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XTX202 in Patients With Advanced Solid Tumors

Phase 1
Completed
Conditions
Advanced Solid Tumor
Interventions
Registration Number
NCT05052268
Lead Sponsor
Xilio Development, Inc.
Brief Summary

A First-in-Human, Multicenter, Phase 1/2, Open-Label Study of XTX202 in Patients with Advanced Solid Tumors

Detailed Description

This is a first-in-human, Phase 1/2, multicenter, open-label study designed to evaluate the safety, tolerability, and efficacy of XTX202, an engineered IL-2 prodrug with its activity masked, as monotherapy in patients with advanced solid tumors.

Phase 1 Part 1a will examine XTX202 monotherapy in an accelerated and standard 3+3 dose-escalation design. Based on the results of Part 1a, Part 1b will be initiated to further examine XTX202 in patients with select advanced solid tumors and to further characterize XTX202.

Based on results of Phase 1 patients with select advanced solid tumors will be enrolled in Phase 2.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
95
Inclusion Criteria
  1. Disease Criteria

    • Phase 1, Part 1a: Any histologically or cytologically confirmed solid tumor malignancy that is locally advanced or metastatic and has failed standard therapy, or standard therapy is not curative or available
    • Phase 1, Part 1b: Histologically or cytologically confirmed solid tumor malignancy with one of the following tumor histologies: RCC of clear cell histology only, melanoma, squamous cell skin carcinoma, ovarian cancer, non-small cell lung cancer. Those patients who previously received immunotherapy must have derived benefit from this treatment. Additionally, patients with any of the above histologies in an advanced setting who plan to undergo debulking surgery or oligometastasectomy may be eligible to receive 2 cycles of XTX202 treatment in a "window of opportunity" subcohort".
    • Phase 2, Part 2a: Patients with metastatic RCC who have previously been treated with an anti-PD-1 and a TKI, per local and institutional SOC. Patients must have progressed on treatment with an anti-PD-1 mAb administered either as monotherapy or in combination with other therapies
    • Phase 2, Part 2b: Patients with unresectable or metastatic melanoma who have previously been treated with at least 1 prior line of therapy in the recurrent or metastatic setting. Prior therapy must have included an anti-PD-1 alone or in combination per local and institutional standard of care, and patient must have progressed on checkpoint inhibitor therapy. Patients with BRAF V600-activating mutation must have previously received targeted therapy per local and institutional standard of care.
  2. ECOG performance status of 0 or 1

  3. Adequate organ function

  4. Part 1b only patients must be willing to provide fresh tumor biopsies before and after initiation of study treatment.

Exclusion Criteria
  1. Received prior treatment with IL-2 therapy
  2. History of clinically significant pulmonary disease
  3. History of clinically significant cardiovascular disease
  4. Has a diagnosis of immunodeficiency
  5. Has an active autoimmune disease that has required systemic treatment in past 2 years, including the use of disease modifying agents, corticosteroids or immunosuppressive drugs
  6. Has an active infection requiring systemic therapy within 4 weeks prior to study treatment

Study & Design

Study Type
INTERVENTIONAL
Study Design
SEQUENTIAL
Arm && Interventions
GroupInterventionDescription
Phase 1 XTX202 Dose Escalation and Pharmacodynamics ExpansionXTX202Part 1A Dose Escalation of XTX202 administered in ascending doses to patients with advanced or metastatic solid tumors to find the recommended phase 2 doses (RP2Ds). Part 1B Evaluation of XTX202 in patients with selected advanced solid tumors to further characterize the pharmacodynamic profile of XTX202
Phase 2 XTX202 Dose ExpansionXTX202Part 2A will enroll patients with metastatic renal cell carcinoma who have progressed following standard-of-care treatment. Part 2B will enroll patients with melanoma who have progressed following standard-of-care treatment.
Primary Outcome Measures
NameTimeMethod
Incidence of changes in clinical laboratory values (Phase 1 only)Up to 24 months
Incidence of Dose Limiting Toxicities (DLTs) (Phase 1 Part 1A only)Cycle 1 day 1 up to just prior to the second dose of study drug at Cycle 2 day 1 (each cycle is 21 days)
Investigator-assessed objective response rate (ORR) per RECIST 1.1 (Phase 2 only)Up to 24 months
Incidence of treatment-emergent adverse events (Phase 1 only)Up to 24 months
Secondary Outcome Measures
NameTimeMethod
Antidrug antibody (ADA) occurrence and titer in serum (Phase 1 only)Up to 24 months
Disease control rate (Phase 2 only)Up to 24 months
Incidence of changes in clinical laboratory values (Phase 2 only)Up to 24 months
Half-life (T1/2)Up to Cycle 7 (21 days per cycle)
Systemic clearance (CL)Up to Cycle 7 (21 days per cycle)
Volume of distribution (Vd)Up to Cycle 7 (21 days per cycle)
Area under the curve (AUC)Up to Cycle 7 (21 days per cycle)
Plasma concentrations of XTX202 (total and intact)Up to Cycle 7 (21 days per cycle)
Time of maximum observed concentration (Tmax)Up to Cycle 7 (21 days per cycle)
Investigator-assessed objective response rate (ORR) per RECIST 1.1 (Phase 1 only)Up to 24 months
Duration of response (DOR) (Phase 2 only)Up to 24 months
Overall survival (OS) (Phase 2 only)Up to 24 months
Maximum observed plasma concentration (Cmax)Up to Cycle 7 (21 days per cycle)
Trough concentrations (Ctrough)Up to Cycle 7 (21 days per cycle)
Progression-free survival (PFS) (Phase 2 only)Up to 24 months
Incidence of treatment-emergent adverse events (Phase 2 only)Up to 24 months

Trial Locations

Locations (15)

Hoag Memorial Hospital Presbyterian- Newport Beach

🇺🇸

Newport Beach, California, United States

Norris Comprehensive Cancer Center

🇺🇸

Los Angeles, California, United States

UC San Diego Moores Cancer Center

🇺🇸

La Jolla, California, United States

University of California Los Angeles

🇺🇸

Los Angeles, California, United States

Moffitt Cancer Center

🇺🇸

Tampa, Florida, United States

HealthPartners Cancer Center at Regions Hospital

🇺🇸

Saint Paul, Minnesota, United States

University of Iowa Hospitals and Clinics

🇺🇸

Iowa City, Iowa, United States

Atlantic Health System/Morristown Medical Center

🇺🇸

Morristown, New Jersey, United States

Carolina BioOncology Institute

🇺🇸

Huntersville, North Carolina, United States

The Ohio State University Wexner Medical Center James Cancer Hospital and Solove Research Institute

🇺🇸

Columbus, Ohio, United States

UPMC Hillman Cancer Center Pavilion

🇺🇸

Pittsburgh, Pennsylvania, United States

Sarah Cannon Research Institute

🇺🇸

Nashville, Tennessee, United States

Massachusetts General Hospital

🇺🇸

Boston, Massachusetts, United States

Rutgers Cancer Institute of NJ

🇺🇸

New Brunswick, New Jersey, United States

Georgetown University Medical Center

🇺🇸

Washington, District of Columbia, United States

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