MedPath

Real World Outcomes Using Novel Agents for AML in the UK

Recruiting
Conditions
Acute Myeloid Leukemia
Interventions
Registration Number
NCT05312112
Lead Sponsor
Guy's and St Thomas' NHS Foundation Trust
Brief Summary

This project will collect data on patients with acute myeloid leukemia in the United Kingdom who were treated with two new targeted therapies during the coronavirus pandemic

Detailed Description

Acute myeloid leukaemia (AML) is a blood cancer which in fit young adults is typically treated with intensive chemotherapy. While this is potentially curative, it is associated with significant side effects and the requirement for long hospital admissions. Infection is a major issue during AML treatment, as both the disease and the chemotherapy impair the immune system.

Early data suggested that COVID-19 is associated with a very high rate of death in AML patients undergoing intensive chemotherapy. Because of this, and the need for significant hospital resources to deliver intensive chemotherapy, the NHS made available two new, less intensive, targeted therapies for the treatment of AML during the COVID-19 pandemic - venetoclax and gilteritinib. The aim was to reduce mortality and healthcare resource use.

Many hundreds of patients across the UK have been treated with these two medications on the temporary access scheme. The research aims to collect de-identified data from treating patients to describe the outcomes of patients treated with these approaches, both in terms of the safety and effectiveness.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
1000
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
VenetoclaxVenetoclaxVenetoclax in newly diagnosed AML
FLT3 inhibitorsGilteritinibFLT3 inhibitors including gilteritinib in relapsed AML
Primary Outcome Measures
NameTimeMethod
Overall survival1 year

Overall survival measured from time of treatment initiation

Early death rateDay 60 after starting treatment

Early death rate measured at day 60 after treatment initiation

Secondary Outcome Measures
NameTimeMethod
Relapse-free survival1 year

RFS as defined by ELN

Response rateAfter 2 cycles of therapy (each cycle is 28 days although may be extended if recovery is delayed)

Response rate as defined by ELN 2017

Incidence of relapse in patients achieving remission1 year

Relapse incidence measured from the time of achieving remission

Treatment toxicity 1During the first cycle of therapy (each cycle is 28 days although may be extended if recovery is delayed)

Number of days in hospital and number of days of intensive care

Treatment toxicity 2During the first cycle of therapy (each cycle is 28 days although may be extended if recovery is delayed)

Duration of neutropenia and thrombocytopenia

Treatment toxicity 3During the first cycle of therapy (each cycle is 28 days although may be extended if recovery is delayed)

Number of blood and platelet transfusions

Comparison of survival between patient sub-groups1 year

Overall survival compared between disease groups

Trial Locations

Locations (1)

Guy's and St Thomas' NHS Foundation Trust

🇬🇧

London, United Kingdom

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