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Therapeutic Cancer Vaccine (AST-301, pNGVL3-hICD) in Patients With Breast Cancer

Phase 2
Terminated
Conditions
Breast Cancer
Interventions
Biological: AST-301(pNGVL3-hICD)
Drug: Placebo
Registration Number
NCT05163223
Lead Sponsor
Aston Sci. Inc.
Brief Summary

The purpose of this study is to evaluate the efficacy and safety of an adjuvant treatment of therapeutic cancer vaccine (AST-301, pNGVL3-hICD) in patients with HER2-low expression (IHC 1+ or 2+ and ISH-) and hormone receptor-negative(ER-, PR-) breast cancer with residual disease after neoadjuvant treatment.

Patients will be randomized 1:1 to either the Experimental arm (combination of AST-301/rhuGM CSF and standard adjuvant therapy) or the Control arm (combination of placebo/rhuGM CSF and standard adjuvant therapy). Standard adjuvant chemotherapy will be pembrolizumab or capecitabine.

Adjuvant therapy will be administered in compliance with the NCCN guideline for breast cancer (Version 8, 2021), and IP (AST-301) will be administered 3 times every 3 weeks in the adjuvant treatment period, with a booster administered at 24 weeks (±7 days) post the third dose of IP administration.

Survival follow up will be performed to determine invasive Disease Free survival(iDFS).

Detailed Description

Not provided

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
10
Inclusion Criteria
  • Has a residual invasive cancer in the breast(non-pCR) after neoadjuvant treatment
  • Has stage I, II, or III disease prior to surgery per American Joint Committee on Cancer (AJCC)
  • HER 2 1+ by IHC or HER2 2+by IHC without gene amplification by ISH, as defined by American Society of Clinical Oncology (ASCO)/College of American Pathologists (CAP) guidelines.
  • Hormone receptor (ER and PR) negative by ASCO/CAP guidelines
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1
  • Demonstrates adequate organ function.

Key

Exclusion Criteria
  • Has a history of hypersensitivity or other contraindications to rhGM-CSF
  • Has a history of invasive malignancy ≤5 years prior to first administration of investigational drug except for adequately treated non-melanoma skin cancer or carcinoma in situ.
  • Is on immune suppression therapy or has a history of immune suppression therapy ≤4 weeks prior to the first administration of investigational drugs
  • Has a history of autoimmune disease or inflammatory disease
  • Has active infection including tuberculosis, hepatitis B, hepatitis C or human immunodeficiency virus (HIV) infection
  • Is pregnant or breastfeeding or expecting to conceive children

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Placebo + ChemotherapyrhuGM-CSF* Placebo/rhuGM-CSF (q 3 weeks, 3 cycles) + Standard adjuvant therapy\* * A booster (Placebo/rhuGM CSF) at 24 weeks post the third vaccination * Standard adjuvant therapy will be pembrolizumab or capecitabine (q 3 weeks)
AST-301(pNGVL3-hICD)+ChemotherapyAST-301(pNGVL3-hICD)* AST-301/rhuGM-CSF (q 3 weeks, 3 cycles) + Standard adjuvant therapy\* * A booster (AST-301/rhuGM-CSF) at 24 weeks post the third vaccination * Standard adjuvant therapy will be pembrolizumab or capecitabine (q 3 weeks)
AST-301(pNGVL3-hICD)+ChemotherapyrhuGM-CSF* AST-301/rhuGM-CSF (q 3 weeks, 3 cycles) + Standard adjuvant therapy\* * A booster (AST-301/rhuGM-CSF) at 24 weeks post the third vaccination * Standard adjuvant therapy will be pembrolizumab or capecitabine (q 3 weeks)
Placebo + ChemotherapyPlacebo* Placebo/rhuGM-CSF (q 3 weeks, 3 cycles) + Standard adjuvant therapy\* * A booster (Placebo/rhuGM CSF) at 24 weeks post the third vaccination * Standard adjuvant therapy will be pembrolizumab or capecitabine (q 3 weeks)
AST-301(pNGVL3-hICD)+ChemotherapyCapecitabine* AST-301/rhuGM-CSF (q 3 weeks, 3 cycles) + Standard adjuvant therapy\* * A booster (AST-301/rhuGM-CSF) at 24 weeks post the third vaccination * Standard adjuvant therapy will be pembrolizumab or capecitabine (q 3 weeks)
AST-301(pNGVL3-hICD)+ChemotherapyPembrolizumab* AST-301/rhuGM-CSF (q 3 weeks, 3 cycles) + Standard adjuvant therapy\* * A booster (AST-301/rhuGM-CSF) at 24 weeks post the third vaccination * Standard adjuvant therapy will be pembrolizumab or capecitabine (q 3 weeks)
Placebo + ChemotherapyPembrolizumab* Placebo/rhuGM-CSF (q 3 weeks, 3 cycles) + Standard adjuvant therapy\* * A booster (Placebo/rhuGM CSF) at 24 weeks post the third vaccination * Standard adjuvant therapy will be pembrolizumab or capecitabine (q 3 weeks)
Placebo + ChemotherapyCapecitabine* Placebo/rhuGM-CSF (q 3 weeks, 3 cycles) + Standard adjuvant therapy\* * A booster (Placebo/rhuGM CSF) at 24 weeks post the third vaccination * Standard adjuvant therapy will be pembrolizumab or capecitabine (q 3 weeks)
Primary Outcome Measures
NameTimeMethod
2-year invasive disease free survival rate (iDFS)Overall study period approximately up to 4years (End of study in this study is defined as 2years frm the date of last Patient In.

iDFS event is defined as Ipsilateral breast tumor recurrence Local/regional invasive recurrence Distant recurrence Invasive contralateral breast cancer Death (from breast cancer/non-breast cancer cause/unknown cause) Secondary primary invasive cancer (non-breast)

Secondary Outcome Measures
NameTimeMethod
Change in central memory T cell populationsUp to approximately 82 weeks

Assessment by FACS

Number of participants with treatment-related adverse events as assessed by CTCAEOverall study period approximately up to 4years

To assess safety of AST-301 administered in breast cancer patients.

Distant Recurrence-Free Survival rate, dRFS rateOverall study period approximately up to 4 years

dRFS rate at the end of study

AST-301 specific T cell immune responsesUp to approximately 82 weeks

Immune response will be assessed by IFN-gamma enzyme-linked immune absorbent spot (ELISpot) assay

Trial Locations

Locations (17)

Ironwood Cancer and Research Centers

🇺🇸

Chandler, Arizona, United States

Scripps Health

🇺🇸

La Jolla, California, United States

China Medical University Hospital

🇨🇳

Taichung City, Taiwan

University of Illinois Cancer Center

🇺🇸

Chicago, Illinois, United States

The Ohio State University Comprehensive Cancer Center

🇺🇸

Columbus, Ohio, United States

Gabrail Cancer Center Research

🇺🇸

Canton, Ohio, United States

University of Washington

🇺🇸

Seattle, Washington, United States

Changhua Christian Hospital

🇨🇳

Changhua City, Taiwan

Chi Mei Medical Center

🇨🇳

Tainan, Taiwan

Kaohsiung Medical University Chung-Ho Memorial Hospital

🇨🇳

Kaohsiung, Taiwan

Moffitt Cancer Center

🇺🇸

Tampa, Florida, United States

Nebraska Cancer Specialist

🇺🇸

Omaha, Nebraska, United States

Providence Cancer Institute

🇺🇸

Portland, Oregon, United States

Toledo Clinic Cancer Center

🇺🇸

Toledo, Ohio, United States

Koo Foundation Sun Yat-Sen Cancer Center

🇨🇳

Taipei city, Taiwan

National Taiwan University Hospital

🇨🇳

Taipei City, Taiwan

Taipei Veterans General Hospital

🇨🇳

Taipei City, Taiwan

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