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Efficacy & Safety Study of Lorlatinib in ALK/ROS1 Metastatic NSCLC Patients With Compassionate Use Treatment

Completed
Conditions
Metastatic Non Small Cell Lung Cancer
Interventions
Registration Number
NCT05167500
Lead Sponsor
Fundaci贸n GECP
Brief Summary

This is an observational, non-interventional, retrospective, multicentre and nationwide study. The information will be obtained retrospectively, in most cases when the treatment has already ended.

The primary objective of this study is determine the activity of lorlatinib (percentage of responses, duration of response, progression-free survival and time to treatment failure) of patients included in the compassionate use program in Spain.

Detailed Description

This is an observational, non-interventional, retrospective, multicentre and nationwide study. The information will be obtained retrospectively, in most cases when the treatment has already ended. In cases where the patient continues on the treatment, the researcher will not modify the clinical management of the patient by participating in the study.

Patients with metastatic non-small cell lung cancer treated with lorlatinib who were included in the compassionate use program in Spain between November 2016 and February 2019 for those with an ALK alteration, and between November 2016 to March 2021 for those with ROS1 alteration. According to the records of the Spanish centres participating in this program, approximately 145 patients have been included.

The primary objective of this study is determine the activity of lorlatinib (percentage of responses, duration of response, progression-free survival and time to treatment failure) of patients included in the compassionate use program in Spain.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
118
Inclusion Criteria
  • Patients with metastatic non-small cell lung cancer treated with lorlatinib who were included in the compassionate use program in Spain between November 2016 and February 2019 for those with an ALK alteration, and between November 2016 to March 2021 for those with ROS1 alteration.
  • Patients must have been treated with at least one cycle of lorlatinib within the compassionate use program.
  • Alive patients must have signed, dated the ethics committee approved written informed consent form in accordance with regulatory and institutional guidelines. This must be obtained before the performance of any protocol-related procedures that are not part of normal subject care.
Exclusion Criteria
  • Alive patients who refuse to sign and date an ethics committee approved written informed consent form.
  • Patients who were accepted in the compassionate use program , but did not receive treatment.

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
Experimental : Lorlatinib inn ALK Or ROS1 Metastatic NSCLC patientLorlatinibPatients with metastatic non-small cell lung cancer treated with lorlatinib who were included in the compassionate use program in Spain between November 2016 and February 2019 for those with an ALK alteration, and between November 2016 to March 2021 for those with ROS1 alteration.
Primary Outcome Measures
NameTimeMethod
Progression-free survivalFrom date of the first dose of lorlatinib treatment until the date of last follow up or death, assessed up to 60 months

Progression-free survival defined as time from the first dose of lorlatinib to the first documentation of progression or death from any cause.

Duration of the responseFrom date of the first dose of lorlatinib treatment until the date of last follow up or death, assessed up to 60 months

Duration of the response defined from the first documentation of tumor response to the first documentation of tumor progression or death from any cause.

Time to treatment failureFrom date of the first dose of lorlatinib treatment until the date of last follow up or death, assessed up to 60 months

Time to treatment failure defined as time from the first dose of lorlatinib to the moment of discontinuation of treatment for any cause, including tumor progression, toxicity or death

Secondary Outcome Measures
NameTimeMethod
Incidence of Treatment-Emergent Adverse Events (Safety and Tolerability)From date of the first dose of lorlatinib treatment until the date of last follow up or death,assessed up to 60 months

Occurrence and severity of adverse events, with severity determined by NCI CTCAE v5.0 criteria.

Overall survival of ALK and ROS1 NSCLC patientsFrom date of the first dose of lorlatinib treatment until the date of last follow up or death, assessed up to 60 months

Overall survival of ALK and ROS1 NSCLC patients from lorlatinib defined as time from the start of treatment until death or last follow-up

Trial Locations

Locations (25)

Hospital Germans Trias i Pujol

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Badalona, Barcelona, Spain

Hospital 12 De Octubre

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Madrid, Spain

Hospital Cl铆nico Santiago

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Santiago De Compostela, A Coru帽a, Spain

Hospital Universitario Central de Asturias

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Oviedo, Asturias, Spain

Hospital Puerta del Mar

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Cadiz, C谩diz, Spain

Hospital Universitario Insular de Gran canaria

馃嚜馃嚫

Las Palmas De Gran Canaria, Gran Canaria, Spain

Complejo Hospitalario Universitario A Coru帽a

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A Coru帽a, La Coru帽a, Spain

Centro Oncol贸gico de Galicia

馃嚜馃嚫

A Coru帽a, La Coru帽a, Spain

Hospital del Mar

馃嚜馃嚫

Barcelona, Spain

Hospital Universitari Quiron Dexeus

馃嚜馃嚫

Barcelona, Spain

Hospital Clinic de Barcelona

馃嚜馃嚫

Barcelona, Spain

Hospital Universitario de Burgos

馃嚜馃嚫

Burgos, Spain

Hospital Universitario de Ja茅n

馃嚜馃嚫

Ja茅n, Spain

Hospital Dr. Josep Trueta

馃嚜馃嚫

Girona, Spain

Complejo Asistencial Universitario de Le贸n

馃嚜馃嚫

Le贸n, Spain

Hospital Gregorio Mara帽贸n

馃嚜馃嚫

Madrid, Spain

Hospital Cl铆nico San Carlos

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Madrid, Spain

Hospital Puerta de Hierro

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Madrid, Spain

Hospital Fundaci贸n de Alcorc贸n

馃嚜馃嚫

Madrid, Spain

Complejo Hospitalario de Toledo

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Toledo, Spain

Hospital Virgen del Rocio

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Sevilla, Spain

Hospital Universitari i Polit茅cnic La Fe

馃嚜馃嚫

Valencia, Spain

Hospital Cl铆nico de Valencia

馃嚜馃嚫

Valencia, Spain

Hospital General de Valencia

馃嚜馃嚫

Valencia, Spain

Hospital Cl铆nico Lozano Blesa

馃嚜馃嚫

Zaragoza, Spain

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