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A Study of the Effects of Renal Impairment on the Pharmacokinetics and Tolerability of Eliglustat Tartrate

Phase 1
Completed
Conditions
Gaucher Disease
Interventions
Registration Number
NCT02536937
Lead Sponsor
Sanofi
Brief Summary

Primary Objective:

To study the effect of mild, moderate, and severe renal impairment on the pharmacokinetics (PK) of eliglustat.

Secondary Objective:

To assess the tolerability of eliglustat tartrate given as a single dose in subjects with mild, moderate, and severe renal impairment in comparison with matched subjects with normal renal function.

Detailed Description

The total study duration from screening period is approximately 31 days. In stage 1, only subjects with severe renal impairment and normal renal function will be enrolled. Subjects with mild and moderate renal impairment may be enrolled in stage 2 if the results in subjects with severe renal impairment show a substantial effect of reduced renal function on pharmacokinetics.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
32
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
GZ385660 (healthy subjects)eliglustatSingle dose of eliglustat tartrate will be given under fed conditions
GZ385660 (subjects with mild renal impairment)eliglustatSingle dose of eliglustat tartrate will be given under fed conditions
GZ385660 (subjects with moderate renal impairment)eliglustatSingle dose of eliglustat tartrate will be given under fed conditions
GZ385660 (subjects with severe renal impairment)eliglustatSingle dose of eliglustat tartrate will be given under fed conditions
Primary Outcome Measures
NameTimeMethod
- Assessment of PK parameter: Maximum plasma concentration observed (Cmax)3 days
- Assessment of PK parameter: Area under the plasma concentration (AUC)3 days
Secondary Outcome Measures
NameTimeMethod
Assessment of PK parameter: Apparent total body clearance (CL/F)3 days
Assessment of PK parameter: Area under the plasma concentration versus time curve (AUClast)3 days
Assessment of PK parameter: Apparent volume of distribution during the terminal phase (Vz/F)3 days
Assessment of PK parameter: Predicted accumulation ratio (Rac,pred)3 days
Assessment of PK parameter: Terminal half-life (t1/2z)3 days
Number of adverse eventsUp to 10 days

Trial Locations

Locations (3)

Investigational Site Number 840004

🇺🇸

Miami, Florida, United States

Investigational Site Number 840001

🇺🇸

Knoxville, Tennessee, United States

Investigational Site Number 840002

🇺🇸

St. Paul, Minnesota, United States

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