MedPath

Idarubicin Combined to Azacitidine in Int-2 or High Risk Myelodysplastic Syndromes

Phase 1
Completed
Conditions
High Grade Myelodysplastic Syndrome Lesions
Interventions
Registration Number
NCT01305135
Lead Sponsor
Groupe Francophone des Myelodysplasies
Brief Summary

Patients will receive escalating doses of ldarubicin combined to Azacitidine given at the FDA/EMEA approved Schedule and dosing.

For the Phase I study :

Determine the safety and tolerance of escalating doses of Idarubicin combined to Azacitidine in patients with INT-2 or higher risk MDS.

For the phase II study:

Primary: Evaluate rate and duration of response (according to IWG 2006 criteria and IWG 2000 criteria) to the combination of Idarubicin and Azacitidine in patients with INT-2 or higher risk MDS

Detailed Description

Patients will receive ldarubicin combined to Azacitidine.

* The first 10 patients will receive Idarubicin 5 mg/m2/d on day 8 of each cycle of Azacitidine 75 mg/m2/d CI during 7 days (First Cohort ).

* Progression or not to the next cohort of 10 patients : Idarubicin 10 mgm2/d on day 8 of each cycle of Azacitidine 75 mg/m2/d CI during 7 days (Second cohort of 10 patients), will be decided after completion of the first cohort, after review of hematological toxicity by an independent safety review committee (SRC).

* The next 21 patients will be treated either according to the first or second cohort schedule of Idarubicin, after review of hematological toxicity and efficacy by an independent safety review committee (SRC).

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
41
Inclusion Criteria
  • Documented diagnosis of MDS, or CMML with WBC < 13,000/mm3 that meets IPSS criteria for intermediate-2 or high-risk disease,
  • IPSS score ≥1.5
  • Myocardial function do not contraindicate the use of idarubicin
  • Age ≥ 18 years
  • Performance Status ≤2 according to ECOG.
  • Serum creatinine < 1.5 x ULN and normal levels of electrolytes (serum sodium 136-145 mmol/l, Potassium 3,5-4,5 mmol/l, alkaline Reserve 23-29 mmol/l, , Calcium 2,15-2,5 mmol/l, Phosphore 0,87-1,45 mmol/l) Serum aspartate aminotransferase (AST)/serum glutamic-oxaloacetic transaminase (SGOT) or alanine transaminase (ALT)/serum glutamate pyruvate transaminase (SGPT) < 1.5 x upper limit of normal (ULN)
  • Serum total bilirubin < 1.5 x ULN.
  • Must be able to adhere to the study visit schedule and other protocol requirements
  • Signed informed consent.

Female subjects of childbearing potential must:

• Accept effective contraception without interruption throughout the duration of study and up to three months after the end of treatment.

Male subjects must

  • Agree to use condoms throughout study drug therapy, during any dose interruption and for one week after cessation of study therapy and up to three months after the final treatment if their partner is of childbearing potential and has no contraception.
  • Agree to learn the procedures for preservation of sperm
Exclusion Criteria
  • Uncontrolled infection
  • Prior therapy with anthracycline for MDS.
  • Eligible for an allogeneic stem cell transplantation.
  • Prior therapy with demethylating agents within the last 3 months
  • Prior therapy with Hematopoietic growth factor (ESA or G-CSF) agents or cytotoxic agents (oral chemotherapy, low doses AraC) within the last 30 days.
  • Prior history of malignancy other than MDS (except basal cell or squamous cell carcinoma or carcinoma in situ of the cervix or breast)
  • Pregnant or lactating females
  • Known HIV-1 positivity
  • Contra-indication to Anthracyclines

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
azacitidine 75mg/m²/d + idarubicin 5mg/m²/dazacitidine and idarubicinphase I : palier 1 have 10 patients and palier 2 have to 10 patients. palier 1: Ida 5mg/m²/d (D8) + AZACITIDINE 75mg/m²/d (D1-D7)
Azacitidine 75mg/m²/d + idarubicin 10mg/m²/dazacitidine and idarubicinpalier 2: Ida 10mg/m²/d (D8)+ Azacitidine 75mg/m²/d (D1-D7)
Primary Outcome Measures
NameTimeMethod
To determined tolerance and dose limiting toxicities to idarubicin and azacitidine association.After 12 weeks treatment
Secondary Outcome Measures
NameTimeMethod
to determined overall response rate and response durationAfter six months

Trial Locations

Locations (32)

CHU Dijon Hôpital d'enfants

🇫🇷

Dijon, France

CHU Albert Michallon

🇫🇷

Grenoble, France

Hôpital Hautepierre

🇫🇷

Strasbourg, France

Hôpital PURPAN - Hématologie Clinique

🇫🇷

Toulouse, France

Hôpital de la cote basque

🇫🇷

Bayonne, France

Centre Hospitalier Lyon Sud

🇫🇷

Lyon, France

Hôpital Avicenne

🇫🇷

Bobigny, France

CHU de Limoges

🇫🇷

Limoges, France

CHU Hotel dieu

🇫🇷

Nantes, France

Centre hospitalier Joffre

🇫🇷

Perpignan, France

Hôpital Aziza Othmana

🇹🇳

Tunis, Tunisia

Hôpital Purpan - Médecine Interne

🇫🇷

Toulouse, France

Hôpital Saint Antoine

🇫🇷

Paris, France

Hôpital Saint Louis - Hématologie Séniors

🇫🇷

Paris, France

CHRU de Caen - Hôpital Côte de Nacre

🇫🇷

Caen, France

CHU Estaing

🇫🇷

Clermont-Ferrand, France

Hôpital saint louis - Hématologie Clinique

🇫🇷

Paris, France

CH Le Mans

🇫🇷

Le Mans, France

Institut Paoli-Calmette

🇫🇷

Marseille, France

CHU Brabois

🇫🇷

Nancy, France

CHU NICE, Hôpital l'Archet

🇫🇷

Nice, France

Hôpital cochin

🇫🇷

Paris, France

CHU de Poitiers

🇫🇷

Poitiers, France

CH de Périgueux

🇫🇷

Périgueux, France

Hôpital Pontchaillou

🇫🇷

Rennes, France

Centre Henri Becquerel

🇫🇷

Rouen, France

Hôpital Bretonneau

🇫🇷

Tours, France

CH de Valence

🇫🇷

Valence, France

Institut Gustave Roussy

🇫🇷

Villejuif, France

CHU de Haut-Lévèque

🇫🇷

Pessac, Bordeaux - Pessac, France

CHU d'Amiens

🇫🇷

Amiens, France

CHU d'Angers

🇫🇷

Angers, France

© Copyright 2025. All Rights Reserved by MedPath