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Study of AEE788 in Patients With Recurrent/Relapse Glioblastoma Multiforme (GBM)

Phase 1
Completed
Conditions
Glioblastoma Multiforme
Interventions
Registration Number
NCT00116376
Lead Sponsor
Novartis Pharmaceuticals
Brief Summary

AEE788 is an orally active, reversible, small-molecule, multi-targeted kinase inhibitor with potent inhibitory activity against the ErbB and VEGF receptor family of tyrosine kinases. It has an IC50 of less than 100 nM against p-EGFR, p-ErbB2, and p-KDR (VEGFR2). This study will assess the safety, pharmacokinetic/pharmacodynamic (PK/PD) profiles and clinical activity of AEE788 in a recurrent GBM population.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
64
Inclusion Criteria
  • Histologically confirmed GBM in first or second recurrence or relapse
  • Adequate hematologic, hepatic and renal function
  • Age ≥ 18 years
  • Karnofsky performance status score ≥ 70%
  • Life expectancy ≥ 12 weeks
Exclusion Criteria
  • Peripheral neuropathy > grade 1
  • Diarrhea > grade 1
  • Gastrointestinal dysfunction
  • Compromised cardiac function
  • Concurrent severe and/or uncontrolled medical conditions

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
AEE788 + non EIACDAEE788-
AEE788 + EIACDAEE788-
Primary Outcome Measures
NameTimeMethod
Maximum tolerated dose2 years
Dose limiting toxicity2 years
Secondary Outcome Measures
NameTimeMethod
Safety, tolerability, pharmacokinetic profiles, change in plasma markers of angiogenesis, tumor PK levels2 years

Trial Locations

Locations (4)

University of California at Los Angeles

🇺🇸

Los Angeles, California, United States

The Brain Tumor Center at Duke, Duke University Medical Center

🇺🇸

Box 3624 DUMC, Trent Drive, Durham, North Carolina, United States

University of Texas, MD Anderson Cancer Center

🇺🇸

Houston, Texas, United States

University of California, San Francisco

🇺🇸

San Francisco, California, United States

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