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Study Evaluating Pharmacovigilance Of Refacto AF

Completed
Conditions
Hemophilia A
Interventions
Drug: ReFacto AF (Moroctocog alfa)
Registration Number
NCT00895037
Lead Sponsor
Pfizer
Brief Summary

The purpose of this observational study is to describe the incidence of adverse events among patients treated with Refacto AF in usual health care settings in Germany and Austria.

Detailed Description

Non-interventional study: subjects to be selected according to the usual clinical practice of their physician

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
101
Inclusion Criteria
  • Patients with hemophilia A of any severity already receiving or starting treatment with ReFacto AF.
Exclusion Criteria
  • Patients with Hemophilia A treated with a product other than Refacto AF.

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
1ReFacto AF (Moroctocog alfa)Patients treated with Refacto AF
Primary Outcome Measures
NameTimeMethod
Number of Participants With Treatment-Emergent Adverse Events (AEs) and Serious Adverse Events (SAEs)Baseline until last visit (up to 87 months)

An AE was any untoward medical occurrence in a participant who received study treatment without regard to possibility of causal relationship. SAE was an AE resulting in any of the following outcomes or deemed significant for any other reason: death; initial or prolonged inpatient hospitalization; life-threatening experience (immediate risk of dying); persistent or significant disability or incapacity; cancer; congenital anomaly. Treatment-emergent are events between first dose of study drug and up to last visit (up to 87 months) that were absent before treatment or that worsened relative to pretreatment state. AEs included both serious and non-serious adverse events.

Number of Participants With Factor VIII (FVIII) Inhibitor Development as Measured by the Nijmegen-Modified Bethesda AssayBaseline until last visit (up to 87 months)

FVIII inhibitor development was defined as measured inhibitor titer of greater than (\>) 0.6 Bethesda Units (BU) using the Nijmegen-modified Bethesda assay.

Number of Participants With Treatment-Related Adverse Events (AEs) and Serious Adverse Events (SAEs)Baseline until last visit (up to 87 months)

Treatment-related AE was any untoward medical occurrence attributed to study drug in a participant who received study drug. SAE was an AE resulting in any of the following outcomes or deemed significant for any other reason: death; initial or prolonged inpatient hospitalization; life-threatening experience (immediate risk of dying); persistent or significant disability/incapacity; cancer; congenital anomaly. AEs included both serious and non-serious adverse events. Relatedness of AEs with Refacto AF was assessed by the investigator.

Mean Total Number of Bleeding Episodes in ParticipantsBaseline until last visit (up to 87 months)

Participants documented all bleeding episodes in a diary during the study.

Secondary Outcome Measures
NameTimeMethod
Investigator Assessment of Treatment Satisfaction of ParticipantsEnd of study visit (any time up to 87 months)

Investigator assessed the treatment satisfaction of participants and categorized as very satisfied, satisfied, unsatisfied, or very unsatisfied.

Mean Total Number of Bleeding Episodes Per Year in ParticipantsBaseline until last visit (up to 87 months)

Participants documented all bleeding episodes in a diary during the study. Mean total number of bleeding episodes per year was calculated as: mean total number of bleeding episodes divided by duration of observation period (in years) for bleeding documentation.

Participant Assessment of Satisfaction With Treatment HandlingEnd of study visit (any time up to 87 months)

Participants evaluated their satisfaction with handing (administration) of Refacto AF and rated it in 4 categories as: very satisfied, satisfied, unsatisfied and very unsatisfied.

Number of Participants With Change From Baseline Status in Days Missed From School or WorkBaseline until last visit (up to 87 months)

Change from baseline status in days missed from school or work was categorized in 3 categories: Improvement, unchanged and worsening. Improvement defined as a decrease in number of days missed by participants from school/work as compared to baseline; worsening was defined as an increase in number of days missed by participants from school/work as compared to baseline; unchanged was defined as no change in number of days missed by participants from school/work as compared to baseline. In this outcome measure, number of participants with change from baseline status (as improved, worsen, unchanged) in days missed from school/work were reported.

Trial Locations

Locations (24)

Universitaetsklinikum Duesseldorf

🇩🇪

Duesseldorf, Germany

Stiftung Deutsche Klinik fur Diagnostik GmbH

🇩🇪

Wiesbaden, Germany

Klinikum Bremen Mitte

🇩🇪

Bremen, Germany

Hämophilie-Zentrum Rhein Main GmbH

🇩🇪

Mörfelden-Walldorf, Germany

Universität Regensburg

🇩🇪

Regensburg, Germany

Asklepios Fachklinikum Stadtroda GmbH

🇩🇪

Stadtroda, Germany

Vivantes Klinikum im Friedrichshain

🇩🇪

Berlin, Germany

Allgemeines Krankenhaus Linz, Kinderklinik

🇦🇹

Linz, Austria

Institut for Thrombophilia and Hemastaseologie

🇩🇪

Muenster, Germany

Universitaetsklinik fuer Kinder- und Jugendmedizin

🇩🇪

Tuebingen, Germany

Praxis Dr. Autenrieth

🇩🇪

Metzingen, Germany

Stauferklinikum Schwaebisch Gmuend

🇩🇪

Mutlangen, Germany

Praxis zur Diagnostik und Therapie Von Blutgerinnungstoerungen

🇩🇪

Frankfurt a. M., Germany

Praxis fur Kinder- und Jugendmedizin

🇩🇪

Grunwald, Germany

Klinikum Stuttgart

🇩🇪

Stuttgart, Germany

LKH - Univ. Klinikum Graz,Abt. fur Hamatologie

🇦🇹

Graz, Austria

Universitaetsklinikum Duesseldorf, Klinik f. Kinder-Onkologie, Haematologie u. Klinische Immunologie

🇩🇪

Duesseldorf, Germany

Universitaetsklinik fuer Innere Medizin 1

🇦🇹

Wien, Austria

Sonnengesundheitszentrum

🇩🇪

München, Bayern, Germany

Werlhof-Institut für Haemostaseologie GmbH

🇩🇪

Hannover, Niedersachsen, Germany

Donaustrasse 78

🇩🇪

Memmingen, Germany

CRC Coagulation Research Centre GmbH

🇩🇪

Duisburg, Germany

SRH Kurpfalzkrankenhaus Heidelberg

🇩🇪

Heidelberg, Germany

Medizinische Hochschule Hannover

🇩🇪

Hannover, Germany

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