EUCTR2019-004645-32-GB进行中（未招募）1 期
A Multicentre, Long-term, Follow-up Study to Investigate the Safety and Durability of Response Following Dosing of an Adeno-associated Viral Vector (FLT190) in Subjects with Fabry Disease - Marvel 2
Freeline Therapeutics Ltd0 个研究点目标入组 15 人开始时间: 2019年12月31日最近更新:
适应症
试验速览
- 阶段
- 1 期
- 状态
- 进行中（未招募）
- 发起方
- 入组人数
- 15
研究概览
简要总结
暂无简介。
研究设计
- 研究类型
- Interventional clinical trial of medicinal product
入排标准
- 性别
- Male
入选标准
- •(i) Subjects who have previously received FLT190 (including those who may have required recommencement/initiation of ERT/PCT).
- •(ii) Subjects able to give full informed consent and able to comply with all requirements of the study including long-term follow-up for 60 months (5 years) post-treatment.
- •Are the trial subjects under 18? no
- •Number of subjects for this age range:
- •F.1.2 Adults (18-64 years) yes
- •F.1.2.1 Number of subjects for this age range 13
- •F.1.3 Elderly (>=65 years) yes
- •F.1.3.1 Number of subjects for this age range 2
排除标准
- •Subjects who do not meet the inclusion criteria will be excluded
研究者
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