MedPath

Assessment of the Efficacy, Safety, and Tolerability of AVP-786 (Deudextromethorphan Hydrobromide [d6-DM]/Quinidine Sulfate [Q]) for the Treatment of Agitation in Patients With Dementia of the Alzheimer's Type

Phase 3
Completed
Conditions
Agitation in Patients With Dementia of the Alzheimer's Type
Interventions
Drug: Placebo
Registration Number
NCT03393520
Lead Sponsor
Otsuka Pharmaceutical Development & Commercialization, Inc.
Brief Summary

This study will be conducted to evaluate the efficacy, safety, and tolerability of AVP-786 compared to placebo, for the treatment of agitation in participants with dementia of the Alzheimer's type.

Detailed Description

Eligible participants for this study must have a diagnosis of probable Alzheimer's disease (AD) and must have clinically significant, moderate/severe agitation secondary to AD.

This is a multicenter, randomized, double-blind, placebo-controlled, parallel-design study, consisting of 12 weeks of treatment.

Approximately 550 participants will be enrolled at approximately 90 centers worldwide.

Study medication will be administered orally twice-daily from Day 1 through Day 85. Screening will occur within approximately 4 weeks prior to randomization. Following screening procedures for assessment of inclusion and exclusion criteria, eligible participants will be randomized into the study.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
601
Inclusion Criteria
  • Diagnosis of probable Alzheimer's Disease (AD) according to the 2011 National Institute on Aging-Alzheimer's Association (NIA-AA) working groups criteria
  • Participants with clinically significant, moderate/severe agitation at the time of screening and for at least 2 weeks prior to baseline that interferes with their daily routine and for which a prescription medication has been indicated, in the opinion of the investigator
  • The diagnosis of agitation must meet the provisional consensus definition of agitation in participants with cognitive disorders developed by the International Psychogeriatric Association (IPA) Agitation Definition Work Group.
  • A Clinical Global Impression of Severity of Illness scale for Agitation (CGIS-Agitation) score of โ‰ฅ 4 (moderately ill) at screening and baseline
  • Participants must have a reliable caregiver who is able and willing to comply with study procedures, including not administering any prohibited medications during the course of the study.
  • Caregiver who is able and willing to comply with all required study procedures. In order to qualify as a reliable informant (i.e., caregiver) capable of assessing changes in participant's condition during the study, the individual must spend a minimum of 2 hours per day for 4 days per week with the participant.
Exclusion Criteria
  • Participants with dementia predominantly of the non-Alzheimer's type (e.g., vascular dementia, frontotemporal dementia, Parkinson's disease, substance-induced dementia)
  • Participants with symptoms of agitation that are not secondary to AD (e.g., secondary to pain, other psychiatric disorder, or delirium)
  • Participants with co-existent clinically significant or unstable systemic diseases that could confound the interpretation of the safety results of the study (e.g., malignancy, poorly controlled diabetes, poorly controlled hypertension, unstable pulmonary, renal or hepatic disease, unstable ischemic cardiac disease, dilated cardiomyopathy, or unstable valvular heart disease)
  • Participants with myasthenia gravis

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
PlaceboPlaceboParticipants will be assigned to treatment with placebo capsules administered twice a day over a 12-week period.
AVP-786; Dose 1AVP-786Participants will receive AVP-786 (Dose 1) capsules administered twice a day over a 12-week period.
AVP-786; Dose 2AVP-786Participants will receive AVP-786 (Dose 2) capsules administered twice a day over a 12-week period.
Primary Outcome Measures
NameTimeMethod
Change from Baseline to Week 12 in the Cohen-Mansfield Agitation Inventory (CMAI) Composite ScoreBaseline; Week 12
Secondary Outcome Measures
NameTimeMethod
Change from Baseline to Week 12 in the Clinical Global Impression of Severity (CGIS)-Agitation Domain ScoreBaseline; Week 12

Trial Locations

Locations (210)

Advanced Research Center, Inc #835

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Anaheim, California, United States

ATP Clinical Research, Inc #763

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Costa Mesa, California, United States

Crystal Biomedical Research, LLC

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Miami Lakes, Florida, United States

Liv Generations of Agritopia / CCT #573

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Gilbert, Arizona, United States

New Horizon Research Center Site #795

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Miami, Florida, United States

Research Institute of West Kendall

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Miami, Florida, United States

Homestead Associates in Research #797

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Miami, Florida, United States

City Medical Group RC

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Miami, Florida, United States

MD First Research #767

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Chandler, Arizona, United States

Medical Advancement Center of Arizona #820

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Tempe, Arizona, United States

Clinical Trials Inc.

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Little Rock, Arkansas, United States

Rohun Medical Corporation Site #770

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Long Beach, California, United States

Torrance Clinical Research Institute, Inc. #826

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Lomita, California, United States

Paradigm Clinical Research Centers, Inc.

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La Mesa, California, United States

Sunwise Clinical Research #831

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Lafayette, California, United States

Havana Research Institute

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Pasadena, California, United States

Alliance for Wellness, Inc dba Alliance for Research #789

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Long Beach, California, United States

Neurology of Central Florida Rsch Ctr # 803

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Altamonte Springs, Florida, United States

Negron Research Services / Humanity Clinical Research #766

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Aventura, Florida, United States

SFM Clinical Research, LLC #563

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Boca Raton, Florida, United States

Helix Biomedics LLC

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Boynton Beach, Florida, United States

Bradenton Research Center #834

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Bradenton, Florida, United States

Beautiful Minds Clinical Research Center #808

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Cutler Bay, Florida, United States

Clinical Research of Brandon #838

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Brandon, Florida, United States

ASCLEPES Research Center #806

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Brooksville, Florida, United States

Science Connections, LLC #814

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Doral, Florida, United States

ConSalud Medical Research #773

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Hialeah, Florida, United States

Direct Helpers Research Center # 801

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Hialeah, Florida, United States

New Med Research Inc #812

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Hollywood, Florida, United States

Alphab Global Research #793

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Jupiter, Florida, United States

Alzheimer's Research and Treatment Center

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Lake Worth, Florida, United States

Zynak Clinical Services

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Lauderdale Lakes, Florida, United States

Meridien Research - Lakeland Site Site #558

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Lakeland, Florida, United States

Adaptive Clinical Research, Inc. Site# 815

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Lauderhill, Florida, United States

Innovative Clinical Research, Inc Site #819

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Lauderhill, Florida, United States

Agility Medical Research, Inc Site #816

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Miami Lakes, Florida, United States

Finlay Medical Research Corp #552

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Miami, Florida, United States

Premier Clinical Research Institute, Inc. #817

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Miami, Florida, United States

Project4Research #774

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Miami, Florida, United States

Central Miami Medical Institute # 798

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Miami, Florida, United States

First Class Medical Services #807

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Miami, Florida, United States

Miami Jewish Health Systems, Inc. #786

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Miami, Florida, United States

Reliant Medical Research, LLC #811

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Miami, Florida, United States

Clinical Research Associates of South Florida

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Miami, Florida, United States

P&S Research, LLC #805

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Miami, Florida, United States

Pharmax Research of South Florida

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Miami, Florida, United States

Bayside Clinical Research

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New Port Richey, Florida, United States

Innovation Medical Research Center #802

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Palmetto, Florida, United States

Quantum Laboratories Site #768

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Pompano Beach, Florida, United States

Neurostudies Inc. Site# 796

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Port Charlotte, Florida, United States

NeuroStudies. Net, LLC

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Decatur, Georgia, United States

DelRicht Research #776

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Covington, Louisiana, United States

Alzheimer Disease Center #804

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Braintree, Massachusetts, United States

Neurobehavioral Medicine Group #828

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Bloomfield, Michigan, United States

Onyx Clinical Research, LLC

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Youngstown, Ohio, United States

Oakland Medical Research #762

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Troy, Michigan, United States

Precise Research Centers Site #765

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Flowood, Mississippi, United States

Galen Research Site #550

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Chesterfield, Missouri, United States

Psychiatric Care and Research Center #827

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O'Fallon, Missouri, United States

Mid Hudson Medical Research, PLLC #836

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New Windsor, New York, United States

Osumc #837

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Columbus, Ohio, United States

Nathan S. Kline Institute for Psychiatric Research

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Orangeburg, New York, United States

The Neurological Institute #843

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Charlotte, North Carolina, United States

NorthStar Medical Research #778

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Middleburg Heights, Ohio, United States

New Hope Clinical Research

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Charlotte, North Carolina, United States

Keystone Clinical Studies, LLC

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Norristown, Pennsylvania, United States

Trinity Universal Research Associates Site #821

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Carrollton, Texas, United States

Texas Neurology #832

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Dallas, Texas, United States

InSite Clinical Research

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DeSoto, Texas, United States

Bio Pharma Informatic LLC Site #822

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Houston, Texas, United States

Katy Neurology #823

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Katy, Texas, United States

Bio Pharma Informatic Inc Site #769

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Houston, Texas, United States

Oล›rodek Alzheimerowski #756

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ลšcinawa, Poland

Perseverance Research Center

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Scottsdale, Arizona, United States

Bio Behavioral Health

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Toms River, New Jersey, United States

Semmelweis Egyetem Site #595

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Budapest, Hungary

DCC "Sv. Vrach and Sv. Sv. Kuzma and Damian" OOD #710

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Sofia, Bulgaria

Debreceni Egyetem Kenezy Gyula Egyetemi Korhaz

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Debrecen, Hungary

Centrum Medyczne Pratia Warszawa

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Warszawa, Poland

ClinHouse Centrum Medyczne #755

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Zabrze, Poland

Szent Janos Korhaz es Eszak-budai Egyesitett Korhazak #586

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Budapest, Hungary

Twoja Przychodnia - Centrum Medyczne Nowa Sol #757

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Nowa Sรณl, Poland

Ad71 #727

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Praha, Czechia

Liv Generations of Ahwatukee / CCT #784

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Phoenix, Arizona, United States

Wasatch Clinical Research, LLC Site #771

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Salt Lake City, Utah, United States

Newton Clinical Research

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Oklahoma City, Oklahoma, United States

Orenda Research & Consulting LLC #840

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Oklahoma City, Oklahoma, United States

Northpointe Psychiatry #761

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Lewisville, Texas, United States

Wellness Clinical Research #824

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McKinney, Texas, United States

PRX Research Site #825

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Mesquite, Texas, United States

Fondazione Santa Lucia - Istituto di Ricovero e Cura a Carattere Scientifico

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Roma, Italy

Northwest Clinical Research Center

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Bellevue, Washington, United States

IPC Research

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Waukesha, Wisconsin, United States

Australian Alzheimer's Research Foundation

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Nedlands, Australia

Neuro Trials Victoria Pty Ltd

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Noble Park, Australia

Medical Center Hipokrat-N EOOD

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Plovdiv, Bulgaria

University Multiprofile Hospital for Active Treatment Dr. Georgi Stranski

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Pleven, Bulgaria

Center for Mental Health - Ruse

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Ruse, Bulgaria

Mental Health Centre Prof.Nikola Shipkovenski #713

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Sofia, Bulgaria

Medical Center Stimul

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Sofia, Bulgaria

First Multiprofile Hospital for Active Treatment Sofia

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Sofia, Bulgaria

Medical Center Sveti Naum #707

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Sofia, Bulgaria

University Multiprofile Hospital for Active Treatment Alexandrovska

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Sofia, Bulgaria

Medica Plus Medical Center #705

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Veliko Tarnovo, Bulgaria

Diagnostic-consultative center Mladost-ะœ Varna OOD #711

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Varna, Bulgaria

Mental Health Center Site #712

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Vratsa, Bulgaria

MUDr. Marta Holanovรก Site# 733

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Brno, Czechia

Fakultni Nemocnice u sv. Anny v Brne #722

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Brno, Czechia

NeuropsychiatrieHK #729

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Hradec Krรกlovรฉ, Czechia

Supervize #723

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Kutnรก Hora, Czechia

Clintrial #720

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Praha, Czechia

INEP Medical s.r.o. Institut Neuropsychiatricke Pece #730

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Praha, Czechia

Neurologicka Ambulance - Forbeli #721

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Praha, Czechia

Neuropsychiatrie #726

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Praha, Czechia

Vestra Clinics #725

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Rychnov nad Knฤ›ลพnou, Czechia

Centre Hospitalier de Calais

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Calais, France

Centre Hospitalier Universitaire de Caen - Hรดpital Cรดte de Nacre

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Caen cedex 9, France

Centre Hospitalier Universitaire Dijon Bourgogn #536

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Dijon Cedex, France

Centre Hospitalier Universitaire de Nantes - Hรดpital Nord Laennec #537

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Nantes Cedex, France

Centre Hospitalier Universitaire de Poitiers

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Poitiers, France

Centre Hospitalier Universitaire Toulouse - Casselardit Ancely #533

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Toulouse, France

Centre Hospitalier Universitaire de Saint-ร‰tienne - Hรดpital Nord #535

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Saint-Etienne, France

Centre Hospitalier Universitaire de Nancy - Hรดpital de Brabois

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Vandoeuvre les Nancy, France

Dr. Kenessey Albert Kรณrhรกz-Rendelล‘intรฉzet

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Balassagyarmat, Hungary

Semmelweis Egyetem

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Budapest, Hungary

Valeomed Egeszsegugyi es Szolgaltato Kft

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Esztergom, Hungary

Dr. Mathe es Tarsa Beteti Tarsasa Site #593

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Kalocsa, Hungary

Petz Aladรกr Egyetemi Oktatรณ Kรณrhรกz Site# 594

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Gyล‘r, Hungary

CRU Hungary Egรฉszsรฉgรผgyi รฉs Szolgรกltatรณ Korlรกtolt Felelล‘ssรฉgลฑ Tรกrsasรกg

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Miskolc, Hungary

Szabolcs-Szatmar-Bereg Megyei Korhazak es Egyetemi Oktatokorhaz

๐Ÿ‡ญ๐Ÿ‡บ

Nyiregyhaza, Hungary

PsychoTech #580

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Pecs, Hungary

Szegedi Tudomanyegyetem Szent-Gyorgyi Albert Klinikai Kozpont

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Szeged, Hungary

Fejรฉr Megyei Szent Gyรถrgy Egyetemi Oktatรณ Kรณrhรกz

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Szรฉkesfehรฉrvรกr, Hungary

Azienda Socio Sanitaria Territoriale degli Spedali Civili di Brescia

๐Ÿ‡ฎ๐Ÿ‡น

Brescia, Italy

Centro San Giovanni di Dio - Fatebenefratelli

๐Ÿ‡ฎ๐Ÿ‡น

Brescia, Italy

Azienda Ospedaliero - Universitaria Careggi #610

๐Ÿ‡ฎ๐Ÿ‡น

Firenze, Italy

Universitร  degli studi G.D'Annunzio Chieti Pescara

๐Ÿ‡ฎ๐Ÿ‡น

Chieti, Italy

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

๐Ÿ‡ฎ๐Ÿ‡น

Milano, Italy

Azienda Ospedaliera San Gerardo di Monza

๐Ÿ‡ฎ๐Ÿ‡น

Monza, Italy

Azienda Sanitaria Locale di Biella - Nuovo Ospedale degli Infermi

๐Ÿ‡ฎ๐Ÿ‡น

Ponderano, Italy

Azienda Ospedaliera Sant'Andrea #606

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Roma, Italy

Fondazione Policlinico Tor Vergata #609

๐Ÿ‡ฎ๐Ÿ‡น

Roma, Italy

ลšrรณdmieล›cie Przychodnia - Bydgoszcz

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Bydgoszcz, Poland

Centrum Medyczne Sensemed

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Chorzรณw, Poland

Care Clinic #750

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Katowice, Poland

Wielospecjalistyczna Poradnia Lekarska Synapsis #741

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Katowice, Poland

Krakowska Akademia Neurologii #740

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Krakรณw, Poland

Pratia MCM Krakรณw #747

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Krakรณw, Poland

Medycyna Milorzab #743

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Lodz, Poland

Centrum Medyczne HCP

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Poznaล„, Poland

Neurologiczny Niepubliczny Zakล‚ad Opieki Zdrowotnej

๐Ÿ‡ต๐Ÿ‡ฑ

Plewiska, Poland

Brain-Soultherapy #728

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Kladno, Czechia

Clinline Services s.r.0 Psychiatricka ambulance #732

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Hostivice, Czechia

Fakultnรญ Nemocnice Hradec Krรกlovรฉ #724

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Hradec Kralovรฉ, Czechia

A-Shine s.r.o.

๐Ÿ‡จ๐Ÿ‡ฟ

Plzen, Czechia

MAC Clinical Research - Blackpool

๐Ÿ‡ฌ๐Ÿ‡ง

Blackpool, United Kingdom

The Alfred Hospital

๐Ÿ‡ฆ๐Ÿ‡บ

Parkville, Australia

Solumed Centrum Medyczne #753

๐Ÿ‡ต๐Ÿ‡ฑ

Poznaล„, Poland

RCMed Oddziaล‚ Sochaczew #510

๐Ÿ‡ต๐Ÿ‡ฑ

Sochaczew, Poland

Amonaria Indywidualna Specjalistyczna Praktyka Lekarska Agnieszka Remlinger-Molenda #508

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Suchy Las, Poland

Centrum Medyczne Euromedis

๐Ÿ‡ต๐Ÿ‡ฑ

Szczecin, Poland

Przychodnia Specjalistyczna Prosen Site#758

๐Ÿ‡ต๐Ÿ‡ฑ

Warszawa, Poland

Centrum Medyczne NeuroProtect

๐Ÿ‡ต๐Ÿ‡ฑ

Warszawa, Poland

ACF Neurological Services

๐Ÿ‡ฟ๐Ÿ‡ฆ

Cape Town, South Africa

Cape Trial Centre #621

๐Ÿ‡ฟ๐Ÿ‡ฆ

Cape Town, South Africa

Apollo Clinical Research #623

๐Ÿ‡ฟ๐Ÿ‡ฆ

Johannesburg, South Africa

Flexivest Fourteen Research Centre #620

๐Ÿ‡ฟ๐Ÿ‡ฆ

Cape Town, South Africa

Medical and Dental Centre #625

๐Ÿ‡ฟ๐Ÿ‡ฆ

Rosebank, South Africa

Dr. Chisto Carel Coetzee

๐Ÿ‡ฟ๐Ÿ‡ฆ

Umhlanga, South Africa

Accellacare Alcobendas #659

๐Ÿ‡ช๐Ÿ‡ธ

Alcobendas, Aocobendas, Spain

Fundaciรณ ACE

๐Ÿ‡ช๐Ÿ‡ธ

Barcelona, Spain

Hospital Universitari Vall d'Hebrรณn

๐Ÿ‡ช๐Ÿ‡ธ

Barcelona, Spain

Fundaciรณ Hospital de la Santa Creu i Sant Pau

๐Ÿ‡ช๐Ÿ‡ธ

Barcelona, Spain

Hospital Clinic de Barcelona

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Barcelona, Spain

Hospital Universitario Reina Sofia #647

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Cรณrdoba, Spain

Hospital General Universitario de Elche

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Elche, Spain

Hospital Universitari de Santa Maria

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Lleida, Spain

Hospital General Universitario Gregorio Maraรฑรณn

๐Ÿ‡ช๐Ÿ‡ธ

Madrid, Spain

Hospital Universitario 12 de Octubre

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Madrid, Spain

Hospital Universitario La Paz

๐Ÿ‡ช๐Ÿ‡ธ

Madrid, Spain

Hospital Universitario Puerta de Hierro - Majadahonda #658

๐Ÿ‡ช๐Ÿ‡ธ

Majadahonda, Spain

Clรญnica Universidad de Navarra

๐Ÿ‡ช๐Ÿ‡ธ

Pamplona, Spain

Hospital Universitario de Salamanca #656

๐Ÿ‡ช๐Ÿ‡ธ

Salamanca, Spain

Hospital Universitario Marquรฉs de Valdecilla

๐Ÿ‡ช๐Ÿ‡ธ

Santander, Spain

Hospital Universitario Virgen Macarena #649

๐Ÿ‡ช๐Ÿ‡ธ

Sevilla, Spain

Hospital Universitario y Politรฉcnico de La Fe

๐Ÿ‡ช๐Ÿ‡ธ

Valencia, Spain

Complejo Asistencial de Zamora Hospital Virgen de la Concha #652

๐Ÿ‡ช๐Ÿ‡ธ

Zamora, Spain

Hospital Viamed Montecanal #643

๐Ÿ‡ช๐Ÿ‡ธ

Zaragoza, Spain

MAC Clinical Research - Barnsley Site #671

๐Ÿ‡ฌ๐Ÿ‡ง

Barnsley, United Kingdom

Research Institute for the Care of Older People

๐Ÿ‡ฌ๐Ÿ‡ง

Bath, United Kingdom

MAC Clinical Research - Cannock #672

๐Ÿ‡ฌ๐Ÿ‡ง

Cannock, United Kingdom

MAC Clinical Research - Leeds

๐Ÿ‡ฌ๐Ÿ‡ง

Leeds, United Kingdom

Re:Cognition Health - London

๐Ÿ‡ฌ๐Ÿ‡ง

London, United Kingdom

South London and Maudsley NHS Foundation Trust

๐Ÿ‡ฌ๐Ÿ‡ง

London, United Kingdom

MAC Clinical Research - Manchester

๐Ÿ‡ฌ๐Ÿ‡ง

Manchester, United Kingdom

Northamptonshire Healthcare NHS Foundation Trust #682

๐Ÿ‡ฌ๐Ÿ‡ง

Northampton, United Kingdom

MAC Clinical Research - Liverpool

๐Ÿ‡ฌ๐Ÿ‡ง

Prescot, United Kingdom

Southern Health NHS Foundation Trust #679

๐Ÿ‡ฌ๐Ÿ‡ง

Southampton, United Kingdom

Avon and Wiltshire Mental Health Partnership NHS Trust

๐Ÿ‡ฌ๐Ÿ‡ง

Swindon, United Kingdom

North West Boroughs Healthcare NHS Foundation Trust #685

๐Ÿ‡ฌ๐Ÿ‡ง

Warrington, United Kingdom

Core Clinical Research # 772

๐Ÿ‡บ๐Ÿ‡ธ

Everett, Washington, United States

Combined Research Orlando #799

๐Ÿ‡บ๐Ÿ‡ธ

Orlando, Florida, United States

Academic Alliance in Dermatology

๐Ÿ‡บ๐Ÿ‡ธ

Tampa, Florida, United States

VICIS Clinical Research Inc. #777

๐Ÿ‡บ๐Ÿ‡ธ

Tampa, Florida, United States

JSV Clinical Research Study, Inc. #829

๐Ÿ‡บ๐Ÿ‡ธ

Tampa, Florida, United States

Hawaii Pacific Neuroscience #833

๐Ÿ‡บ๐Ÿ‡ธ

Honolulu, Hawaii, United States

Five Towns Neurology PC/Village Site #764

๐Ÿ‡บ๐Ÿ‡ธ

Woodmere, New York, United States

Insight Clinical Trials LLC #570

๐Ÿ‡บ๐Ÿ‡ธ

Beachwood, Ohio, United States

Valley Medical Research Site#788

๐Ÿ‡บ๐Ÿ‡ธ

Centerville, Ohio, United States

Belfast Health and Social Care Trust

๐Ÿ‡ฌ๐Ÿ‡ง

Belfast, United Kingdom

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