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A Study of Thalidomide Plus Dexamethasone (Thal-Dex) Versus DOXIL plusThalidomide Plus Dexamethasone (DOXIL -Thal-Dex) in Patients With Newly Diagnosed Multiple Myeloma

Phase 3
Completed
Conditions
Multiple Myeloma
Interventions
Registration Number
NCT00097981
Lead Sponsor
Johnson & Johnson Pharmaceutical Research & Development, L.L.C.
Brief Summary

The purpose of this study is to determine if Thalidomide + Dexamethasone or DOXIL (doxorubicin HCl liposome injection) + Thalidomide + Dexamethasone is more effective in treating newly diagnosed patients with multiple myeloma. The number of patients whose multiple myeloma disappears for a period of time (complete Response) will be studied to make the determination of which treatment is more effective.

Detailed Description

This is a multi-center, open-label (all people know the identity of the intervention), randomized (the study medication is assigned by chance) study to compare the safety and effectiveness of Thalidomide + Dexamethasone versus DOXIL (doxorubicin HCl liposome injection) + Thalidomide + Dexamethasone in patients with newly diagnosed multiple myeloma. Treatments are administered in 28-day cycles. Patients will receive 4 to 12 treatment cycles, depending on the response of their multiple myeloma to the treatment (measured according to the European Group for Blood and Marrow Transplant Response Criteria). Patients will have additional tests that include Multiple Gated Acquisition (MUGA) scans or echocardiograms to assess the patients for potential cardiotoxicity that could be related to treatment with DOXIL (doxorubicin HCl liposome injection). Maximum duration of study participation for each participant will be 48 weeks.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
225
Inclusion Criteria
  • Previously untreated, histologically confirmed multiple myeloma (per International Myeloma Working Group [IMWG] criteria
  • Eastern Cooperative Oncology Group (ECOG) status 0-2
  • Adequate absolute neutrophil count (ANC), platelet count and hemoglobin
  • Adequate serum calcium
  • Enrollment in System for Thalidomide Education and Prescribing Safety Program (S.T.E.P.S.)
Exclusion Criteria
  • No treatment with dexamethasone for multiple myeloma
  • No peripheral neuropathy of Grade 2 or higher
  • No Left Ventricular Ejection Fraction (LVEF) of less than 45 percentage
  • No history of life-threatening thromboembolic events of any kind (ie, myocardial infarction, pulmonary embolism, stroke or others), within 1 year before enrollment in the study
  • No deep vein thrombosis (DVT) within 1 year of enrollment
  • No current anticoagulation for DVT

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Thalidomide + dexamethasoneThalidomide-
Thalidomide + dexamethasoneDexamethasone-
Thalidomide + dexamethasone + DOXILThalidomide-
Thalidomide + dexamethasone + DOXILDexamethasone-
Thalidomide + dexamethasone + DOXILDOXIL-
Primary Outcome Measures
NameTimeMethod
Complete Response Rate: Number of Participants Who Achieved a Complete ResponseFrom Cycle 2 until 28 days following completion of treatment

Complete response rate to study medication is defined as number of participants who acheived complete response by the local investigator according to the current European Group for Blood and Marrow Transplantation (EBMT) criteria. According to EBMT criteria, CR is defined as the absence of serum and urine monoclonal paraprotein + plus no increase in size or number of lytic bone lesions. Complete response was assessed at the beginning of every treatment cycle prior to treatment, starting at Cycle 2.

Secondary Outcome Measures
NameTimeMethod
Overall Response: Number of Participants Who Achieved a Complete Response (CR) or Partial Response (PR)From Cycle 2 until 28 days following completion of treatment

Overall response to study medication is defined as number of participants who acheived a complete response (CR) or partial response (PR) by the local investigator according to the current European Group for Blood and Marrow Transplantation (EBMT) criteria. According to EBMT criteria, CR is defined as the absence of serum and urine monoclonal paraprotein + plus no increase in size or number of lytic bone lesions; and PR is defined as not all CR criteria + 50 percentage or more reduction in serum monoclonal paraprotein.

Time to 1st ResponseFrom Cycle 2 until 28 days following completion of treatment

Time to first response was defined as the interval from date of randomization to date of achieving a partial response (PR) or better according to the current European Group for Blood and Marrow Transplantation (EBMT) criteria. According to EBMT criteria, PR is defined as not all CR criteria + 50 percentage or more reduction in serum monoclonal paraprotein.

Time to ProgressionFrom randomization until death or as assessed up to 2 years post last participant last treatment visit

Time to progression is the interval between the date of randomization until disease progression or death due to progression.

Overall Survival: Number of Participants Died Due to Any CauseFrom randomization until death or as assessed up to 2 years post last participant last treatment visit
Transplantation: Number of Participants Who Underwent Transplantation (Peripheral Stem Cell / Bone Marrow)From randomization until death or as assessed up to 2 years post last participant last treatment visit
Engraftment: Number of Participants Who Underwent EngraftmentFrom randomization until death or as assessed up to 2 years post last participant last treatment visit

Engraftment is the process of transplanted stem cells reproducing new cells.

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