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Acetylcysteine in Patients With Sickle Cell Disease (NAC).

Recruiting
Conditions
Sickle Cell DiseaseSickle Cell AnemiaPainful CrisisPainSikkelcel ziekteSikkelcel anemiePijnlijke crisePijn
Registration Number
NL-OMON28196
Lead Sponsor
Academic Medical Center, Amsterdam
Brief Summary

/A

Detailed Description

Not available

Recruitment & Eligibility

Status
Recruiting
Sex
Not specified
Target Recruitment
140
Inclusion Criteria

1. Age 12 years or older;

2. Sickle cell disease, either homozygous sickle cell disease (HbSS), compound heterozygous sickle cell disease (HbSC), HbSβ0 or HbSβ+ thalassemia;

Exclusion Criteria

1. Chronic blood transfusion or transfusion in the preceding 3 months;

2. Painful crisis in the last 4 weeks (with respect to the moment of inclusion);

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
The frequency of SCD related pain in daily life in patients with Sickle Cell Disease evaluated over a period of 6 months.
Secondary Outcome Measures
NameTimeMethod
1. The severity of SCD related pain in daily life;<br /><br>2. The incidence and severity of painful crises;<br /><br>3. The frequency and length of hospital admissions;<br /><br>4. The health-related Quality of Life;<br /><br>5. The SCD-related societal costs;<br /><br>6. The tolerability of NAC;<br /><br>7. Frequency of use of pain medication at home;<br /><br>8. Frequency of SCD complications (e.g. acute chest syndrome);<br /><br>9. The changes in hematological markers of oxidative stress, hemolysis, hypercoagulability, inflammation, erythrocyte adhesion and endothelial dysfunction.
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