Please refer to ClinicalTrials.gov : NCT03070119.
Phase 3
Completed
- Conditions
- amyotrophic lateral sclerosis (ALS) with a confirmed mutation in the human superoxide dismutase 1 (SOD1) gene
- Registration Number
- JPRN-jRCT2080225019
- Lead Sponsor
- Biogen Japan Ltd.
- Brief Summary
Not available
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- completed
- Sex
- All
- Target Recruitment
- 138
Inclusion Criteria
Please refer to ClinicalTrials.gov : NCT03070119.
Exclusion Criteria
Please refer to ClinicalTrials.gov : NCT03070119.
Study & Design
- Study Type
- Interventional
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method safety<br>efficacy<br>confirmatory<br>pharmacokinetics<br>pharmacodynamics<br>other
- Secondary Outcome Measures
Name Time Method exploratory<br>pharmacokinetics<br>pharmacodynamics<br>other