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Induction Chemotherapy Before or After Preoperative Chemoradiotherapy and Surgery for Locally Advanced Rectal Cancer

Phase 2
Completed
Conditions
Rectal Neoplasms
Rectal Cancer Stage II
Rectal Cancer Stage III
Interventions
Drug: Induction Chemotherapy arm A
Radiation: Radiation arm B
Radiation: Radiation arm A
Drug: Chemotherapy arm B
Procedure: Surgery
Registration Number
NCT02363374
Lead Sponsor
Prof. Dr. med. Claus Rödel
Brief Summary

Preoperative 5-FU-based (5-fluorouracil) chemoradiotherapy (CRT), total mesorectal excision surgery, and 4 cycles of adjuvant 5-FU - as established by CAO/ARO/AIO-94 - is at present a standard of care for patients with locally advanced rectal cancer (UICC stage II and III). The phase III German CAO/ARO/AIO-04 trial showed, that the addition of oxaliplatin increased treatment efficacy in terms of early secondary efficacy endpoints (e.g. the pCR-rate). With a median follow-up of 50 months, the primary endpoint of this trial - disease free survival - was significantly improved in the oxaliplatin-containing treatment arm (3-year disease-free survival (DFS) 71.2% versus 75.9%, hazard ratio (HR) 0.79, 95% confidence interval (CI) 0.64-0.98, p=0.03). The hereby proposed randomized phase II trial CAO/ARO/AIO-12 aims at finding novel and innovative aspects of rectal cancer treatment, and will thus provide important information for defining the experimental arm in the upcoming large scale trial of the group. Compared to the current standard, in both study arms, the sequence of the three treatment modalities is modified, placing the chemotherapy block before surgery. The pre-operative sequence of chemotherapy -\> chemoradiotherapy (arm A) has been shown to be feasible with no early tumor progression prior to definitive surgical resection in a small randomized phase II study from Spain. The sequence chemoradiotherapy -\> chemotherapy (arm B) may be beneficial according to response kinetics considerations, and by maintaining a highly effective local treatment in the first place. Both approaches could avoid the problem of major compliance problems with post-operative adjuvant chemotherapy. CAO/ARO/AIO: German Rectal Cancer Study Group

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
311
Inclusion Criteria
  • Male and female patients with histologically confirmed diagnosis of rectal cancer localised 0 - 12 cm from the anocutaneous line as measured by rigid rectoscopy (i.e. lower and middle third of the rectum)
  • Staging requirements: High-resolution, thin-sliced (i.e. 3mm) magnetic resonance imaging (MRI) of the pelvis is the mandatory local staging procedure.
  • MRI-defined inclusion criteria: presence of at least one of the following high risk conditions: any cT3 (clinical stage tumor-3) if the distal extent of the tumor is < 6 cm from anocutaneous line or cT3 in the middle third of the rectum (≥ 6-12 cm) with MRI evidence of extramural tumor spread into the mesorectal fat of more than 5 mm (>cT3b), or resectable cT4 tumors, or any clear cN+ (clinical staging nodes) based on MRI-criteria
  • Trans-rectal endoscopic ultrasound (EUS) is additionally used when MRI is not definitive to exclude early cT1/T2 disease in the lower third of the rectum or early cT3a/b tumors in the middle third of the rectum.
  • Spiral-CT of the abdomen and chest to exclude distant metastases.
  • Aged at least 18 years. No upper age limit.
  • WHO/ECOG (World Health Organisation/Eastern Cooperative Oncology Group) Performance Status ≤ 1
  • Adequate haematological, hepatic, renal and metabolic function parameters: Leukocytes ≥ 3.000/mm^3, absolute neutrophil count (ANC) ≥ 1.500/mm^3, platelets ≥100.000/mm^3, Hb > 9 g/dl; Serum creatinine ≤ 1.5 x upper limit of normal; Bilirubin ≤ 2.0 mg/dl, serum glutamic-oxaloacetic transaminase (SGOT), serum glutamic-pyruvic transaminase (SGPT), and alkaline phosphatase (AP) ≤ 3 x upper limit of normal
  • Informed consent of the patient
Exclusion Criteria
  • Lower border of the tumor localised more than 12 cm from the anocutaneous line as measured by rigid rectoscopy
  • Distant metastases (to be excluded by CT scan of the thorax and abdomen)
  • Prior antineoplastic therapy for rectal cancer
  • Prior radiotherapy of the pelvic region
  • Major surgery within the last 4 weeks prior to inclusion
  • Subject pregnant or breast feeding, or planning to become pregnant within 6 months after the end of treatment.
  • Subject (male or female) is not willing to use highly effective methods of contraception (per institutional standard) during treatment and for 6 months (male or female) after the end of treatment (adequate: oral contraceptives, intrauterine device or barrier method in conjunction with spermicidal jelly).
  • On-treatment participation in a clinical study in the period 30 days prior to inclusion
  • Previous or current drug abuse
  • Concomitant other antineoplastic therapy
  • Serious concurrent diseases, including neurologic or psychiatric disorders (incl. dementia and uncontrolled seizures), active, uncontrolled infections, active, disseminated coagulation disorder
  • Clinically significant cardiovascular disease in (incl. myocardial infarction, unstable angina, symptomatic congestive heart failure, serious uncontrolled cardiac arrhythmia) ≤ 6 months before enrolment
  • Chronic diarrhea (> grade 1 according NCI CTCAE)
  • Prior or concurrent malignancy ≤ 3 years prior to enrolment in study (Exception: non-melanoma skin cancer or cervical carcinoma FIGO (International Federation of Gynecology and Obstetrics) stage 0-1), if the patient is continuously disease-free
  • Known allergic reactions on study medication
  • Known dihydropyrimidine dehydrogenase deficiency
  • Psychological, familial, sociological or geographical condition potentially hampering compliance with the study protocol and follow-up schedule (these conditions should be discussed with the patient before registration in the trial)

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Arm A: Chemotherapy -> ChemoradiotherapyInduction Chemotherapy arm AInduction chemotherapy followed by chemoradiotherapy before surgery
Arm A: Chemotherapy -> ChemoradiotherapyRadiation arm AInduction chemotherapy followed by chemoradiotherapy before surgery
Arm A: Chemotherapy -> ChemoradiotherapySurgeryInduction chemotherapy followed by chemoradiotherapy before surgery
Arm B: Chemoradiotherapy -> ChemotherapyRadiation arm BCombined chemoradiotherapy followed by three cycles chemotherapy before surgery
Arm B: Chemoradiotherapy -> ChemotherapyChemotherapy arm BCombined chemoradiotherapy followed by three cycles chemotherapy before surgery
Arm B: Chemoradiotherapy -> ChemotherapySurgeryCombined chemoradiotherapy followed by three cycles chemotherapy before surgery
Primary Outcome Measures
NameTimeMethod
Number of patients with pathological complete response (pCR), i.e. ypT0N0.123 +30 days

Efficacy (pCR) of induction chemotherapy followed by chemoradiotherapy, or the other way round, before surgery in patients with locally advanced rectal cancer.

Secondary Outcome Measures
NameTimeMethod
Pathological staging123 +14 days
Safety of the respective combination sequences by Toxicity assessment according to NCI CTCAE V.4.05 years
Surgical morbidity123 +30 days
Surgical complications123 +30 days
Relapse-free survival (local / distant / overall)5 years
Tumor downstaging assessed by ypTNM (neoadjuvant pathological staging tumor nodes metastasis) findings in relation to initial cTNM (clinical stage tumor nodes metastasis)123 +14 days
Tumor regression grading according to Dworak123 +14 days
R0 resection rate; negative circumferential resection rate123 +14 days
Rate of sphincter-sparing surgery123 +14 days
Overall survival5 years

Trial Locations

Locations (10)

HELIOS Park-Klinikum Leipzig

🇩🇪

Leipzig, Germany

RWTH Aachen

🇩🇪

Aachen, Germany

University Clinic

🇩🇪

Wuerzburg, Germany

University Hospital Frankfurt Goethe University

🇩🇪

Frankfurt, Germany

Hospital Miria Hilf

🇩🇪

Moenchengladbach, Germany

Hospital Barmherziger Brueder

🇩🇪

Regensburg, Germany

Pius Hospital Oldenburg

🇩🇪

Oldenburg, Germany

Clinic for Radiotherapy

🇩🇪

Chemnitz, Germany

Diacura Clinic for Radiotherapy

🇩🇪

Coburg, Germany

Internist Practice

🇩🇪

Dresden, Germany

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