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Study of Re-Treatment With ALXN2220 in Patients With ATTR-CM

Not Applicable
Recruiting
Conditions
Amyloid Transthyretin Cardiomyopathy
Interventions
Registration Number
NCT07213583
Lead Sponsor
Neurimmune AG
Brief Summary

This is a Phase 2, single-arm, multicenter study to evaluate the pharmacodynamics and safety of re-treatment with ALXN2220 in previous participants of Study NI006-101.

Detailed Description

This is a Phase 2, single arm, multicenter study to evaluate the pharmacodynamics and safety of re-treatment with ALXN2220 in the patient population of previous participants in Study NI006-101.

The study will also explore changes in cardiac structure and function, and clinical function of this dosing regimen, as well as changes in cardiac amyloid load, structure and function during the treatment-pause since conclusion of Study NI006-101. The study consists of a Screening Period and a 48 week Active Treatment Period.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
35
Inclusion Criteria
  • Must have received at least one dose of ALXN2220 in Study NI006-101
Exclusion Criteria
  • Suspected or known intolerance/allergy to proteins or any components of the study drug
  • Treatment or study discontinuation in Study NI006-101 due to a treatment-related adverse event that was serious, severe or life-threatening (on Common terminology criteria for adverse events (CTCAE) scale)
  • Any new or uncontrolled condition after completion of Study NI006-101 that could make the participant unsuitable for participation in this study

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
ALXN2220ALXN2220Participants will receive ALXN2220 via intravenous (IV) infusion during the Active Treatment Period
Primary Outcome Measures
NameTimeMethod
Change from Baseline to Week 48 in ECV measured by cMRIBaseline, Week 48
Change from Baseline to Week 48 in Heart Retention/Whole Body Retention measured by scintigraphyBaseline, Week 48
Secondary Outcome Measures
NameTimeMethod
Incidence of TEAEs, including serious TEAEsFrom Baseline up to Week 48
ALXN2220 serum concentrationsFrom Baseline up to Week 48
Incidence of Anti-Drug AntibodiesFrom Baseline up to Week 48

Trial Locations

Locations (6)

Hôpital Henri Mondor

🇫🇷

Créteil, France

CHU de Rennes - Hôpital Pontchaillou

🇫🇷

Rennes, France

CHU Toulouse - Hôpital Rangueil

🇫🇷

Toulouse, France

Universitätsklinikum Heidelberg

🇩🇪

Heidelberg, Germany

University Medical Center Groningen

🇳🇱

Groningen, Netherlands

Hospital Universitario Puerta de Hierro Majadahonda

🇪🇸

Majadahonda, Spain

Hôpital Henri Mondor
🇫🇷Créteil, France

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