MedPath

Hydroxychloroquine in Treating Patients With Newly Diagnosed Chronic Graft-Versus-Host Disease

Phase 3
Completed
Conditions
Graft Versus Host Disease
Registration Number
NCT00031824
Lead Sponsor
Children's Oncology Group
Brief Summary

RATIONALE: Hydroxychloroquine may decrease the immune response and be effective in treating chronic graft-versus-host disease. It is not yet known if standard therapy for graft-versus-host disease is more effective with or without hydroxychloroquine.

PURPOSE: Randomized phase III trial to compare the effectiveness of standard therapy alone with that of standard therapy plus hydroxychloroquine in treating patients who have newly diagnosed chronic graft-versus-host disease.

Detailed Description

OBJECTIVES:

Primary

* Compare the efficacy of prednisone and cyclosporine with vs without hydroxychloroquine in patients with newly diagnosed extensive chronic graft-versus-host disease (GVHD).

Secondary

* Compare the event-free and overall survival in patients treated with these regimens.

* Compare the health-related quality of life, including longitudinal change in and magnitude of persistent disability, in patients treated with these regimens.

* Correlate cytokine levels and T-helper cell subtypes with chronic GVHD activity and response in patients treated with these regimens.

* Correlate whole blood hydroxychloroquine levels with response and toxicity in patients treated with these regimens.

OUTLINE: This is a randomized, placebo-controlled, double-blind, multicenter study. Patients are randomized to one of two treatment arms.

Patients may receive standard therapy comprising prednisone orally or IV 2-3 times daily or every other day and cyclosporine orally or IV twice daily or tacrolimus orally twice daily or IV by continuous infusion before randomization. Patients not receiving cyclosporine or tacrolimus prior to randomization may receive cyclosporine or tacrolimus after randomization according to institutional preference.

* Arm I: Within 10-14 days of beginning therapy with prednisone and cyclosporine or tacrolimus, patients receive oral hydroxychloroquine twice daily.

* Arm II: Patients receive standard therapy with prednisone and cyclosporine or tacrolimus as in arm I and oral placebo twice daily.

In both arms, treatment continues for 9 months in the absence of disease progression or unacceptable toxicity. Patients with no response after 2 months of therapy are taken off study.

Quality of life is assessed at baseline, 1 month, 9 months, and 1 year.

Patients are followed every month for 3 months and at 9 months.

PROJECTED ACCRUAL: A total of 232 patients (116 per treatment arm) will be accrued for this study within 3.6 years.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
82
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Primary Outcome Measures
NameTimeMethod
Progression Free SurvivalLength of study
Secondary Outcome Measures
NameTimeMethod
Compare the efficacy of a two-drug regimenLength of study

Compare the efficacy of a two-drug regimen including prednisone and cyclosporine versus that of a three-drug regimen including hydroxychloroquine, prednisone, and cyclosporine in patients treated for newly-diagnosed extensive chronic GVHD.

Compare conventional outcomes measuresLength of study

Compare conventional outcomes measures (event-free survival, overall survival) and health-related quality-of-life (HRQL), including longitudinal change in and magnitude of persistent disability, for the two-drug versus the three-drug regimen.

To determine if cytokine levels and T helper cell subtypes (Th1 and Th2) correlate with chronic GVHD activity and responseLength of study
Determine if whole blood hydroxychloroquine levels correlate with response and toxicity.

Trial Locations

Locations (103)

Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins

🇺🇸

Baltimore, Maryland, United States

All Children's Hospital

🇺🇸

St. Petersburg, Florida, United States

Maine Children's Cancer Program

🇺🇸

Scarborough, Maine, United States

Dana-Farber/Harvard Cancer Center at Dana Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

Riley Children Cancer Center at Riley Hospital for Children

🇺🇸

Indianapolis, Indiana, United States

Children's Hospital and Health Center, San Diego

🇺🇸

San Diego, California, United States

UCSF Comprehensive Cancer Center

🇺🇸

San Francisco, California, United States

Children's Hospitals and Clinics - Minneapolis/St. Paul

🇺🇸

Minneapolis, Minnesota, United States

Duke Comprehensive Cancer Center

🇺🇸

Durham, North Carolina, United States

University of Texas Health Science Center at San Antonio

🇺🇸

San Antonio, Texas, United States

Huntsman Cancer Institute at University of Utah

🇺🇸

Salt Lake City, Utah, United States

Pediatric Hematology and Oncology Associates of South Texas, PLLC

🇺🇸

San Antonio, Texas, United States

Children's Hospital Los Angeles

🇺🇸

Los Angeles, California, United States

Southern California Permanente Medical Group

🇺🇸

Downey, California, United States

Arkansas Cancer Research Center at University of Arkansas for Medical Sciences

🇺🇸

Little Rock, Arkansas, United States

Arizona Cancer Center at University of Arizona Health Sciences Center

🇺🇸

Tucson, Arizona, United States

Kaiser Permanente Medical Center - Los Angeles

🇺🇸

Los Angeles, California, United States

University of Florida Shands Cancer Center

🇺🇸

Gainesville, Florida, United States

University of Michigan Comprehensive Cancer Center

🇺🇸

Ann Arbor, Michigan, United States

Methodist Cancer Center at Methodist Specialty and Transplant Hospital

🇺🇸

Saint Louis, Missouri, United States

AFLAC Cancer Center and Blood Disorders Service of Children's Healthcare of Atlanta - Scottish Rite Campus

🇺🇸

Atlanta, Georgia, United States

James P. Wilmot Cancer Center at University of Rochester Medical Center

🇺🇸

Rochester, New York, United States

University of Mississippi Medical Center

🇺🇸

Jackson, Mississippi, United States

SUNY Upstate Medical University Hospital

🇺🇸

Syracuse, New York, United States

Lineberger Comprehensive Cancer Center at University of North Carolina - Chapel Hill

🇺🇸

Chapel Hill, North Carolina, United States

Princess Margaret Hospital for Children

🇦🇺

Perth, Western Australia, Australia

Cook Children's Medical Center - Fort Worth

🇺🇸

Fort Worth, Texas, United States

Cardinal Glennon Children's Hospital

🇺🇸

Saint Louis, Missouri, United States

NYU Cancer Institute at New York University Medical Center

🇺🇸

New York, New York, United States

University of Minnesota Cancer Center

🇺🇸

Minneapolis, Minnesota, United States

Children's Hospital at Milton S. Hershey Medical Center

🇺🇸

Hershey, Pennsylvania, United States

Herbert Irving Comprehensive Cancer Center at Columbia University

🇺🇸

New York, New York, United States

New York Medical College

🇺🇸

Valhalla, New York, United States

Cincinnati Children's Hospital Medical Center

🇺🇸

Cincinnati, Ohio, United States

St. Jude Children's Research Hospital

🇺🇸

Memphis, Tennessee, United States

CancerCare Manitoba

🇨🇦

Winnipeg, Manitoba, Canada

Children's Hospital of Philadelphia

🇺🇸

Philadelphia, Pennsylvania, United States

Hollings Cancer Center at Medical University of South Carolina

🇺🇸

Charleston, South Carolina, United States

Alberta Children's Hospital

🇨🇦

Calgary, Alberta, Canada

McGill Cancer Centre at McGill University

🇨🇦

Montreal, Quebec, Canada

INOVA Fairfax Hospital

🇺🇸

Falls Church, Virginia, United States

Swiss Pediatric Oncology Group Lausanne

🇨🇭

Lausanne, Switzerland

Hopital Sainte Justine

🇨🇦

Montreal, Quebec, Canada

Starship Children's Health

🇳🇿

Auckland, New Zealand

Hospital for Sick Children

🇨🇦

Toronto, Ontario, Canada

St. Louis Children's Hospital

🇺🇸

Saint Louis, Missouri, United States

Children's Hospital Cancer Center

🇺🇸

Denver, Colorado, United States

Children's Hospital of Michigan

🇺🇸

Detroit, Michigan, United States

UNMC Eppley Cancer Center at the University of Nebraska Medical Center

🇺🇸

Omaha, Nebraska, United States

CCOP - Columbia River Oncology Program

🇺🇸

Portland, Oregon, United States

Cancer Institute at Oregon Health and Science University

🇺🇸

Portland, Oregon, United States

Doernbecher Children's Hospital at Oregon Health & Science University

🇺🇸

Portland, Oregon, United States

Midwest Children's Cancer Center

🇺🇸

Milwaukee, Wisconsin, United States

Schneider Children's Hospital

🇺🇸

New Hyde Park, New York, United States

Children's National Medical Center

🇺🇸

Washington, District of Columbia, United States

Madigan Army Medical Center

🇺🇸

Tacoma, Washington, United States

Simmons Cancer Center at University of Texas Southwestern Medical Center - Dallas

🇺🇸

Dallas, Texas, United States

Columbus Children's Hospital

🇺🇸

Columbus, Ohio, United States

CCOP - Scott and White Hospital

🇺🇸

Temple, Texas, United States

Children's Hospital and Regional Medical Center - Seattle

🇺🇸

Seattle, Washington, United States

MBCCOP - South Texas Pediatrics

🇺🇸

San Antonio, Texas, United States

Deaconess Medical Center

🇺🇸

Spokane, Washington, United States

University of Wisconsin Comprehensive Cancer Center

🇺🇸

Madison, Wisconsin, United States

Children's Hospital at Westmead

🇦🇺

Westmead, New South Wales, Australia

Royal Children's Hospital

🇦🇺

Parkville, Victoria, Australia

Women's and Children's Hospital

🇦🇺

North Adelaide, South Australia, Australia

City of Hope Comprehensive Cancer Center

🇺🇸

Duarte, California, United States

University Medical Center at Princeton

🇺🇸

Los Angeles, California, United States

Children's Hospital and Research Center at Oakland

🇺🇸

Oakland, California, United States

Samuel Oschin Comprehensive Cancer Institute at Cedars-Sinai Medical Center

🇺🇸

Los Angeles, California, United States

Jonsson Comprehensive Cancer Center at UCLA

🇺🇸

Los Angeles, California, United States

Lucile Packard Children's Hospital at Stanford University Medical Center

🇺🇸

Palo Alto, California, United States

Children's Hospital of Orange County

🇺🇸

Orange, California, United States

Presbyterian - St. Luke's Medical Center

🇺🇸

Colorado Springs, Colorado, United States

Lombardi Cancer Center at Georgetown University Medical Center

🇺🇸

Washington, District of Columbia, United States

Nemours Children's Clinic

🇺🇸

Jacksonville, Florida, United States

University of Chicago Cancer Research Center

🇺🇸

Chicago, Illinois, United States

Miami Children's Hospital

🇺🇸

Miami, Florida, United States

MBCCOP-Medical College of Georgia Cancer Center

🇺🇸

Augusta, Georgia, United States

Cancer Research Center of Hawaii

🇺🇸

Honolulu, Hawaii, United States

Children's Memorial Hospital - Chicago

🇺🇸

Chicago, Illinois, United States

Markey Cancer Center at University of Kentucky Chandler Medical Center

🇺🇸

Lexington, Kentucky, United States

Holden Comprehensive Cancer Center at University of Iowa

🇺🇸

Iowa City, Iowa, United States

Kosair Children's Hospital

🇺🇸

Louisville, Kentucky, United States

MBCCOP - LSU Health Sciences Center

🇺🇸

New Orleans, Louisiana, United States

Children's Hospital of New Orleans

🇺🇸

New Orleans, Louisiana, United States

Floating Hospital for Children

🇺🇸

Boston, Massachusetts, United States

Massachusetts General Hospital Cancer Center

🇺🇸

Boston, Massachusetts, United States

DeVos Children's Hospital

🇺🇸

Grand Rapids, Michigan, United States

Oklahoma University Medical Center

🇺🇸

Oklahoma City, Oklahoma, United States

Children's Mercy Hospital

🇺🇸

Kansas City, Missouri, United States

Memorial Sloan-Kettering Cancer Center

🇺🇸

New York, New York, United States

Cancer Center at Hackensack University Medical Center

🇺🇸

Hackensack, New Jersey, United States

Ireland Cancer Center at University Hospitals of Cleveland and Case Western Reserve University

🇺🇸

Cleveland, Ohio, United States

Children's Hospital of Pittsburgh

🇺🇸

Pittsburgh, Pennsylvania, United States

Vanderbilt Children's Hospital

🇺🇸

Nashville, Tennessee, United States

M.D. Anderson Cancer Center at University of Texas

🇺🇸

Houston, Texas, United States

CCOP - St. Vincent Hospital Cancer Center, Green Bay

🇺🇸

Green Bay, Wisconsin, United States

CCOP - Marshfield Clinic Research Foundation

🇺🇸

Marshfield, Wisconsin, United States

San Jorge Children's Hospital

🇵🇷

Santurce, Puerto Rico

Baylor College of Medicine

🇺🇸

Houston, Texas, United States

Swiss Pediatric Oncology Group Bern

🇨🇭

Bern, Switzerland

British Columbia Children's Hospital

🇨🇦

Vancouver, British Columbia, Canada

© Copyright 2025. All Rights Reserved by MedPath