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Pharmacokinetics Study of VALTOCO® in Pediatric Subjects With Epilepsy

Phase 1
Completed
Conditions
Epilepsy
Interventions
Registration Number
NCT05076838
Lead Sponsor
Neurelis, Inc.
Brief Summary

This is a Phase 1/2a, open-label, single-dose, PK study of VALTOCO with open-label safety period in pediatric epilepsy subjects age 2 to 5 years.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
35
Inclusion Criteria
  • Subject has a clinical diagnosis of epilepsy and, in the opinion of the Investigator, may need benzodiazepine intervention for seizure control.
  • Subjects having either partial or generalized epilepsy with motor seizures or seizures with clear alteration of awareness, for which rescue medications have been used at least once in the last 3 months or in the opinion of the investigator, may need a benzodiazepine intervention for seizure control 1-2 times every 3 months on average.
Exclusion Criteria
  • Subjects whose body weight are < 6 kg or > 33 kg.
  • Subject is undergoing intracranial electroencephalogram (EEG) monitoring.
  • In the opinion of the investigator, a history of clinically significant medical history that would jeopardize the safety of the subject or impact the validity of the study results (such as significant gastrointestinal, renal, nasal polyps or any nasal passage abnormality that could interfere with nasal spray administration.
  • Subject has had significant traumatic injury, major surgery or open biopsy within 30 days prior to study screening.
  • Participation in a clinical trial within 30 days prior to the first dose of study drug.
  • Inadequate or difficult venous access that may jeopardize the quality or timing of the PK samples.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Valtoco In Pediatric Subjects with EpilepsyDiazepam Nasal Spray [Valtoco]5 mg, 10 mg, or 15 mg dose of intranasal VALTOCO will be administered based on the subject's body weight.
Primary Outcome Measures
NameTimeMethod
Maximum Plasma Concentration (Cmax) of diazepam after intranasal VALTOCO administered to subjects with epilepsy 2 to 5 years of age0-6 hours
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (13)

Duke University Hospital

🇺🇸

Durham, North Carolina, United States

Center for Rare Neurological Diseases

🇺🇸

Norcross, Georgia, United States

Boston Children's Health Physicians

🇺🇸

Hawthorne, New York, United States

Le Bonheur Children's Hospital

🇺🇸

Memphis, Tennessee, United States

Children's Hospital of the King's Daughters

🇺🇸

Norfolk, Virginia, United States

Massachusetts General Hospital

🇺🇸

Boston, Massachusetts, United States

UT Southwestern Medical Center

🇺🇸

Dallas, Texas, United States

Northwest Florida Clinical Research Group, LLC.

🇺🇸

Gulf Breeze, Florida, United States

AdventHealth Research Institute

🇺🇸

Orlando, Florida, United States

Nicklaus Children's Hospital

🇺🇸

Miami, Florida, United States

Northeast Regional Epilepsy Group

🇺🇸

Hackensack, New Jersey, United States

University of Missouri Women & Children's Hospital

🇺🇸

Columbia, Missouri, United States

University of Rochester

🇺🇸

Rochester, New York, United States

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