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Pharmacodynamics, Safety/Tolerability and Efficacy of Topical Omiganan in Patients With uVIN

Phase 2
Completed
Conditions
Usual Type Vulval Intraepithelial Neoplasia (uVIN)
Interventions
Drug: Vehicle topical gel
Registration Number
NCT02596074
Lead Sponsor
Maruho Co., Ltd.
Brief Summary

To assess the pharmacodynamics, safety/tolerability and efficacy of topical Omiganan (CLS001) in patients with usual type vulvar intraepithelial neoplasia (uVIN).

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
Female
Target Recruitment
12
Inclusion Criteria
  1. Women ≥ 18 years

  2. Biopsy proven uVIN, biopsies to have been taken within the last three months

  3. Written informed consent to participate in the trial

  4. At least one lesion that can be accurately measured (using RECIST criteria)

    • in at least one dimension with longest diameter ≥ 20mm
    • OR in two perpendicular dimensions that when multiplied together give a surface area of ≥ 120mm2 (e.g. 15mm x 8mm or 12mm x 10mm)
    • This is to ensure that 4x4mm biopsies can be performed on this lesion.
Exclusion Criteria
  1. Has any concomitant disease or significant medical conditions that would, in the opinion of the Investigator, potentially compromise the safety or compliance of the patient or may preclude the patient's successful completion of the clinical trial.
  2. Clinically significant abnormalities, as judged by the Investigator, in laboratory test results (including hepatic and renal panels, complete blood count, chemistry panel and urinalysis) or ECG. In the case of uncertain or questionable results, tests performed during screening may be repeated before randomization to confirm eligibility or judged to be clinically irrelevant for healthy subjects.
  3. Indication of a current active infectious disease of the vulva, other than HPV
  4. Pregnant, breast feeding or trying to conceive
  5. Active treatment for uVIN (i.e. surgical excision, lasertherapy, imiquimod, photodynamic therapy) within the previous month
  6. Patients receiving immunosuppressive therapy
  7. HIV positive or transplant patients
  8. Any condition that in the opinion of the investigator could interfere with the conduct of the study

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Omiganan (CLS001)Omiganan (CLS001) topical gelCLS001 topical gel, 2.5%
VehicleVehicle topical gelVehicle topical gel
Primary Outcome Measures
NameTimeMethod
Pharmacodynamics (HPV Viral Load Assessment)24 Weeks

Assessment of target lesions by quantitative PCR including HPV genotyping in swabs and biopsies

Pharmacodynamics (Local Immunity Status)24 Weeks

Histological changes in immune cells in the mucosa/submucosa

Clinical Assessment (Lesions by RECIST)24 Weeks

Efficacy assessment of lesions by RECIST

Clinical Assessment (Sum of the longest diameter (SLD))24 Weeks

Efficacy assessment of the sum of the longest diameter (SLD))

Clinical Assessment (Percent clearance of Lesions)24 Weeks

Efficacy assessment of percent clearance of lesions

Clinical Assessment (Histology)24 Weeks

Efficacy assessment of the histology (regression of uVIN to no dysplasia)

Secondary Outcome Measures
NameTimeMethod
Safety and Tolerability (Adverse Events)48 Weeks

Adverse Events will be collected throughout the study

Safety and Tolerability (Laboratory Safety Testing)48 Weeks

Laboratory Samples will be collected throughout the study

Safety and Tolerability (12-Lead ECGs)48 Weeks

12-Lead ECGs will be performed throughout the study

Safety and Tolerability (Vital Signs)48 Weeks

Vital Signs will be collected throughout the study

Pharmacokinetics (Area Under the Curve)12 Weeks

AUC will be computed

Pharmacokinetics (Maximum Plasma Concentration)12 Weeks

Cmax will be determined

Pharmacokinetics (Tmax)12 Weeks

Tmax will be determined

Trial Locations

Locations (1)

LUMC/Centre for Human Drug Research

🇳🇱

Leiden, Netherlands

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