MedPath

Efficacy and Safety Study of KIACTA in Preventing Renal Function Decline in AA Amyloidosis

Phase 3
Completed
Conditions
Amyloidosis
Interventions
Drug: Placebo
Drug: KIACTA (eprodisate disodium)
Registration Number
NCT01215747
Lead Sponsor
C.T. Development America, Inc.
Brief Summary

The primary purpose of this study is to assess the efficacy and safety of treatment with Kiacta in adult patients with AA Amyloidosis.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
261
Inclusion Criteria
  • females must be of nonchildbearing potential (more than 1 yr postmenopausal)or use effective contraception for at least 2 months prior to the baseline visit and through 30 days after the last dose of study medication
  • confirmed diagnosis of AA amyloidosis demonstrated by positive biopsy using congo red staining and immunohistochemistry or immunoelectronmicroscopy. Mass spectroscopy will be used upon approval of the sponsor on a case to case basis.
  • persistent proteinuria greater than 1 g/24h at 2 distinct 24-hr urine collections
  • must have CrCl greater than 25 ml/min/1.73 m2 at 2 distinct 24 hr urine collections
Exclusion Criteria
  • evidence or suspicion of chronic kidney disease secondary to a disease other than AA amyloidosis (eg, diabetes, long-standing uncontrolled hypertension, polycystic kidney disease, recurring polynephritis, or systemic lupus erythematosus)
  • history of kidney transplantation
  • evidence or suspicion of a cause of potentially reversible acute renal failure within 3 months prior to baseline visit
  • presence of concomitant diseases or medication that could interfere with the interpretation of study results or compromise patient safety
  • presence of condition that could reduce life expectancy to less than 2 yrs
  • Type 1 or 2 diabetes mellitus
  • significant hepatic enzyme elevation
  • unstable angina, myocardial infarction, coronary artery bypass graft surgery, or percutaneous transluminal coronary angioplasty within 6 months prior to the baseline visit; presence of NY Heart Assoc class III or IV heart failure
  • presence of, or history of stroke or transient ischemic attack within 6 months prior to baseline visit
  • initiation of, or any changes in, angiotensin converting enzyme inhibitor, angiotensin II receptor antagonist therapy, or renin inhibitor within 3 months prior to baseline visit
  • initiation of, or any changes in, cytotoxic agents, anti-tumor necrosis factor agents, anti interleukin-1 or 6 agents, or colchicine therapy within 3 months prior to baseline visit
  • previous use of Kiacta
  • history of malignancy within 5 yrs prior to study entry, except for cervical carcinoma in situ, nonmelanomatous carcinoma of the skin, or ductal carcinoma in situ of the breast that has been surgically cured
  • use of investigational drug within 30 days prior to the first screening visit
  • active alcohol and/or drug abuse

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
PlaceboPlacebo-
Kiacta (eprodisate disodium)KIACTA (eprodisate disodium)-
Primary Outcome Measures
NameTimeMethod
Time from baseline to a persistent decrease in Creatinine clearance (CrCL) of 40% or more, a persistent increase in Serum Creatinine(SCr) of 80% or more, or progression to end-stage renal disease(ESRD)Up to 24 months
Secondary Outcome Measures
NameTimeMethod
Progression to end-stage renal disease (ESRD)baseline, every 3 months to end of study visit
urinary protein/creatinine ratioscreening, baseline, every 3 months, 12 months, early termination, treatment completion, end of study visit
Time from baseline to persistent decrease in CrCL of 40% or more, a persistent increase in SCr of 80% or more, progression to ESRD, or all-cause mortalityUp to 24 months
serum amyloid Abaseline, every 3 months, 12 months, early termination, treatment completion, end of study visit
serum cystatin C over timebaseline, every 3 months, 12 months, early termination, treatment completion, end of study visit
rate of change (slope) in creatinine clearance (CrCL) over timebaseline to primary endpoint, measured every 3 months to end of study visit
estimated glomerular filtration rate (eGFR)screening, baseline, every 3 months, 12 months , early termination, treatment completion, end of study visit

Trial Locations

Locations (45)

Hôpital Henri Mondor

🇫🇷

Creteil, France

Hôpital Charles Nicolle

🇹🇳

Tunis, Tunisia

Hôpital Claude Huriez

🇫🇷

Lille, France

UZ Leuven

🇧🇪

Leuven, Belgium

Hospital Clinic de Barcelona

🇪🇸

Barcelona, Spain

Karolinska Universitetssjukhuset i Huddinge

🇸🇪

Stockholm, Sweden

Royal Free Hospital

🇬🇧

London, United Kingdom

Boston Medical Center

🇺🇸

Boston, Massachusetts, United States

Raffi Minasian MD a Medical Corporation

🇺🇸

Glendale, California, United States

Ohio State University Medical Center

🇺🇸

Columbus, Ohio, United States

Tartu University Hospital

🇪🇪

Tartu, Estonia

Helsingin yliopistollinen keskussairaala / Meilahti

🇫🇮

Helsinki, Finland

Universität Heidelberg

🇩🇪

Heidelberg, Germany

Regency Hospital

🇮🇳

Kanpur, India

The Chaim Sheba Medical Center

🇮🇱

Ramat-Gan, Israel

Pauls Stradins Clinical University Hospital

🇱🇻

Riga, Latvia

Sverdlovsk Regional Clinical Hospital #1

🇷🇺

Ekaterinburg, Russian Federation

Fattouma Bourguiba University Hospital

🇹🇳

Monastir, Tunisia

Hospital Civil Carlos Haya

🇪🇸

Malaga, Spain

Municipal Medical & Preventive Institution Donetsk Regional Clinical Territorial Medical Association

🇺🇦

Donetsk, Ukraine

IRCCS Policlinico San Matteo

🇮🇹

Pavia, Italy

Research Institute of Clinical and Experimental Lymphology

🇷🇺

Novosibirsk, Russian Federation

Hacettepe University Medical Faculty

🇹🇷

Ankara, Turkey

Institute of Rheumatology of RAMN

🇷🇺

Moscow, Russian Federation

Bnei Zion Medical Center

🇮🇱

Haifa, Israel

Academisch Ziekenhuis Maastricht

🇳🇱

Maastricht, Netherlands

Al Hussain University Hospital

🇪🇬

Cairo, Egypt

Tbilisi Heart and Vascular Clinic Ltd

🇬🇪

Tbilisi, Georgia

Universitair Medisch Centrum Groningen

🇳🇱

Groningen, Netherlands

Akademicki Szpital Kliniczny im. Jana Mikulicza-Radeckiego we Wroclawiu

🇵🇱

Wroclaw, Poland

La Rabta Hospital

🇹🇳

Tunis, Tunisia

Eskisehir Osmangazi University Medical Faculty

🇹🇷

Eskisehir, Turkey

National Scientific Center "Institute of cardiology n.a. academician M.D Strazhesko"

🇺🇦

Kyiv, Ukraine

Muljibhai Patel Urological Hospital

🇮🇳

Nadiad, India

Kemerovo State Medical Academy of Roszdrav

🇷🇺

Kemerovo, Russian Federation

State Institution "Institute of Nephrology of AMS of Ukraine"

🇺🇦

Kyiv, Ukraine

Sir Ganga Ram Hospital

🇮🇳

New Delhi, India

Hospital of Lithuanian University of Health Sciences Kaunas Clinics

🇱🇹

Kaunas, Lithuania

Vilnius University Hospital Santariskiu Klinikos

🇱🇹

Vilnius, Lithuania

Hospital Nacional Arzobispo Loayza

🇵🇪

Lima, Peru

ARS RHEUMATICA Sp. z o.o.

🇵🇱

Warszawa, Poland

Hedi Chaker University Hospital

🇹🇳

Sfax, Tunisia

Sahloul Hospital

🇹🇳

Sousse, Tunisia

Wojewodzki Szpital Specjalistyczny

🇵🇱

Olsztyn, Poland

Cukurova University Medical Faculty Balcali Hospital

🇹🇷

Adana, Turkey

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