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Open-label study to evaluate the efficacy and tolerability of orally administered rosiglitazone in patients with progressive bone Fibrodysplasia (FOP)

Conditions
Fibrodysplasia Ossificans Progressive (FOP) is a rare genetically based disability, characterized by progressive heterotopic ossification, usually associated with congenital malformation of the toes.
MedDRA version: 14.1Level: HLGTClassification code 10028393Term: Musculoskeletal and connective tissue disorders NECSystem Organ Class: 10028395 - Musculoskeletal and connective tissue disorders
Therapeutic area: Diseases [C] - Musculoskeletal Diseases [C05]
Registration Number
EUCTR2011-002516-85-IT
Lead Sponsor
A.O. UNIVERSITARIA INTEGRATA DI VERONA
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Authorised-recruitment may be ongoing or finished
Sex
All
Target Recruitment
Not specified
Inclusion Criteria

·patients of both sexes, older than 18 ·patients affected by FOP genetically confirmed ·patients with a joint mobility limitation > grade 2 (on a scale of 4 points) on at least one joint ·written informed consent signed by the patient or by a legally acceptable representative
Are the trial subjects under 18? no
Number of subjects for this age range: 0
F.1.2 Adults (18-64 years) yes
F.1.2.1 Number of subjects for this age range 18
F.1.3 Elderly (>=65 years) no
F.1.3.1 Number of subjects for this age range

Exclusion Criteria

·Patients affected by Bone Fibrodysplasia other than FOP ·Patients affected by heart failure, ischemic heart disease or with impaired liver function (ALT> 2 times the upper limit of normal) ·Patients under 18 ·Known hypersensitivity to the drug or the excipients 3.Pregnant or lactating women 4.alcoholism 5.drug dependence

Study & Design

Study Type
Interventional clinical trial of medicinal product
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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