion Criteria
  • Diagnosed with a rare disease
  • High suspicion of a rare disease
  • Treated or living in Switzerland
  • Signed informed consent
Read More
Exclusion Criteria
  • None
Read More

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Personal DataAt diagnosis (age 0-99 years)

Registering patients personal data

DiagnosisAt diagnosis (age 0-99 years)

Orpha Code of the diagnosed rare disease

Date of DiagnosisAt diagnosis (age 0-99 years)

Date on which the diagnosis was made

Disease HistoryAt registration (age 0-99 years)

History of first occurrence of symptoms

Diagnostic MethodAt diagnosis (age 0-99 years)

Diagnostic method that was decisive for the diagnosis

Molecular genetic informationAt diagnosis (age 0-99 years)

Name of affected genes and mutations

Other RegistriesAt registration (age 0-99 years)

Name of other national or international registries the patient is registered

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (20)

Ostschweizer Kinderspital

🇨🇭

St.Gallen, Switzerland

Ostschweizer Zentrum für seltene Krankheiten

🇨🇭

St.Gallen, Switzerland

Center for Rare Diseases, Zurich

🇨🇭

Zurich, Switzerland

Universitätsspital Zürich, USZ

🇨🇭

Zurich, Switzerland

Center for Rare Diseases, Basel

🇨🇭

Basel, Switzerland

Center for Rare Diseases, Inselspital

🇨🇭

Bern, Switzerland

Centro Malattie Rare della Svizzera Italiana

🇨🇭

Bellinzona, Switzerland

Kantonsspital Aarau

🇨🇭

Aarau, Switzerland

Hôpitaux universitaires de Genève, HUG

🇨🇭

Geneva, Switzerland

Kantonsspital Aarau, Pädiatrie

🇨🇭

Aarau, Switzerland

Universitäs-Kinderspital beider Basel, UKBB

🇨🇭

Basel, Switzerland

Universitätsspital Basel, USB

🇨🇭

Basel, Switzerland

University of Bern, Inselspital Bern

🇨🇭

Bern, Switzerland

Center for Rare Diseases, Geneva

🇨🇭

Geneva, Switzerland

Kantonsspital St. Gallen

🇨🇭

St. Gallen, Switzerland

Ostschweizer Zentrum für seltene Krankheiten, Pädiatrie

🇨🇭

St. Gallen, Switzerland

Universitäts-Kinderspital Zürich, Kispi

🇨🇭

Zurich, Switzerland

Universitätsklinik Balgrist

🇨🇭

Zurich, Switzerland

Center for Rare Diseases, Lausanne

🇨🇭

Lausanne, Switzerland

Centre hospitalier universitaire vaudois, CHUV

🇨🇭

Lausanne, Switzerland

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