MedPath

Study to Evaluate Eflornithine + Lomustine vs Lomustine in Recurrent Anaplastic Astrocytoma (AA) Patients

Phase 3
Conditions
Anaplastic Astrocytoma
Recurrent Anaplastic Astrocytoma
Interventions
Registration Number
NCT02796261
Lead Sponsor
Orbus Therapeutics, Inc.
Brief Summary

The purpose of this study is to compare the efficacy and safety of eflornithine in combination with lomustine, compared to lomustine taken alone, in treating patients whose anaplastic astrocytoma has recurred/progressed after radiation and temozolomide chemotherapy.

Detailed Description

This study will consist of 4 study periods of up to 50 months in total, consisting of:

Screening Period - A maximum screening duration of 4 weeks.

Treatment Period - Treatment Arm A up to 24 months; Treatment Arm B up to 12 months.

End of Treatment Visit - A minimum of 4 weeks post last treatment for both arms.

Follow-Up Period - Up to approximately 36 months, or until patient death.

A total of approximately 340 patients will be randomized in a 1:1 ratio to receive either eflornithine + lomustine or lomustine alone.

Recruitment & Eligibility

Status
UNKNOWN
Sex
All
Target Recruitment
343
Inclusion Criteria

Patients must meet all of the following inclusion criteria to be eligible for participation in this study:

  • Surgical or biopsy-proven diagnosis of WHO grade 3 AA.

  • First AA tumor progression or recurrence ≤ 6 months prior to randomization based on MRI using T2 hyperintesity, gadolinium (Gd)-contrast enhancement, or both. To avoid enrollment of patients with glioblastoma, patients with Gd-contrast enhancing tumors will be eligible if there is no necrosis seen on MRI and any of the following criteria is true:

    1. Gd-contrast lesion margins are not clearly defined,
    2. Gd-contrast lesions are only measurable in one dimension,
    3. Gd-contrast lesion has two perpendicular diameters less than 10 mm,
    4. Gd-contrast lesion has two perpendicular diameters greater than 10 mm but less than 20 mm and lesion does not demonstrate central necrosis,
    5. Recent histopathological confirmation of WHO grade 3 AA
  • Received EBRT and temozolomide chemotherapy prior to first tumor progression or recurrence of WHO Grade 3 AA.

  • Completion of EBRT ≥ 6 months prior to randomization.

  • A patient whose AA tumor has progressed or recurred and has had another surgical resection prior to randomization will be eligible if a) pathology review confirms AA, and b) post-surgical MRI demonstrates measurable tumor on T2 FLAIR.

  • Karnofsky Performance Status (KPS) score of ≥ 70.

Exclusion Criteria

Patients who meet any of the following exclusion criteria are not eligible for study participation:

  • MRI defining progression is consistent with a diagnosis of glioblastoma or radiation necrosis.
  • Patients who are considered to be refractory to EBRT and temozolomide but who have not progressed.
  • Prior systemic therapy for recurrence of AA.
  • Presence of extracranial or leptomeningeal disease.
  • Prior lomustine use.
  • Any other clinical condition or prior therapy that, in the opinion of the Investigator, would make the patient unsuitable for the study.
  • Pregnant or breastfeeding.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Eflornithine + LomustineEflornithineEflornithine dosed on a 2 weeks on, 1 week off schedule + Lomustine dosed every 6 weeks
Eflornithine + LomustineLomustineEflornithine dosed on a 2 weeks on, 1 week off schedule + Lomustine dosed every 6 weeks
LomustineLomustineLomustine dosed every 6 weeks
Primary Outcome Measures
NameTimeMethod
Overall survival4 years
Secondary Outcome Measures
NameTimeMethod
Progression-free survival (PFS)4 years
Objective response rate (ORR)4 years

Trial Locations

Locations (78)

Montreal Neurological Institute and Hospital

🇨🇦

Montréal, Quebec, Canada

Centre Jean Perrin

🇫🇷

Clermont-Ferrand, France

Centre Georges François Leclerc

🇫🇷

Dijon, France

Hôpital de la Timone

🇫🇷

Marseille, France

Klinik und Poliklinik fur Neurologie der Universitat Regensburg

🇩🇪

Regensburg, Bayern, Germany

Heinrich-Heine-Universitat Duesseldorf

🇩🇪

Düsseldorf, Nordrhein-Westfalen, Germany

Louisiana State University Health Sciences Center New Orleans

🇺🇸

New Orleans, Louisiana, United States

Hôpital Roger Salengro

🇫🇷

Lille, France

Medical University of South Carolina, Hollings Cancer Center

🇺🇸

Charleston, South Carolina, United States

Tom Baker Cancer Center

🇨🇦

Calgary, Alberta, Canada

JFK Medical Center

🇺🇸

Edison, New Jersey, United States

Wake Forest University Health Sciences

🇺🇸

Winston-Salem, North Carolina, United States

Ottawa Hospital

🇨🇦

Ottawa, Ontario, Canada

Princess Margaret Cancer Center

🇨🇦

Toronto, Ontario, Canada

Universitätsklinikum Essen

🇩🇪

Essen, Nordrhein-Westfalen, Germany

Vrije Universiteit Medisch Centrum (VUMC)

🇳🇱

Amsterdam, Noord-Holland, Netherlands

Universitair Medisch Centrum Utrecht

🇳🇱

Utrecht, Netherlands

University Hospitals Birmingham NHS Foundation Trust

🇬🇧

Birmingham, United Kingdom

Dana Farber Cancer Institute, Brigham and Women's Hospital

🇺🇸

Boston, Massachusetts, United States

Maine Center for Cancer Medicine and Blood Disorders

🇺🇸

Scarborough, Maine, United States

Massachusetts General Hospital

🇺🇸

Boston, Massachusetts, United States

Beth Israel Deaconess Medical Center

🇺🇸

Boston, Massachusetts, United States

MD Anderson Cancer Center

🇺🇸

Houston, Texas, United States

Sunnybrook Research Institute

🇨🇦

Toronto, Ontario, Canada

Fondazione IRCCS - Instituto Neurologico Carlo Besta

🇮🇹

Milano, Italy

Duke University Medical Center

🇺🇸

Durham, North Carolina, United States

Azienda Ospedaliera Universitaria Citta della Salute e della Scienza di Torino - Ospedale Molinette

🇮🇹

Torino, Italy

Sint Elisabeth Ziekenhuis

🇳🇱

Tilburg, Noord-Brabant, Netherlands

Cliniques Universitaires UCL De Mont-Godinne

🇧🇪

Yvoir, Namur, Belgium

Saint Joseph's Hospital and Medical Center

🇺🇸

Phoenix, Arizona, United States

University of Alabama at Birmingham

🇺🇸

Birmingham, Alabama, United States

University of California San Francisco Medical Center

🇺🇸

San Francisco, California, United States

Henry Ford Hospital

🇺🇸

Detroit, Michigan, United States

Providence Brain & Spine Institute

🇺🇸

Portland, Oregon, United States

Vanderbilt University

🇺🇸

Nashville, Tennessee, United States

University of California Irvine Medical Center

🇺🇸

Orange, California, United States

University of Southern California Norris Comprehensive Cancer Center

🇺🇸

Los Angeles, California, United States

Winship Cancer Institute

🇺🇸

Atlanta, Georgia, United States

University of Kentucky Chandler Medical Center

🇺🇸

Lexington, Kentucky, United States

Kaiser Permanente

🇺🇸

Sacramento, California, United States

Piedmont Physicians Neuro-Oncology

🇺🇸

Atlanta, Georgia, United States

UCSD Moores Cancer Center

🇺🇸

San Diego, California, United States

Norton Cancer Institute - Louisville

🇺🇸

Louisville, Kentucky, United States

The University of Iowa

🇺🇸

Iowa City, Iowa, United States

The Cleveland Clinic, Richard E. Jacobs Health Center

🇺🇸

Cleveland, Ohio, United States

Mayo Clinic Minnesota

🇺🇸

Rochester, Minnesota, United States

Mount Sinai Hospital

🇺🇸

New York, New York, United States

Columbia University Medical Center, The Neurological Institute

🇺🇸

New York, New York, United States

Saint Luke's Cancer Institute

🇺🇸

Kansas City, Missouri, United States

University of North Carolina - Chapel Hill

🇺🇸

Chapel Hill, North Carolina, United States

University of Utah

🇺🇸

Salt Lake City, Utah, United States

Swedish Health Services

🇺🇸

Seattle, Washington, United States

Hôpital Universitaire Pitié Salpêtrière

🇫🇷

Paris, France

Institut de Cancerologie de l'Ouest - Angers

🇫🇷

Angers, France

CHRU de Brest

🇫🇷

Brest, France

Edinburgh Cancer Centre - Western General Hospital

🇬🇧

Edinburgh, United Kingdom

Hôpital Pierre Wertheimer - Hospices Civils de Lyon

🇫🇷

Bron, France

Erasmus Medisch Centrum Daniel den Hoed

🇳🇱

Rotterdam, Zuid-Holland, Netherlands

The Royal Marsden NHS Foundation Trust

🇬🇧

London, United Kingdom

The Christie NHS Foundation Trust

🇬🇧

Manchester, United Kingdom

Istituto Oncologico Veneto

🇮🇹

Padova, Italy

Universitaetsklinikum Hamburg-Eppendorf

🇩🇪

Hamburg, Germany

HCA Midwest Division

🇺🇸

Kansas City, Missouri, United States

Kaiser Permanente Center

🇺🇸

Redwood City, California, United States

Northwestern Medicine CDH Cancer Center

🇺🇸

Warrenville, Illinois, United States

OhioHealth Research and Innovation Institute

🇺🇸

Columbus, Ohio, United States

University of Colorado

🇺🇸

Aurora, Colorado, United States

University of South Florida (USF) - H. Lee Moffitt Cancer Center and Research Institute

🇺🇸

Tampa, Florida, United States

Northwestern University

🇺🇸

Chicago, Illinois, United States

John Wayne Cancer Institute

🇺🇸

Santa Monica, California, United States

Washington University

🇺🇸

Saint Louis, Missouri, United States

University of Pennsylvania

🇺🇸

Philadelphia, Pennsylvania, United States

Thomas Jefferson University Hospital

🇺🇸

Philadelphia, Pennsylvania, United States

Neuro-Oncology Associates

🇺🇸

Dallas, Texas, United States

Texas Oncology Austin Brain Tumor Center

🇺🇸

Austin, Texas, United States

Universitair Ziekenhuis Leuven

🇧🇪

Leuven, Flemish Brabant, Belgium

CancerCare Manitoba

🇨🇦

Winnipeg, Manitoba, Canada

Guy's Hospital

🇬🇧

London, United Kingdom

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