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A Phase III double blind, randomised, placebo-controlled study of the efficacy, safety and tolerability of idebenone in the treatment of Friedreich's Ataxia patients. - MICONOS

Phase 1
Conditions
Friedreich's Ataxia
Registration Number
EUCTR2005-004083-22-GB
Lead Sponsor
Santhera Pharmaceuticals (Switzerland) Ltd
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
ot Recruiting
Sex
All
Target Recruitment
204
Inclusion Criteria

•Documented diagnosis of FRDA with confirmed FRDA mutations
•Patients 8 years of age or older at time of enrolment
•Patients with body weight = 25kg
•Patients who in the opinion of the investigator are able to comply with the requirements of the study
•Negative urine pregnancy test at screening (women of childbearing potential)

Are the trial subjects under 18? yes
Number of subjects for this age range:
F.1.2 Adults (18-64 years) yes
F.1.2.1 Number of subjects for this age range
F.1.3 Elderly (>=65 years) no
F.1.3.1 Number of subjects for this age range

Exclusion Criteria

•Treatment with idebenone or coenyzme Q within 1 month
•Pregnancy and/or breast-feeding
•Clinically significant abnormalities of clinical haematology or biochemistry including, but not limited to, elevations greater than 1.5 times the upper limit of normal of SGOT, SGPT or creatinine
•Past or present history of abuse of drugs or alcohol

Study & Design

Study Type
Interventional clinical trial of medicinal product
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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