MedPath

Efficacy and Safety Study of BERIPLEX® P/N (Kcentra) Compared With Plasma in Patients With Acute Major Bleeding Caused by Anticoagulant Therapy

Phase 3
Completed
Conditions
Blood Coagulation Disorders
Acute Major Bleeding
Interventions
Biological: Fresh frozen plasma
Biological: Beriplex® P/N (Kcentra)
Registration Number
NCT00708435
Lead Sponsor
CSL Behring
Brief Summary

The purpose of this study is to evaluate efficacy, safety and tolerance of BERIPLEX® P/N (Kcentra) compared with plasma in regard to rapid reversal of coagulopathy induced by coumarin derivatives in subjects who require immediate correction of INR (International Normalized Ratio)and to stop an acute major bleeding.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
216
Inclusion Criteria
  • Male and female subjects ≥ 18 years
  • Subjects who have received oral vitamin K-antagonist therapy
  • Subjects who have acute major bleeding, defined as one of the following: life-threatening or potentially life-threatening, acute bleeding associated with a fall in hemoglobin (Hb) level ≥ 2g/dL, bleeding requiring blood product transfusion
  • INR ≥ 2 within 3 hours before start of study treatment
  • Informed consent has been obtained
Read More
Exclusion Criteria
  • Expected survival of less than 3 days, or expected surgery in less than 1 day
  • Acute trauma for which reversal of vitamin K antagonists alone would not be expected to control the acute bleeding event
  • Use of unfractionated or low molecular weight heparin use from 24 hours prior to enrollment or expected need within 24 hours after start of infusion
  • For patients with ICH: Glasgow coma score (GCS) < 7; intracerebral hematoma volume > 30cc as assessed by ABC/21; for subdural hematomas: maximum thickness ≥ 10 mm, midline shift ≥ 5 mm; for subarachnoid hemorrhage: any evidence of hydrocephalus; infratentorial ICH location; epidural hematomas; intraventricular extension of hemorrhage; modified Rankin score (mRS) of >3 prior to ICH
  • History of thrombotic event, myocardial infarction, disseminated intravascular coagulation, cerebral vascular accident, transient ischemic attack, unstable angina pectoris, or severe peripheral vascular disease within 3 months of enrollment
  • Known history of antiphospholipid antibody syndrome or lupus anticoagulant antibodies
  • Suspected or confirmed sepsis at time of enrollment
  • Administration of whole blood, plasma, plasma fractions or platelets within 2 weeks prior to inclusion into the study
  • Large blood vessel rupture (e.g. in advanced cancer patient)
  • Pre-existing progressive fatal disease with a life expectancy of less than 2 months
  • Known inhibitors to coagulation factors II, VII, IX, or X; or hereditary protein C or protein S deficiency; or heparin-induced, type II thrombocytopenia
  • Treatment with any other investigational medicinal product within 30 days prior to inclusion into the study
  • Presence or history of hypersensitivity to components of the study medication
  • Pregnant or breast-feeding women
  • Prior inclusion in this study or any other CSL Behring-sponsored Beriplex study
Read More

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Fresh frozen plasmaFresh frozen plasma-
Beriplex® P/NBeriplex® P/N (Kcentra)-
Primary Outcome Measures
NameTimeMethod
Percentage of Participants Achieving Hemostatic Efficacy of Stopping an Ongoing Major BleedAt 1 and 4 hours after the end of infusion

Hemostatic efficacy was determined by a blinded independent board as excellent, good, or poor/none, based on prespecified definitions. Assessments of visible or non-visible musculoskeletal bleeding were made at 1 and 4 hours after the end of infusion. Hemostatic efficacy was the binary endpoint of effective or non-effective hemostasis, where 'effective' was a hemostatic efficacy rating of "excellent" or "good," and 'non-effective' was a hemostatic efficacy rating of "poor/none".

Percentage of Participants Who Had a Rapid Decrease of the International Normalized Ratio (INR)30 minutes after end of infusion

A rapid decrease of the international normalized ratio (INR) was defined as an INR ≤ 1.3 at 30 minutes after the end of the infusion. The INR is a standard way to describe the time it takes for blood to clot; an INR range of 0.8 to 1.2 is considered normal for a healthy person who is not using oral anticoagulant therapy.

Secondary Outcome Measures
NameTimeMethod
Plasma Levels of Factors II, VII, IX, and X, Protein C, and Protein SFrom preinfusion until 24 h after the start of infusion

Plasma levels are presented as the percentage of normal at pre-infusion and 30 min and 24 h after the start of infusion. The plasma level assay results are reported as a potency relative to a standard, where 100% is considered to be normal.

45-Day All-cause MortalityUntil Day 45
Percentage of Participants With INR Correction at Various Times After RandomizationFrom randomization until INR correction; calculated at 2.5, 3, 5, 8, 14, and 26 h after randomization.

The time taken from randomization to INR correction (defined as an INR ≤ 1.3) was recorded. The percentage of participants with INR correction was calculated at 2.5, 3, 5, 8, 14, and 26 h after randomization.

Use of Other Blood Products and Hemostatic AgentsFrom the start of infusion until 24 h after the start of infusion

Other blood products and hemostatic agents containing coagulation factors (such as whole blood, plasma, albumin, platelets) not including PRBCs.

Percentage of Participants Who Had Hemostatic Efficacy for Visible or Non-visible Musculoskeletal BleedingAt 3 and 6 hours after the start of infusion

Hemostatic efficacy was determined by a blinded independent board as excellent, good, or poor/none, based on prespecified definitions. Assessments of visible or non-visible musculoskeletal bleeding were made at 3 and 6 hours after the start of infusion. Hemostatic efficacy was the binary endpoint of effective or non-effective hemostasis, where 'effective' was a hemostatic efficacy rating of "excellent" or "good," and 'non-effective' was a hemostatic efficacy rating of "poor/none".

Incremental in Vivo Recovery (IVR) (Response) of Factors II, VII, IX, and X, Protein C, and Protein S for BeriplexBefore infusion and up to 3 h after the start of infusion

The incremental IVR \[(IU/dL)/(IU/kg)\] was calculated as follows: (IU/dL activity rise in plasma)/(IU/kg body weight infused) = \[maximum increase in component plasma level within 3 hours compared to pre-infusion (IU/dL)\]/{\[exact dose of component in drug administered (IU)\]/\[body weight (kg)\]}.

Percentage of Participants With INR Correction at Various Times After the Start of InfusionFrom the start of infusion until INR correction; calculated at 0.5, 1, 3, 6, 12, and 24 h after the start of infusion.

The time taken from the start of infusion to INR correction (defined as an INR ≤ 1.3) was recorded. The percentage of participants with INR correction was calculated at 0.5, 1, 3, 6, 12, and 24 h after the start of infusion.

Transfusion of Red Blood CellsFrom the start of infusion until 24 h after the start of infusion

Red blood cells were packed red blood cells (PRBCs).

Overall Treatment-emergent Adverse Events (TEAEs)From the start of infusion up to the allowed time window of the Day 10 visit for non-serious AEs and from the start of infusion up to the allowed time window of the Day 45 visit for SAEs.

Number of participants with TEAEs. Treatment-related AEs were defined as events whose relationship to study treatment was definitely related, probably related, or possibly related in the opinion of the investigator. AEs with missing relationship were considered related to treatment. Serious TEAEs were treatment-emergent SAEs. Deaths reported up to and including Day 45; one additional Beriplex death occurred after Day 45.

Trial Locations

Locations (5)

Study Site

🇺🇦

Vinnytsa, Ukraine

Study Site 1

🇷🇺

St. Petersburg, Russian Federation

Study Site 4

🇧🇬

Sofia, Bulgaria

Study Site 2

🇷🇺

St. Petersburg, Russian Federation

Study Site 3

🇷🇴

Bucharest, Romania

© Copyright 2025. All Rights Reserved by MedPath