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Evaluation of a new paediatric formulation of hydroxycarbamide in children with sickle cell disease

Phase 1
Active, not recruiting
Conditions
Drepanocytosis
MedDRA version: 21.0Level: LLTClassification code 10051835Term: DrepanocytosisSystem Organ Class: 100000004850
Therapeutic area: Body processes [G] - Genetic Phenomena [G05]
Registration Number
EUCTR2022-000168-22-FR
Lead Sponsor
Addmedica
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Active
Sex
All
Target Recruitment
45
Inclusion Criteria

• Written informed consent, signed and dated by both parents or by the legally
acceptable representative(s) of the children,
• Child with sickle cell disease, treated with 100 mg and/or 1000 mg Siklos® filmcoated tablets, at the same daily dose for more than 4 weeks,
• Child aged between 2 and 6 years old,
• Parents capable of communicating with the investigator and understanding the
requirements and constraints of the study protocol and willing to comply with the
study requirements,
• Children affiliated to a social security plan (including universal health coverage) or
beneficiary of a similar insurance plan.
Are the trial subjects under 18? yes
Number of subjects for this age range: 45
F.1.2 Adults (18-64 years) no
F.1.2.1 Number of subjects for this age range
F.1.3 Elderly (>=65 years) no
F.1.3.1 Number of subjects for this age range

Exclusion Criteria

• Participation in any other clinical study for any other pharmaceutical product within
4 weeks preceding study inclusion,
• Known hypersensitivity or allergy to the excipients,
• Any surgical or medical condition or any significant illness that, in the opinion of
the investigator, constitutes a risk or a contraindication to the participation of the
patient to the study, or that may interfere with the objectives, conduct or evaluation
of the study.

Study & Design

Study Type
Interventional clinical trial of medicinal product
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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