MedPath

Immunotherapy Study for Surgically Resected Pancreatic Cancer

Phase 3
Completed
Conditions
Pancreatic Cancer
Interventions
Biological: HyperAcute-Pancreas Immunotherapy
Radiation: 5FU Chemoradiation
Registration Number
NCT01072981
Lead Sponsor
NewLink Genetics Corporation
Brief Summary

The purpose of this study is to assess overall survival after treatment with a regimen of adjuvant therapy (Gemcitabine alone or with 5-FU chemoradiation) with or without HyperAcute®-Pancreas (algenpantucel-L) immunotherapy in subjects who have undergone surgical resection.

Detailed Description

Unfortunately, despite the best clinical efforts and breakthroughs in biotechnology, most patients diagnosed with pancreatic cancer continue to die from the rapid progression of their disease. The primary reason for this is that the disease is typically without symptoms until significant local and/or distant spread has occurred and is often beyond the chance for cure at the time of the diagnosis. The lack of any treatment to significantly increase long term survival rates is reflected by the poor outcomes associated with this disease, specifically time to disease progression and overall survival.

These disappointing facts typically shape discussions of treatment options for patients with this disease. However, another important part of the body is now being looked at as a target for therapy against this disease -- the immune system. Scientists have clearly shown that pancreatic tumor cells produce a number of defective proteins, or express normal proteins in highly uncharacteristic ways, as part of this cancer. In some cancers, these abnormalities can cause an immune response to the cancer cells much in the way one responds to infected tissue. In progressive cancers however, the immune system fails to identify or respond to these abnormalities and the cancer cells are not attacked or destroyed for reasons not yet fully understood. This clinical trial proposes a new way to stimulate the immune system to recognize the abnormal components found in pancreatic cancer cells and to stimulate an immune response that destroys or blocks the growth of the cancer.

This new method of treatment helps the immune system of pancreatic cancer patients to "identify" the cancerous tissue so that it can be eliminated from the body. As an example, most people are aware that patients with certain diseases may require an organ transplant to replace a damaged kidney or heart. After receiving their transplant these patients receive special drugs because they are at great danger of having an immune response that destroys or "rejects" the transplanted organ. This "rejection" occurs when their immune system responds to differences between the cells of the transplanted organ and their own immune system by attacking the foreign tissue in the same way as it would attack infected tissue. When the differences between foreign tissues and the patient's body are even larger, perhaps like differences between organs from pigs and the immune system cells of humans, the rejection is very rapid, highly destructive and the immunity it generates is long lasting. This is called hyperacute rejection and the medicine used to immunize patients in this protocol tries to harness this response to teach a patient's immune system to fight their pancreatic cancer just as the body would learn to reject a transplanted organ from an animal.

To do this, the investigators have placed a mouse gene into human pancreatic cancer cells so that the immune system will easily recognize them as foreign, stimulating the patient immune system to attack the vaccine cells just as they would any other animal cells. As part of the process of destroying the immunotherapy cells, the patient immune system is stimulated to identify as many differences from normal human as possible. This extra stimulation is thought to encourage immune responses against the pancreatic cancer in the patient based on shared abnormalities of pancreatic cancer vaccine cells and the patient's pancreatic cancer cells.

In this experimental therapy, patients are given injections of an immunotherapy consisting of two types of cancer cells that the investigators have modified to make them more easily recognized and attacked by the immune system. The investigators propose to test this new treatment in patients with pancreatic cancer who have undergone tumor removal surgery but remain at extremely high risk of disease progression to demonstrate that treatment with the immunotherapy increases the time until the tumor recurs or increases overall survival when given in combination with the current standard of care therapy for this disease.

For more information, please see our study specific website: www.pancreaticcancer-clinicaltrials.com

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
722
Inclusion Criteria
  • A histological diagnosis of adenocarcinoma of the pancreas confirmed by pathology.
  • American Joint Committee on Cancer (AJCC) Stage I or II Pancreatic carcinoma. Patients must have undergone surgical resection for the tumor and extent of resection must be either R0 (complete resection with grossly and microscopically negative margins of resection) or R1 (grossly negative but positive microscopically margins of resection).
  • Eastern Cooperative Oncology Group (ECOG) Performance Status ≤ 2.
  • Serum albumin ≥2.0 gm/dL.
  • Expected survival ≥6 months.
  • Subjects must be able to take in adequate daily calorie intake based on judgment of clinical investigator.
  • Adequate organ function including:
  • A. Marrow: white blood cells (WBC) ≥3000/mm3 and platelets ≥100,000/mm3.
  • B. Hepatic: serum total bilirubin ≤2 x ULN mg/dL, ALT (SGPT) and AST (SGOT) ≤3 x upper limit of normal (ULN).
  • C. Renal: serum creatinine (sCr) ≤2.0 x ULN, or creatinine clearance (Ccr) ≥30 mL/min.
  • First vaccination must be within 10 weeks after surgery.
  • Patients must have the ability to understand the study, its inherent risks, side effects and potential benefits and be able to give written informed consent to participate. Patients may not be consented by a durable power of attorney (DPA).
  • All subjects of child producing potential must agree to use contraception or avoidance of pregnancy measures while enrolled on study and receiving the experimental product, and for one month after the last immunization.
Exclusion Criteria
  • Age <18-years-old.
  • Active metastases. Suspicious lesions on CT scans must be reviewed by a second, different reviewer. If active disease not ruled out by second, different reviewer (at clinical institution), a positron emission tomography (PET) CT or further imaging tests or histology may be needed to rule out disease before enrollment is allowed.
  • Other malignancy within five years, unless the probability of recurrence of the prior malignancy is <5% as determined by the Principal Investigator based on available information. Patient's curatively treated for squamous and basal cell carcinoma of the skin or patients with a history of malignant tumor in the past that have been disease free for at least five years are also eligible for this study.
  • History of organ transplant.
  • Current, active immunosuppressive therapy such as cyclosporine, tacrolimus, etc.
  • Subjects taking chronic systemic corticosteroid therapy for any reason are not eligible. Subjects may receive steroids as prophylactic anti-emetics, not to exceed 10 mg Decadron weekly. Subjects may also receive pulse doses for Gemcitabine hypersensitivity, not to exceed Decadron 8 mg twice a day (BID) x 3 days prior to start day of Gemcitabine. Subjects receiving inhaled or topical corticosteroids are eligible. Subjects who require chronic systemic corticosteroids after beginning vaccination, will be removed from study.
  • Significant or uncontrolled congestive heart failure (CHF),myocardial infarction or significant ventricular arrhythmias within the last six months.
  • Active infection or antibiotics within 48 hours prior to study,including unexplained fever (temp > 38.1C).
  • Autoimmune disease (e.g., systemic lupus erythematosis (SLE), rheumatoid arthritis (RA), etc.). Patients with a remote history of asthma or mild active asthma are eligible.
  • Other serious medical conditions that may be expected to limit life expectancy to less than 2 years (e.g., liver cirrhosis) or a serious illness in medical opinion of the clinical investigator.
  • Any condition, psychiatric or otherwise, that would preclude informed consent, consistent follow-up or compliance with any aspect of the study (e.g., untreated schizophrenia or other significant cognitive impairment, etc.).
  • A known allergy to any component of the HyperAcute® immunotherapy.
  • Pregnant or nursing women due to the unknown effects of vaccination on the developing fetus or newborn infant. (For patients with child bearing potential, a βHCG must be completed within 14 days of first vaccination).
  • Known HIV positive.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Standard of Care alone5FU Chemoradiation\*Adjuvant Standard of Care Treatment (SOC) consisting of gemcitabine with or without 5FU chemoradiation Alone
HyperAcute-Pancreas Immunotherapy + Standard of Care5FU Chemoradiation\*Adjuvant Standard of Care Treatment (SOC) consisting of gemcitabine with or without 5FU chemoradiation + HyperAcute Immunotherapy
HyperAcute-Pancreas Immunotherapy + Standard of CareHyperAcute-Pancreas Immunotherapy\*Adjuvant Standard of Care Treatment (SOC) consisting of gemcitabine with or without 5FU chemoradiation + HyperAcute Immunotherapy
HyperAcute-Pancreas Immunotherapy + Standard of CareGemcitabine\*Adjuvant Standard of Care Treatment (SOC) consisting of gemcitabine with or without 5FU chemoradiation + HyperAcute Immunotherapy
Standard of Care aloneGemcitabine\*Adjuvant Standard of Care Treatment (SOC) consisting of gemcitabine with or without 5FU chemoradiation Alone
Primary Outcome Measures
NameTimeMethod
The primary objective is to assess overall survivalApproximately 41 months and 48 months
Secondary Outcome Measures
NameTimeMethod
The secondary objective is to assess disease free survival and to conduct correlative scientific studies of subject samples to determine the mechanism of any observed anti-tumor effect.Approximately 41 months and 48 months

Trial Locations

Locations (74)

Stamford Hospital

🇺🇸

Stamford, Connecticut, United States

Fox Chase Cancer Center

🇺🇸

Philadelphia, Pennsylvania, United States

Massachusetts General Hospital

🇺🇸

Boston, Massachusetts, United States

University Hospitals Case Western

🇺🇸

Cleveland, Ohio, United States

University of Pittsburg Medical Center

🇺🇸

Pittsburgh, Pennsylvania, United States

Baylor College of Medicine

🇺🇸

Houston, Texas, United States

University of Washington- Seattle Cancer Center Alliance

🇺🇸

Seattle, Washington, United States

University of New Mexico

🇺🇸

Albuquerque, New Mexico, United States

University of Miami

🇺🇸

Miami, Florida, United States

University of Cincinnati

🇺🇸

Cincinnati, Ohio, United States

Vince Lombardi Cancer Clinic

🇺🇸

Green Bay, Wisconsin, United States

University of Wisconsin

🇺🇸

Madison, Wisconsin, United States

City of Hope National Medical Center

🇺🇸

Duarte, California, United States

Arizona Cancer Center

🇺🇸

Tucson, Arizona, United States

University of Arkansas for Medical Sciences

🇺🇸

Little Rock, Arkansas, United States

Boca Raton Hospital

🇺🇸

Boca Raton, Florida, United States

Stanford Cancer Center

🇺🇸

Palo Alto, California, United States

Cedars-Sinai Medical Center

🇺🇸

Los Angeles, California, United States

Georgetown University

🇺🇸

Washington, District of Columbia, United States

Lakeland Regional Cancer Center

🇺🇸

Lakeland, Florida, United States

Illinois Cancer Specialists

🇺🇸

Arlington Heights, Illinois, United States

University of Maryland

🇺🇸

Baltimore, Maryland, United States

Dana-Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

Lahey Clinic

🇺🇸

Burlington, Massachusetts, United States

Northwestern University

🇺🇸

Chicago, Illinois, United States

Beaumont Hospital

🇺🇸

Royal Oak, Michigan, United States

Mount Sinai Medical Center

🇺🇸

New York, New York, United States

Investigative Clinical Research of Indiana, LLC

🇺🇸

Indianapolis, Indiana, United States

Indiana University Health Goshen Center for Cancer Care

🇺🇸

Goshen, Indiana, United States

Ben Taub Hospital

🇺🇸

Houston, Texas, United States

Mary Bird Perkins Cancer Center

🇺🇸

Baton Rouge, Louisiana, United States

Beth Israel Deaconess Medical Center

🇺🇸

Boston, Massachusetts, United States

Penn State Hershey Cancer Institute

🇺🇸

Hershey, Pennsylvania, United States

Washington University

🇺🇸

Saint Louis, Missouri, United States

Greenville Health System

🇺🇸

Greenville, South Carolina, United States

The Methodist Hospital

🇺🇸

Houston, Texas, United States

University of Southern California

🇺🇸

Los Angeles, California, United States

Indiana University

🇺🇸

Indianapolis, Indiana, United States

University of Iowa

🇺🇸

Iowa City, Iowa, United States

Edward H. Kaplan, MD and Associates

🇺🇸

Skokie, Illinois, United States

University of Pennsylvania

🇺🇸

Philadelphia, Pennsylvania, United States

University of Virginia

🇺🇸

Charlottesville, Virginia, United States

University of South Alabama

🇺🇸

Mobile, Alabama, United States

University of Missouri

🇺🇸

Columbia, Missouri, United States

University of Florida

🇺🇸

Gainesville, Florida, United States

Northshore University Health Systems

🇺🇸

Evanston, Illinois, United States

University of Kansas Cancer Center

🇺🇸

Westwood, Kansas, United States

Ohio State University

🇺🇸

Columbus, Ohio, United States

Columbia University

🇺🇸

New York, New York, United States

St. Luke's Hospital and Health Network

🇺🇸

Bethlehem, Pennsylvania, United States

Roger Williams Medical Center

🇺🇸

Providence, Rhode Island, United States

University of Texas Southwestern Medical Center

🇺🇸

Dallas, Texas, United States

Joe Arrington Cancer Research and Treatment Center

🇺🇸

Lubbock, Texas, United States

Lynchburg Hematology-Oncology Clinic, Inc.

🇺🇸

Lynchburg, Virginia, United States

Sutter Institute for Medical Research

🇺🇸

Sacramento, California, United States

MOFFITT

🇺🇸

Tampa, Florida, United States

University of Oklahoma

🇺🇸

Oklahoma City, Oklahoma, United States

Virginia Commonwealth University

🇺🇸

Richmond, Virginia, United States

University of Alabama

🇺🇸

Birmingham, Alabama, United States

Mayo Clinic

🇺🇸

Rochester, Minnesota, United States

University of Colorado

🇺🇸

Aurora, Colorado, United States

Ochsner Cancer Institute

🇺🇸

New Orleans, Louisiana, United States

California Pacific Medical Center

🇺🇸

San Francisco, California, United States

USF Tampa General

🇺🇸

Tampa, Florida, United States

University of Louisville

🇺🇸

Louisville, Kentucky, United States

University of Michigan

🇺🇸

Ann Arbor, Michigan, United States

Henry Ford Hospital

🇺🇸

Detroit, Michigan, United States

University of Texas Health Sciences

🇺🇸

San Antonio, Texas, United States

Virginia Piper Cancer Institute

🇺🇸

Minneapolis, Minnesota, United States

University of Nebraska Medical Center

🇺🇸

Omaha, Nebraska, United States

Duke University Medical Center

🇺🇸

Durham, North Carolina, United States

Wake Forest Baptist Health Comprehensive Cancer Center

🇺🇸

Winston-Salem, North Carolina, United States

Oregon Health and Science University

🇺🇸

Portland, Oregon, United States

Thomas Jefferson University

🇺🇸

Philadelphia, Pennsylvania, United States

© Copyright 2025. All Rights Reserved by MedPath