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Assessment of Patterns of Patient Reported Outcomes in Adults With Congenital Heart Disease - International Study II

Completed
Conditions
Congenital Heart Disease
Interventions
Other: This is an observational study, there is no intervention
Registration Number
NCT04902768
Lead Sponsor
KU Leuven
Brief Summary

This is an international, cross-sectional and descriptive study that aims to investigate differences in patient-reported outcome measures (PROMs) and patient-reported experience measures (PREMs) and that aims to explore the profile and healthcare needs of adults with congenital heart diseases.

Detailed Description

The research aims of this study are:

1. To further explore differences in a modified selection of patient-reported outcome measures (PROMs) and (as a new addition in APPROACH-IS II) explore differences in patient-reported experience measures (PREMs), by enrolling adults with congenital heart diseases in low, middle, and high income countries and including new potential explanatory variables ("Part 1").

2. To explore the profile and healthcare needs of a subgroup of older adults with congenital heart disease, with a particular focus on investigating the frailty phenotype ("Part 2").

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
8415
Inclusion Criteria
  • Diagnosed with congenital heart disease, defined as: "a gross structural abnormality of the heart and/or intra-thoracic great vessels that is actually or potentially of functional significance (including mild, moderate, and complex heart defects)"
  • Aged 18 years of age or older at the moment of study inclusion
  • Diagnosed with congenital heart disease before the age of 10 years
  • Follow-up at an ACHD center or included in a national/regional registry
  • Physical, cognitive, and language abilities to complete self-report questionnaires
Exclusion Criteria
  • Prior heart transplantation

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
Adults with congenital heart diseaseThis is an observational study, there is no intervention-
Primary Outcome Measures
NameTimeMethod
Patient-reported health statusBaseline

This outcome is measured using the Linear Analogue Scale Health Status (LAS HS). Scores range from 0 (worst imaginable health state) to 100 (best imaginable health state).

Patients' perception of providers' autonomy supportBaseline

This outcome is measured using the modified Health Care Climate Questionnaire (mHCCQ). Each of the 6 items is scored from 1 to 7. Scores are calculated by averaging the individual item scores. Higher average score represents a higher level of perceived autonomy support.

Patient-reported quality of lifeBaseline

This outcome is measured using the Linear Analog Scale on Quality of Life (LAS QOL). Scores range from 0 (worst imaginable quality of life) to 100 (best imaginable quality of life).

Cognitive functioningBaseline

This outcome is measured using the Montreal Cognitive Assessment Screener (MoCA). Scores range from 0 to 30. Scores of \<26 indicate cognitive dysfunction.

Patient-reported depressive symptomsBaseline

This outcomes is measured using the Patient Health Questionnaire 8. Scores range from 0 to 24. Scores of ≥10 indicate depression.

Patient-reported anxiety symptomsBaseline

This outcome is measured using the General Anxiety Disorder 7. Scores range from 0 to 21. Scores of 5, 10, and 15 are taken as cut-off points for mild, moderate and severe anxiety.

Frailty phenotypeBaseline

This outcome is classified using the Fried method (i.e., non-frail (no positive criterion), pre-frail (1 or 2 criteria positive), or frail (when ≥3 criteria are positive).

Secondary Outcome Measures
NameTimeMethod
Patient-reported empowermentBaseline

This outcome is measured using the Gothenburg Empowerment Scale (GES generic v1.1). Scores range from 15 to 75. Higher score reflects a higher level of empowerment.

Patient-reported social supportBaseline

This outcomes is measured using the Multidimensional Scale on Perceived Social Support Scale (MSPSS). Scores range from 12 to 84. Higher score indicates greater social support perceived by an individual.

Advance care planningBaseline

This outcome is measured using a survey developed for APPROACH-IS II by the Steering Committee, based on previous research. A sample question is 'Have you personally written down information about the care you would want in case you become seriously ill in the future?'.

Patient-reported stigmaBaseline

This outcome is measured using the Chronic Illness Stigma Scale (CISS). Scores range from 8 to 40. Higher scores indicating higher levels of perceived stigma.

Patient-reported illness identityBaseline

This outcome is measured using the Illness Identity Questionnaire (IIQ). The questionnaire consists of a five-item rejection scale, seven-item enrichment scale, five-item acceptance scale and eight-item engulfment scale. A mean score is calculated per subscale. Higher scores indicate more rejection, enrichment, acceptance or engulfment.

Patient-reported parental involvementBaseline

This outcome is measured using an adapted version of the subscale on parents of the Multidimensional Scale on Perceived Social Support. Scores range from 5 to 35. Higher score indicates greater parental support in childhood and adolescence.

Patient-reported social media to connect with peersBaseline

This outcome is measured using a survey developed for APPROACH-IS II by the Steering Committee, based on previous research. A sample question is 'How would you describe your experiences connecting with other people with CHD through social media?'.

Medical variables by chart review (eg. diagnosis, cardiac surgeries)Baseline

This outcome is classified according to the adult congenital heart disease anatomic and physiological (ACHD AP) classification system of Stout and colleagues.

Patient-reported healthcare utilizationBaseline

This outcomes was measured using the Patient-Reported Inpatient and outpatient Utilization Survey (PRIUS). Higher numbers indicate more healthcare use.

Patient-reported functional statusBaseline

This outcome is classified according to the New York Heart Association (NYHA).

Presence and burden of comorbiditiesBaseline

This outcome is measured using the Charlson Comorbidity Index.

Patient-reported socio-demographic variables (eg. age, educational level)Baseline

Self-reported

Trial Locations

Locations (53)

Nationwide Children's Hospital

🇺🇸

Columbus, Ohio, United States

University of California

🇺🇸

San Francisco, California, United States

Boston Children's / Brigham and Women's

🇺🇸

Boston, Massachusetts, United States

Oregon Health and Science University

🇺🇸

Portland, Oregon, United States

Umea University Hospital

🇸🇪

Umeå, Sweden

Ege University Health Application and Research Center, Cardiology Department

🇹🇷

Bornova, Turkey

Royal Brompton Hospital, Royal Brompton & Harefield Hospitals, Guy's and St Thomas' NHS Foundation Trust

🇬🇧

London, United Kingdom

Centrum voor Congenital Hartafwijkingen

🇳🇱

Groningen, Netherlands

Policlinico San Donato (IRCCS)

🇮🇹

Milan, Italy

Samsung Medical Center

🇰🇷

Seoul, Korea, Republic of

Chiba Cerebral and Cardiovascular Center

🇯🇵

Chiba, Japan

Skånes Universitetssjukhus

🇸🇪

Lund, Sweden

University Hospital Bern

🇨🇭

Bern, Switzerland

Sahlgrenska University Hospital

🇸🇪

Gothenburg, Sweden

Uppsala University Hospital

🇸🇪

Uppsala, Sweden

Freeman Hospital, Newcastle Upon Tyne Hospitals NHS Foundation Trust

🇬🇧

Newcastle, United Kingdom

Mount Sinai Heart

🇺🇸

New York, New York, United States

Lucile Packard Children's Hospital and Stanford Health Care

🇺🇸

Stanford, California, United States

University of Florida Health

🇺🇸

Gainesville, Florida, United States

Taussig Heart Center of Johns Hopkins Hospital

🇺🇸

Baltimore, Maryland, United States

Philadelphia Penn Medicine

🇺🇸

Philadelphia, Pennsylvania, United States

University of Southwestern Medical Center

🇺🇸

Dallas, Texas, United States

Melbourne Children's Cardiology

🇦🇺

Melbourne, Australia

Hospital de Niños

🇦🇷

Córdoba, Argentina

Hospital San Juan De Dios De La Plata

🇦🇷

Buenos Aires, Argentina

Vienna General Hospital

🇦🇹

Vienna, Austria

Ghent University Hospital

🇧🇪

Ghent, Belgium

Hospital das Clinicas da Faculdade de Medicina de Ribeirão Preto

🇧🇷

Ribeirão Preto, Brazil

National Heart Hospital

🇧🇬

Sofia, Bulgaria

Montreal Heart Institute, Université de Montréal

🇨🇦

Montréal, Canada

Copenhagen University Hospital

🇩🇰

Copenhagen, Denmark

Mazankowski Alberta Heart Institute

🇨🇦

Edmonton, Canada

Hôpital cardiologique Haut-Leveque

🇫🇷

Bordeaux, France

Montpellier University Hospital

🇫🇷

Montpellier, France

Hôpital Européen Georges Pompidou

🇫🇷

Paris, France

Karolinska Universitetssjukhuset

🇸🇪

Stockholm, Sweden

Centre Hospitalier Régional de Thiès

🇸🇳

Thiès, Senegal

National Taiwan University Hospital

🇨🇳

Taipei City, Taiwan

Meintegral Clinic

🇨🇴

Manizales, Colombia

College of Health sciences, Addis Ababa University

🇪🇹

Addis Ababa, Ethiopia

Amrita Institute of Medical Sciences

🇮🇳

Kochi, India

Paediatric & Congenital Heart Centre, IJN (National Heart Institute)

🇲🇾

Kuala Lumpur, Malaysia

Mater Dei Hospital

🇲🇹

Imsida, Malta

Hôpitaux Universitaires de Genève

🇨🇭

Genève, Switzerland

University Hospitals Leuven

🇧🇪

Leuven, Belgium

Reference Center of Congenital Heart Disease , University Hospital Center of São João

🇵🇹

Porto, Portugal

Clinique Medical Le Jourdain

🇨🇲

Yaoundé, Cameroon

AHEPA University Hospital

🇬🇷

Thessaloníki, Greece

Centre Hospitalier universitaire vaudois

🇨🇭

Lausanne, Switzerland

Princess Marina Hospital

🇧🇼

Gaborone, Botswana

Intituto Nacional Del Torax

🇨🇱

Santiago, Chile

Oslo University Hospital, Rikshospitalet

🇳🇴

Oslo, Norway

Aga Khan University Hospital

🇵🇰

Karachi, Pakistan

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