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Familial Fecal Microbiota Transplant for the Treatment of Subjects With Autism Spectrum Disorders

Phase 1
Not yet recruiting
Conditions
Autism Spectrum Disorder
Autism
Interventions
Biological: Fecal Microbiota Transplant
Registration Number
NCT04630847
Lead Sponsor
ProgenaBiome
Brief Summary

This is an open-label clinical trial to evaluate the benefits of familial fecal microbiota transplant following a 6-week treatment with Vancomycin in minor and adult subjects with ASD for treatment of social deficits and language delays.

Detailed Description

This is an open-label clinical trial to evaluate the benefits of familial fecal microbiota transplant following a 6-week treatment with Vancomycin in minor and adult subjects with ASD for treatment of social deficits and language delays. Participants are given FMT by colonoscopy

Recruitment & Eligibility

Status
NOT_YET_RECRUITING
Sex
All
Target Recruitment
30
Inclusion Criteria
  1. Subject at least two years of age.
  2. Subject has confirmed diagnosis of ASD based on the DSM-V.
  3. Subject with ASD whose parents/caregiver/guardian/LAR can complete informed consent process.
  4. A reliable parent or caregiver who can report the side effects and communicate effectively with the research team.
  5. Stable medications during the two months prior to enrollment.
  6. Currently receiving interventions in the community or school for ASD.
  7. If male, and partner is of childbearing potential, must be willing to utilize at least one highly effective method of birth control for the duration of the study.
Exclusion Criteria
  1. Female subjects who are pregnant, nursing, or intend to become pregnant during the study period.
  2. Subjects whose caregivers are unable/unwilling to cooperate with the protocol requirements.
  3. Subject will be excluded who are suffering with Rett syndrome and Childhood Disintegrative Disorder.
  4. Other serious co-morbid medical disorders affecting brain function and behaviour, including uncontrolled seizures.
  5. Subjects unable to refrain from taking non-study antibiotics for the period of the study.
  6. Subjects diagnosed with cancer, except small localized basal cell carcinoma.
  7. Subjects known to abuse alcohol or drugs.
  8. Subjects who have undergone gastric bypass or total colectomy, or who are scheduled for these procedures.
  9. Infection with HIV.
  10. Infection with Hepatitis B or C.
  11. Hepatic values greater than 20
  12. Allergy to benzodiazepine.
  13. Inability to stop loperamide, diphenoxylatye/atropine, or cholestyramine before the study
  14. Unable to stop opiate treatment unless on a stable dose including PRN dosing, and no dose increase planned for the duration of the study
  15. Known positive stool cultures for enteropathogens including, but not limited to Shigella, Salmonella, and Campylobacter within 30 days before enrollment.
  16. Known stool studies positive for ova and/or parasites in 30 days prior to enrollment.
  17. Planned travel outside United States during study period.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Autism SubjectsFecal Microbiota TransplantThese subjects will be administered fecal microbiota transplant by colonoscopy
Primary Outcome Measures
NameTimeMethod
Adverse Events52 Weeks

Number of participants with grade III or higher adverse events

Serious Adverse Events52 Weeks

Number of participants with serous adverse events

Secondary Outcome Measures
NameTimeMethod
ATEC52 Weeks

Number of participants with changes in the Autism Treatment Evaluation Checklist scores

CARS-252 Weeks

Number of participants with changes in Childhood Autism Rating Scale 2 scores

QoLA52 Weeks

Number of participants with changes in Quality of Life Autism scores

SRS-II52 Weeks

Number of participants with changes in Social Responsiveness Scale scores

Shannon Diversity Index52 Weeks

Changes in Shannon Diversity index compared between pre and post FMT scores

Trial Locations

Locations (1)

ProgenaBiome

🇺🇸

Ventura, California, United States

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