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Peripheral targeting of inhaled rhDNase for chronic obstructive asthma in childhood.

Phase 3
Completed
Conditions
asthma
10038716
Registration Number
NL-OMON34039
Lead Sponsor
Erasmus MC, Universitair Medisch Centrum Rotterdam
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Completed
Sex
Not specified
Target Recruitment
60
Inclusion Criteria

Age 6 - 18 years;
Asthma diagnosed according to GINA guidelines;
Treatment with at least 400 microg/day inhaled Budesonide or equivalent (dose constant for at least 6 months) and bronchodilators as needed or daily;
Clinically stable asthma while using a constant dose of inhaled corticosteroids (ICS);
Persistent peripheral airways obstruction as assessed by pulmonary function testing, defined as:
o Dissociation between FVC and FEF75 values: FEF75 at least 20% (absolute % predicted) lower than FVC. ;FVC within normal limits (for this study defined as FVC > 80% pred).

Exclusion Criteria

Asthma exacerbation with hospital admission in last 3 months;
Intensive Care Unit (ICU) admission for asthma in last year;
Current respiratory tract infection;
Inability to follow instructions of the investigator;
Inability to inhale rhDNase;
Concomitant medical conditions that effect inhaled treatment (e.g. cleft palate, severe airway malacia);
Neuromuscular disease;
Smoking.

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
<p>The primary study parameter is the percent change in FEF75. </p><br>
Secondary Outcome Measures
NameTimeMethod
<p>Secondary endpoints will include:<br /><br>§ Lung clearance index (LCI) measurements as assessed by multiple breath<br /><br>washout;<br /><br>§ Cumulative symptom diary scores evaluating asthma symptoms in the 2nd week of<br /><br>intervention (e.g. shortness of breath, cough, exercise intolerance,<br /><br>bronchodilator use etc.);<br /><br>§ FENO;<br /><br>§ Other values obtained in the flow volume curve: FEV1, FVC, PEF.</p><br>
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