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Prospective Study of Pregnancy in Women with Cystic Fibrosis

Active, not recruiting
Conditions
Cystic Fibrosis
Pregnancy Related
Registration Number
NCT04828382
Lead Sponsor
Amalia Magaret
Brief Summary

In this study, the investigators aim to evaluate changes in lung function in women with cystic fibrosis (CF) during pregnancy and for 2 years after pregnancy based on exposure to highly effective cystic fibrosis transmembrane conductance regulator (CFTR) modulators.

Detailed Description

Advances in medical treatment, including the use of highly effective CFTR modulators have greatly increased life expectancy in women with CF, but the effects of pregnancy on women with CF are yet unknown. It is anticipated that over 90% of the CF population will be on CFTR modulators in the next few years. More knowledge about the effects of CFTR modulators in pregnancy is needed.

This is a prospective, multi-center, observational study to follow pregnant women with CF, conducted at 40 US sites. Women are enrolled in the first trimester of pregnancy and assessed every 3 months during pregnancy and during the first year after delivery, then every 6 months for an additional year. Changes in lung function over the course of pregnancy will be evaluated based on cumulative CFTR modulator use while pregnant while accounting for other factors that may influence changes in pulmonary function: baseline lung function, genotype, history of exacerbations, and pre-existing co-morbid conditions.

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
Female
Target Recruitment
285
Inclusion Criteria
  • Pregnant, intending to continue pregnancy, enrolled in the Cystic Fibrosis Foundation Patient Registry (CFFPR)
Exclusion Criteria
  • None

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Forced expiratory volume at one second (FEV1) percent predicted after delivery and restart of modulators42 weeks

Change in FEV1 percent predicted after delivery and restart of modulators relative to measures assessed prior to pregnancy

Forced expiratory volume at one second (FEV1) percent predicted after delivery42 weeks

Change in FEV1 percent predicted after delivery relative to measures assessed prior to pregnancy

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (40)

The Minnesota Cystic Fibrosis Center

🇺🇸

Minneapolis, Minnesota, United States

University of Alabama at Birmingham

🇺🇸

Birmingham, Alabama, United States

University of Arkansas for Medical Sciences

🇺🇸

Little Rock, Arkansas, United States

University of California San Diego

🇺🇸

La Jolla, California, United States

National Jewish Health

🇺🇸

Denver, Colorado, United States

University of Florida

🇺🇸

Gainesville, Florida, United States

Joe DiMaggio Children's Hospital

🇺🇸

Hollywood, Florida, United States

Emory University

🇺🇸

Atlanta, Georgia, United States

Saint Luke's Cystic Fibrosis Center of Idaho

🇺🇸

Boise, Idaho, United States

Indiana University Medical Center

🇺🇸

Indianapolis, Indiana, United States

University of Kansas Medical Center

🇺🇸

Kansas City, Kansas, United States

University of Kentucky

🇺🇸

Lexington, Kentucky, United States

Tulane University

🇺🇸

New Orleans, Louisiana, United States

John Hopkins Hospital

🇺🇸

Baltimore, Maryland, United States

Massachusetts General Hospital

🇺🇸

Boston, Massachusetts, United States

Boston Children's Hospital, Brigham & Women's Hospital

🇺🇸

Boston, Massachusetts, United States

University of Michigan Health System

🇺🇸

Ann Arbor, Michigan, United States

Helen DeVos Children's Hospital

🇺🇸

Grand Rapids, Michigan, United States

Washington University School of Medicine

🇺🇸

Saint Louis, Missouri, United States

University of Nebraska Medical Center

🇺🇸

Omaha, Nebraska, United States

The Cystic Fibrosis Center of Western New York

🇺🇸

Buffalo, New York, United States

Columbia University Cystic Fibrosis Program

🇺🇸

New York, New York, United States

University of Rochester Medical Center Strong Memorial

🇺🇸

Rochester, New York, United States

SUNY Upstate Medical University

🇺🇸

Syracuse, New York, United States

University of North Carolina at Chapel Hill

🇺🇸

Chapel Hill, North Carolina, United States

University of Cincinnati Medical Center

🇺🇸

Cincinnati, Ohio, United States

Rainbow Babies and Children's Hospital/University Hospitals Cleveland Medical Center

🇺🇸

Cleveland, Ohio, United States

Cleveland Clinic Cystic Fibrosis Program

🇺🇸

Cleveland, Ohio, United States

Nationwide Children's Hospital

🇺🇸

Columbus, Ohio, United States

Oregon Health Sciences University

🇺🇸

Portland, Oregon, United States

University of Pennsylvania

🇺🇸

Philadelphia, Pennsylvania, United States

University of Pittsburgh Medical Center

🇺🇸

Pittsburgh, Pennsylvania, United States

Medical University of South Carolina

🇺🇸

Charleston, South Carolina, United States

Vanderbilt Children's Hospital

🇺🇸

Nashville, Tennessee, United States

University of Texas Southwestern

🇺🇸

Dallas, Texas, United States

Baylor College of Medicine

🇺🇸

Houston, Texas, United States

Intermountain Cystic Fibrosis Center

🇺🇸

Salt Lake City, Utah, United States

University of Washington Medical Center

🇺🇸

Seattle, Washington, United States

University of Wisconsin

🇺🇸

Madison, Wisconsin, United States

Froedtert & Medical College of Wisconsin

🇺🇸

Milwaukee, Wisconsin, United States

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