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Clinical and Molecular Description of PKD1 and PKD2 Mutation Negative Carriers in ADPKD

Not Applicable
Completed
Conditions
Autosomal Dominant Polycystic Kidney Disease (ADPKD)
Registration Number
NCT02112136
Lead Sponsor
University Hospital, Brest
Brief Summary

The aim of this study is to identify families with ADPKD , characterize the phenotype and screen for mutations in known genes (PKD1 and PKD2, and then HNF1b and UMOD in PKD1 PKD2 negative carriers).

Genome wide analysis will be performed in families without mutations identified.

Detailed Description

* Inclusion of ADPKD patients in 20 different centers of Nephrology in the Western part of France

* Characterization of the Phenotype

* Collect DNA sample

* Analysis of PKD1 and PKD2 genes first

* Analysis of HNFIb and UMOD for PKD1 and PKD2 negative patients

* Recruitment of affected and non-affected relatives of PKD1 and PKD2 negative ADPKD patients

* Identify new genes involved in ADPKD using exome sequencing in PKD1 and PKD2 negative pedigrees

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
1450
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Primary Outcome Measures
NameTimeMethod
Number of patients/families with no mutations identified in PKD1 and PKD2 genes3 years
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (25)

CHU Angers

🇫🇷

Angers, France

AUB Brest

🇫🇷

Brest, France

Centre de néphrologie et de dialyse d'Armorique

🇫🇷

Brest, France

CHRU Brest

🇫🇷

Brest, France

CH Laval

🇫🇷

Laval, France

CH du Mans

🇫🇷

Le Mans, France

ECHO dialyse

🇫🇷

Le Mans, France

Centre de dialyse de Lorient

🇫🇷

Lorient, France

CH Bretagne Sud

🇫🇷

Lorient, France

Hôpital Hôtel Dieu - CHU Nantes

🇫🇷

Nantes, France

Scroll for more (15 remaining)
CHU Angers
🇫🇷Angers, France

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