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An Open-Label Study of AKCEA-APOCIII-LRX Administered Subcutaneously to Patients With Familial Chylomicronemia Syndrome (FCS) Previously Treated With Volanesorsen (ISIS 304801)

Phase 1
Recruiting
Conditions
Familial Chylomicronemia Syndrome
MedDRA version: 20.0Level: LLTClassification code: 10059191Term: Familial hypertriglyceridemia Class: 10010331
MedDRA version: 20.1Level: LLTClassification code: 10020607Term: Hyperchylomicronemia Class: 10027433
Therapeutic area: Diseases [C] - Congenital, Hereditary, and Neonatal Diseases and Abnormalities [C16]
Registration Number
CTIS2023-508815-22-00
Lead Sponsor
Ionis Pharmaceuticals Inc.
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Recruiting
Sex
All
Target Recruitment
30
Inclusion Criteria

Patients with FCS (clinical or genetic diagnosis) currently on or previously treated with volanesorsen (ISIS 304801) Study participants in countries where Waylivra is commercially approved and available for patients should not be deprived of the treatment option with Waylivra. Participation in this study for such patients will only be allowed when Waylivra was discontinued due to AEs, Other protocol-defined inclusion criteria apply.

Exclusion Criteria

Treatment with another investigational drug (non-oligonucleotide), biological agent, or device within 4 weeks of Screening, or 5 half-lives of investigational agent, whichever is longer. Have any other conditions including significant medical history which, in the opinion of the Investigator would make the patient unsuitable for inclusion, or could interfere with the patient participating in or completing the Study

Study & Design

Study Type
Interventional clinical trial of medicinal product
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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