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Multiple Dose Study Of PF-05231023 In Adult Subjects Who Have Poor Lipid Control With And Without Type 2 Diabetes Mellitus

Phase 1
Completed
Conditions
Diabetes Melliuts, Type 2
Interventions
Drug: 100 mg PF-05231023
Drug: 150 mg PF-05231023
Other: Placebo
Drug: 25 mg PF-05231023
Drug: 50 mg PF-05231023
Registration Number
NCT01673178
Lead Sponsor
Pfizer
Brief Summary

This is a trial in obese subjects who have poor lipid control with and without Type 2 diabetes mellitus to study the safety, tolerability and pharmacokinetics of multiple doses of PF-05231023

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
107
Inclusion Criteria
  • Male and female subjects of non-childbearing potential between the ages of 30 and 70 years with and without a diagnosis of Type 2 diabetes mellitus (according to the American Diabetes Association guidelines).
  • Subjects with poor lipid control as confirmed by laboratory tests.
  • BMI of 30 to 40 Kg/m2 and a total body weight of >50 kg (110 lbs).
Exclusion Criteria
  • Evidence or history of clinically significant hematological, renal, endocrine, pulmonary, gastrointestinal, cardiovascular, hepatic, psychiatric, neurologic, or allergic disease (including drug allergies, but excluding asymptomatic, seasonal allergies at time of dosing).
  • Levels of blood enzymes indicating pancreatitis or elevated liver function enzymes outside of the laboratory's reference range as confirmed by laboratory tests.
  • Subjects with Type 1 Diabetes Mellitus.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
100 mg100 mg PF-05231023-
150 mg150 mg PF-05231023-
Placebo ArmPlacebo-
25 mg25 mg PF-05231023-
50 mg50 mg PF-05231023-
Primary Outcome Measures
NameTimeMethod
Thyroid Stimulating Hormone (TSH) Level at Day 1Day 1
Thyroid Stimulating Hormone (TSH) Level at Day 39Day 39
Phosphate Level at BaselineBaseline
Percent Change From Baseline in Blood Osteocalcin and Bone-Specific Alkaline Phosphatase Levels at Day 49Baseline, Day 49
Number of Participants With Clinically Significant Vital Sign AbnormalitiesBaseline up to Day 49

Criteria for clinically significant vital signs abnormalities included supine/sitting pulse rate of \<40 beats per minute (bpm) or \>120 bpm, supine systolic blood pressure (SBP) of \<90 millimeter of mercury (mmHg), \>=30 mmHg maximum increase and decrease from baseline in same posture, supine diastolic blood pressure (DBP) of \<50 mmHg; \>=20 mmHg maximum increase and decrease from baseline in same posture.

Number of Participants With Clinically Significant Electrocardiogram FindingsBaseline up to Day 49

Clinically significant ECG findings included PR interval \>=300 milliseconds (msec) or \>=25 percent (%) increase from baseline (if baseline PR interval \>200 msec) or \>=50% increase (if baseline PR interval less than or equal to \[\<=\] 200 msec); QRS interval \>=140 msec or \>=50% increase from baseline; QT interval \>=500 msec, corrected QT interval based on Fridericia's formula (QTcF) 450 to \<480 msec, 480 to \<500 msec, \>=500 msec or \>=30 msec but \<60 msec increase from baseline or \>=60 msec increase from baseline.

Change From Baseline in Phosphate Level at Day 25Baseline, Day 25
Percent Change From Baseline in Serum N-terminal Propeptides of Type 1 Collagen (PINP) and C-Telopeptide Cross-Linking of Type 1 Collagen (CTX) Levels at Day 25Baseline, Day 25
Percent Change From Baseline in Blood Osteocalcin and Bone-Specific Alkaline Phosphatase Levels at Day 25Baseline, Day 25
Average Urinary Calcium and Phosphate Levels Over 24 Hours at BaselineBaseline
Change From Baseline in Average Urinary Calcium and Phosphate Levels Over 24 Hours at Day 24Day 24
Blood Osteocalcin and Bone-Specific Alkaline Phosphatase Levels at BaselineBaseline
Number of Participants With Abnormal Physical ExaminationsBaseline up to Day 49

Physical examination included general examination and examination of head, ears, eyes, nose, mouth, throat, neck, abdomen, skin, heart, lungs, lymph nodes, and gastrointestinal and musculoskeletal and neurological system.

Thyroid Stimulating Hormone (TSH) Level at BaselineBaseline

Results are reported in micro international units per milliliter (mcIU/mL).

Change From Baseline in Phosphate Level at Day 15Baseline, Day 15
Tartrate-resistant Acid Phosphatase Isoform 5b (TRAP 5b) Levels at BaselineBaseline
Percent Change From Baseline in Tartrate-resistant Acid Phosphatase Isoform 5b (TRAP 5b) Levels at Day 49Day 49
Number of Participants With Treatment-Emergent Adverse Events (AEs) and Serious Adverse Events (SAEs)Baseline up to 28 days after last dose

An AE was any untoward medical occurrence in a participant who received study drug without regard to possibility of causal relationship. An SAE was an AE resulting in any of the following outcomes or deemed significant for any other reason: death; initial or prolonged inpatient hospitalization; life-threatening experience (immediate risk of dying); persistent or significant disability/incapacity; congenital anomaly. Treatment-emergent events were between first dose of study drug and up to 28 days after last dose that were absent before treatment or that worsened relative to pre-treatment state.

Number of Participants With Laboratory AbnormalitiesBaseline up to Day 49

Criteria for laboratory test abnormality: Hematology (hemoglobin, hematocrit, red blood corpuscles \[RBC\] count: less than \[\<\]0.8\*lower limit of normal \[LLN\], platelets: \<0.5\*LLN/greater than \[\>\]1.75\*upper limit of normal \[ULN\], leukocytes: \<0.6\*LLN or \>1.5\*ULN, lymphocytes, total neutrophils: \<0.8\*LLN or \>1.2\*ULN, basophils, eosinophil: \<0.8\*LLN, monocytes: \>1.2\*ULN); Liver Function (aspartate aminotransferase, alanine aminotransferase, alkaline phosphatase: \>0.3\*ULN, total protein, albumin: \<0.8\*LLN or \>1.2\*ULN); total bilirubin, direct bilirubin, indirect bilirubin: \>1.5\*ULN; Renal Function (blood urea nitrogen, creatinine: \>1.3\*ULN, uric acid: \>1.2\*ULN); Electrolytes (sodium: \<0.95\*LLN or \>1.05\*ULN, potassium, chloride, calcium, bicarbonate: \<0.9\*LLN or \>1.1\*ULN; creatine kinase: \>2.0\*ULN; glucose fasting: \<0.6\*LLN or \>1.5\*ULN, urine white blood corpuscles \[WBC\] and RBC: greater than or equal to (\>=) 20/High Power Field \[HPF\]).

Percent Change From Baseline in Tartrate-resistant Acid Phosphatase Isoform 5b (TRAP 5b) Levels at Day 25Baseline, Day 25
Thyroid Stimulating Hormone (TSH) Level at Day 25Day 25
Thyroid Stimulating Hormone (TSH) Level at Day 49Day 49
Creatine Phosphokinase (CPK) Level at BaselineBaseline
Change From Baseline in Creatine Phosphokinase (CPK) Level at Day 15Baseline, Day 15
Change From Baseline in Creatine Phosphokinase (CPK) Level at Day 49Baseline, Day 49
Serum N-terminal Propeptides of Type 1 Collagen (PINP) and C-Telopeptide Cross-Linking of Type 1 Collagen (CTX) Levels at BaselineBaseline
Percent Change From Baseline in Serum N-terminal Propeptides of Type 1 Collagen (PINP) and C-Telopeptide Cross-Linking of Type 1 Collagen (CTX) Levels at Day 39Baseline, Day 39
Change From Baseline in Phosphate Level at Day 8Baseline, Day 8
Change From Baseline in Creatine Phosphokinase (CPK) Level at Day 8Baseline, Day 8
Percent Change From Baseline Serum N-terminal Propeptides of Type 1 Collagen (PINP) and C-Telopeptide Cross-Linking of Type 1 Collagen (CTX) Levels at Day 49Baseline, Day 49
Percent Change From Baseline in Blood Osteocalcin and Bone-Specific Alkaline Phosphatase Levels at Day 39Baseline, Day 39
Number of Participants With Anti-PF-05231023 Antibodies and Neutralizing Antibodies at Day 39Day 39

Anti-PF-05231023 antibodies and neutralizing antibodies were analyzed only for participants who received PF-05231023 as per planned analysis. One sample at Day 39 was inadvertently tested for neutralizing antibody even though the corresponding anti-PF-05231023 antibody was negative.

Number of Participants With Anti-PF-05231023 Antibodies and Neutralizing Antibodies at Day 49Day 49
Change From Baseline in Phosphate Level at Day 49Baseline, Day 49
Change From Baseline in Creatine Phosphokinase (CPK) Level at Day 25Baseline, Day 25
Percent Change From Baseline in Tartrate-resistant Acid Phosphatase Isoform 5b (TRAP 5b) Levels at Day 39Baseline, Day 39
Number of Participants With Anti-PF-05231023 Antibodies and Neutralizing Antibodies at Day 1Day 1

Anti-PF-05231023 antibodies and neutralizing antibodies were analyzed only for participants who received PF-05231023 as per planned analysis. One sample at Day 1 was inadvertently tested for neutralizing antibody even though the corresponding anti-PF-05231023 antibody was negative.

Secondary Outcome Measures
NameTimeMethod
Area Under the Curve From Time Zero to End of Dosing Interval (AUCtau) of PF-05231023 After Single Dose0 (pre-dose), 0.5 (end of infusion), 1, 2.5, 3.5, 5.5, 9.5, 11.5 hours after start of infusion on Day 1, Day 4, 0 hours (pre-dose) on Day 8

AUCtau was calculated for the intact C-terminus and N-terminus PF-05231023 from the concentration-time data using standard non-compartmental method. Only participants who received PF-05231023 were to be analyzed for this outcome measure.

Minimum Observed Plasma Trough Concentration (Cmin) of PF-05231023 After Last Dose0 (pre-dose), 0.5 (end of infusion), 1, 2.5, 3.5, 4.5 hours after start of infusion on Day 22, Day 24, 25, 29, 39, 49

Cmin was calculated for the intact C-terminus and N-terminus PF-05231023 from the concentration-time data using standard non-compartmental method. Only participants who received PF-05231023 were to be analyzed for this outcome measure.

Time to Reach Maximum Observed Plasma Concentration (Tmax) of PF-05231023 After Single Dose0 (pre-dose), 0.5 (end of infusion), 1, 2.5, 3.5, 5.5, 9.5, 11.5 hours after start of infusion on Day 1, Day 4, 0 hour (pre-dose) on Day 8

Tmax was calculated for the intact C-terminus and N-terminus PF-05231023 from the concentration-time data using standard non-compartmental method. Only participants who received PF-05231023 were to be analyzed for this outcome measure.

Area Under the Curve From Time Zero to End of Dosing Interval (AUCtau) of PF-05231023 After Last Dose0 (pre-dose), 0.5 (end of infusion), 1, 2.5, 3.5, 4.5 hours after start of infusion on Day 22, Day 24, 25, 29

AUCtau was calculated for the intact C-terminus and N-terminus PF-05231023 from the concentration-time data using standard non-compartmental method. Only participants who received PF-05231023 were to be analyzed for this outcome measure.

Apparent Clearance (CL) of PF-052310230 (pre-dose), 0.5 (end of infusion), 1, 2.5, 3.5, 4.5 hours after start of infusion on Day 22, Day 24, 25, 29, 39, 49

CL is a quantitative measure of the rate at which a drug substance is removed from the body. CL was calculated for the intact C-terminus and N-terminus PF-05231023 from the concentration-time data using standard non-compartmental method. Only participants who received PF-05231023 were to be analyzed for this outcome measure.

Maximum Observed Plasma Concentration (Cmax) of PF-05231023 After Single Dose0 (pre-dose), 0.5 (end of infusion), 1, 2.5, 3.5, 5.5, 9.5, 11.5 hours after start of infusion on Day 1, Day 4, 0 hour (pre-dose) on Day 8

Cmax was calculated for the intact C-terminus and N-terminus PF-05231023 from the concentration-time data using standard non-compartmental method. Only participants who received PF-05231023 were to be analyzed for this outcome measure.

Time to Reach Maximum Observed Plasma Concentration (Tmax) of PF-05231023 After Last Dose0 (pre-dose), 0.5 (end of infusion), 1, 2.5, 3.5, 4.5 hours after start of infusion on Day 22, Day 24, 25, 29, 39, 49

Tmax was calculated for the intact C-terminus and N-terminus PF-05231023 from the concentration-time data using standard non-compartmental method. Only participants who received PF-05231023 were to be analyzed for this outcome measure.

Maximum Observed Plasma Concentration (Cmax) of PF-05231023 After Last Dose0 (pre-dose), 0.5 (end of infusion), 1, 2.5, 3.5, 4.5 hours after start of infusion on Day 22, Day 24, 25, 29, 39, 49

Cmax was calculated for the intact C-terminus and N-terminus PF-05231023 from the concentration-time data using standard non-compartmental method. Only participants who received PF-05231023 were to be analyzed for this outcome measure.

Accumulation Ratio for Area Under the Curve From Time Zero to End of Dosing Interval (Rac) of PF-052310230 (pre-dose), 0.5 (end of infusion ), 1, 2.5, 3.5, 5.5, 9.5, 11.5 hours after start of infusion on Day 1; Day 4, 0 hour (pre-dose) on Day 8; 0 (pre-dose), 0.5 (end of infusion), 1, 2.5, 3.5, 4.5 hours after start of infusion on Day 22; Day 24, 25, 29

Rac was obtained from AUCtau after last dose (Day 22) divided by AUCtau after single dose (Day 1). Rac was calculated for the intact C-terminus and N-terminus PF-05231023 from the concentration-time data using standard non-compartmental method. Only participants who received PF-05231023 were to be analyzed for this outcome measure.

Accumulation Ratio for Maximum Observed Plasma Concentration (Rac,Cmax) of PF-052310230 (pre-dose),0.5(end of infusion), 1, 2.5, 3.5, 5.5, 9.5, 11.5 hours after start of infusion on Day 1; Day 4, 0 hour (pre-dose) on Day 8; 0 (pre-dose), 0.5 (end of infusion), 1, 2.5, 3.5, 4.5 hours after start of infusion on Day 22; Day 24,25,29,39,49

Rac was obtained from AUCtau after last dose (Day 22) divided by AUCtau after single dose (Day 1). Rac was calculated for the intact C-terminus and N-terminus PF-05231023 from the concentration-time data using standard non-compartmental method. Only participants who received PF-05231023 were to be analyzed for this outcome measure.

Average Plasma Concentration (Cav ) of PF-05231023 After the Last Dose0 (pre-dose), 0.5 (end of infusion), 1, 2.5, 3.5, 4.5 hours after start of infusion on Day 22, Day 24, 25, 29, 39, 49

Cav was calculated for the intact C-terminus and N-terminus PF-05231023 from the concentration-time data using standard non-compartmental method. Only participants who received PF-05231023 were to be analyzed for this outcome measure.

Plasma Decay Half-Life (t1/2) of PF-052310230 (pre-dose), 0.5 (end of infusion), 1, 2.5, 3.5, 4.5 hours after start of infusion on Day 22, Day 24, 25, 29, 39, 49

Plasma decay half-life is the time measured for the plasma concentration to decrease by one half. Half-Life was calculated for the intact C-terminus and N-terminus PF-05231023 from the concentration-time data using standard non-compartmental method. Only participants who received PF-05231023 were to be analyzed for this outcome measure.

Trial Locations

Locations (17)

Anaheim Clinical Trials, LLC

🇺🇸

Anaheim, California, United States

Profil Institute for Clinical Research, Inc.

🇺🇸

Chula Vista, California, United States

Diablo Clinical Research, Inc.

🇺🇸

Walnut Creek, California, United States

Avail Clinical Research, LLC

🇺🇸

DeLand, Florida, United States

Elite Research Institute

🇺🇸

Miami, Florida, United States

MRA Clinical Research, LLC

🇺🇸

South Miami, Florida, United States

Miami Research Associates, Inc.

🇺🇸

South Miami, Florida, United States

Central Kentucky Research Associates, Inc.

🇺🇸

Lexington, Kentucky, United States

L-MARC Research Center

🇺🇸

Louisville, Kentucky, United States

Prism Research

🇺🇸

Saint Paul, Minnesota, United States

Carolina Phase 1 Research

🇺🇸

Raleigh, North Carolina, United States

Wake Internal Medicine Consultants

🇺🇸

Raleigh, North Carolina, United States

Medpace Clinical Pharmacology Unit

🇺🇸

Cincinnati, Ohio, United States

Community Research

🇺🇸

Cincinnati, Ohio, United States

Mercy Hospital Pharmacy

🇺🇸

Cincinnati, Ohio, United States

Covance Clinical Research Unit

🇺🇸

Dallas, Texas, United States

High Point Clinical Trials Center, LLC

🇺🇸

High Point, North Carolina, United States

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