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Empagliflozin and Anakinra for the Treatment of Postprandial Hypoglycemia in Patients With Prediabetes

Phase 2
Active, not recruiting
Conditions
Postprandial Hypoglycemia
Interventions
Other: saline subcutaneous (s.c.) (placebo)
Other: tablet per oral (p.o.) (placebo)
Registration Number
NCT05174507
Lead Sponsor
University Hospital, Basel, Switzerland
Brief Summary

This study is to analyze whether the SGLT2-inhibitor empagliflozin or the IL-1 receptor antagonist anakinra may improve postprandial hypoglycemia in subjects with prediabetes.

Detailed Description

Subjects with prediabetes may develop postprandial hypoglycemia. This is probably due to a dysfunction of the insulin producing β-cell characterized by a delayed and exaggerated insulin secretion leading to an initial peak in glycaemia followed by a rapid fall and eventually resulting in hypoglycemia. The latter occurring typically within 1 to 3 hours after food intake.

In patients with gastric bypass surgery and postprandial hypoglycemia the SGLT2-inhibitor empagliflozin and the IL-1 receptor antagonist anakinra reduced postprandial insulin release and prevented hypoglycemia. This study is to analyze whether a similar therapeutic approach using empagliflozin and anakinra may also improve postprandial hypoglycemia in subjects with prediabetes.

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
26
Inclusion Criteria
  • Subjects with prediabetes defined by Glycosylated haemoglobin A1c (HbA1c) 5.7-6.4 % or fasting plasma glucose 6.1-6.9 mmol/l) or plasma glucose 2 h following 75 glucose ingestion of 7.8-11.0 mmol/l.
  • Hypoglycemia occuring 1 to 3 h following ingestion of a standardized liquid mixed-meal (75 g carbohydrates) and fulfilling the Whipple's triad (glucose below 3.0 mmol/l).
  • Age ≥ 18 years
  • For subjects with reproductive potential, willingness to use contraceptive measures adequate to prevent the subject from becoming pregnant during the study
Exclusion Criteria
  • Upper gastrointestinal surgery
  • Diagnosis of any type of diabetes mellitus
  • Signs of current infection
  • Use of investigational drug up to one week prior to start of treatment phase
  • Glucocorticoid therapy
  • Neutropenia (leukocyte count < 1.5 × 109/L or absolute neutrophil count (ANC) < 0.5 × 109/L)
  • Anemia (hemoglobin < 11 g/dL for males, < 10 g/dL for females)
  • Clinically significant kidney or liver disease (creatinine > 1.5 mg/dL, aspartate aminotransferase (AST)/ALT > 2 × ULN, alkaline phosphatase > 2 × ULN, or total bilirubin [tBili] > 1.5 × ULN)
  • Uncontrolled disease
  • Currently pregnant or breastfeeding
  • No subjects meeting the criteria for vulnerability
  • Participation in another study with investigational drug within the 30 days preceding and during the present study.

Study & Design

Study Type
INTERVENTIONAL
Study Design
CROSSOVER
Arm && Interventions
GroupInterventionDescription
Group 1 (anakinra; placebo; empagliflozin)tablet per oral (p.o.) (placebo)Group 1: study day 1: anakinra; study day2: placebo; study day 3: empagliflozin
Group 2 (placebo; anakinra; empagliflozin)saline subcutaneous (s.c.) (placebo)study day 1: placebo; study day2: anakinra; study day 3: empagliflozin
Group 2 (placebo; anakinra; empagliflozin)tablet per oral (p.o.) (placebo)study day 1: placebo; study day2: anakinra; study day 3: empagliflozin
Group 4 (empagliflozin; anakinra; placebo)saline subcutaneous (s.c.) (placebo)study day 1: empagliflozin; study day2: anakinra; study day 3: placebo
Group 3 (empagliflozin; placebo; anakinra)tablet per oral (p.o.) (placebo)study day 1: empagliflozin; study day2: placebo; study day 3: anakinra
Group 1 (anakinra; placebo; empagliflozin)saline subcutaneous (s.c.) (placebo)Group 1: study day 1: anakinra; study day2: placebo; study day 3: empagliflozin
Group 3 (empagliflozin; placebo; anakinra)saline subcutaneous (s.c.) (placebo)study day 1: empagliflozin; study day2: placebo; study day 3: anakinra
Group 5 (placebo; empagliflozin; anakinra)tablet per oral (p.o.) (placebo)study day 1: placebo; study day2: empagliflozin; study day 3: anakinra
Group 4 (empagliflozin; anakinra; placebo)tablet per oral (p.o.) (placebo)study day 1: empagliflozin; study day2: anakinra; study day 3: placebo
Group 6 (anakinra; empagliflozin; placebo)saline subcutaneous (s.c.) (placebo)study day 1:anakinra; study day2: empagliflozin; study day 3: placebo
Group 5 (placebo; empagliflozin; anakinra)saline subcutaneous (s.c.) (placebo)study day 1: placebo; study day2: empagliflozin; study day 3: anakinra
Group 6 (anakinra; empagliflozin; placebo)tablet per oral (p.o.) (placebo)study day 1:anakinra; study day2: empagliflozin; study day 3: placebo
Group 1 (anakinra; placebo; empagliflozin)empagliflozinGroup 1: study day 1: anakinra; study day2: placebo; study day 3: empagliflozin
Group 1 (anakinra; placebo; empagliflozin)anakinraGroup 1: study day 1: anakinra; study day2: placebo; study day 3: empagliflozin
Group 2 (placebo; anakinra; empagliflozin)empagliflozinstudy day 1: placebo; study day2: anakinra; study day 3: empagliflozin
Group 3 (empagliflozin; placebo; anakinra)anakinrastudy day 1: empagliflozin; study day2: placebo; study day 3: anakinra
Group 2 (placebo; anakinra; empagliflozin)anakinrastudy day 1: placebo; study day2: anakinra; study day 3: empagliflozin
Group 3 (empagliflozin; placebo; anakinra)empagliflozinstudy day 1: empagliflozin; study day2: placebo; study day 3: anakinra
Group 4 (empagliflozin; anakinra; placebo)empagliflozinstudy day 1: empagliflozin; study day2: anakinra; study day 3: placebo
Group 4 (empagliflozin; anakinra; placebo)anakinrastudy day 1: empagliflozin; study day2: anakinra; study day 3: placebo
Group 5 (placebo; empagliflozin; anakinra)anakinrastudy day 1: placebo; study day2: empagliflozin; study day 3: anakinra
Group 5 (placebo; empagliflozin; anakinra)empagliflozinstudy day 1: placebo; study day2: empagliflozin; study day 3: anakinra
Group 6 (anakinra; empagliflozin; placebo)empagliflozinstudy day 1:anakinra; study day2: empagliflozin; study day 3: placebo
Group 6 (anakinra; empagliflozin; placebo)anakinrastudy day 1:anakinra; study day2: empagliflozin; study day 3: placebo
Primary Outcome Measures
NameTimeMethod
Number of symptomatic hypoglycemiaup to 3 hours after ingestion of the liquid mixed-meal

Incidence of symptomatic hypoglycemia following a standardized mixed-meal test defined by appearance of typical symptoms, blood glucose level below 3.0 mmol/l and relief of symptoms when the glucose level is raised (Whipple's triad).

Secondary Outcome Measures
NameTimeMethod
Nadir plasma glucose (mmol/l)up to 3 hours after ingestion of the liquid mixed-meal

Nadir plasma glucose (mmol/l)

Change in inflammatory stateat baseline and 60 min after ingestion of the mixed meal

Change in inflammatory laboratory parameters (Interleukin (IL)1ß, IL6, Tumor necrosis factor (TNF) α, IL-10, IL-1Ra) in supernatants of Lipopolysaccharide (LPS)-stimulated and unstimulated peripheral blood mononuclear cells (PBMC)

Change in RNA sequencing (RNAseq) in peripheral PBMCat baseline and 60 min after ingestion of the mixed meal

Change in RNAseq in peripheral PBMC

Change in proinsulin to insulin ratio in serumat baseline and 60 min after ingestion of the mixed meal

Change in proinsulin to insulin ratio in serum

Severity of symptoms of hypoglycemia according to the Edinburgh Hypoglycemia Scaleup to 3 hours after ingestion of the liquid mixed-meal

The Edinburgh Hypoglycemia Scale is a classification of the 11 most common symptoms of hypoglycemia. Subjective intensity-grading:

* no symptoms 0

* light symptoms 1

* moderate symptoms 2

* severe symptoms 3

Trial Locations

Locations (1)

Department of Endocrinology, Diabetes and Metabolism, University Hospital Basel

🇨🇭

Basel, Switzerland

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