MedPath

Effects of Triptorelin Pamoate in Children With Precocious Puberty - Follow up Study

Phase 3
Completed
Conditions
Precocious Puberty
Interventions
Registration Number
NCT00909844
Lead Sponsor
Ipsen
Brief Summary

The purpose of the protocol is to assess the efficacy of triptorelin 11.25 mg with respect to the proportion of children who maintain a regression or stabilisation of sexual maturity until the end of the study.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
35
Inclusion Criteria
  • The child must have completed study 2-54-52014-143
  • The child must have an effective response to 2 injections of triptorelin 11.25 mg according to investigator's evaluation with no significant treatment side effects
Exclusion Criteria
  • The patient has a known hypersensitivity to any of the test materials or related compounds
  • The patient is unable or unwilling to comply fully with the protocol

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
TriptorelinTriptorelin (I.N.N.)-
Primary Outcome Measures
NameTimeMethod
Percentage of Children With a Stabilisation or Regression of Tanner Pubertal Stage at the End of the Study (Final Visit), Compared to Pretreatment (Month -6) and Baseline (Month 0)Months 12, 24, 36, 48 and Final Visit (if applicable; up to 63 months)

The primary objective was to assess efficacy of triptorelin pamoate 11.25 mg with respect to percentage of children maintaining a regression or stabilisation of sexual maturity (based on Tanner breast \[girls\] or genital \[boys\] pubertal stage) until end of study. Study treatment lasted until end of the therapeutic period; visits for Months 36 and 48 were optional since a child may have already finished the study at a prior visit. The Final Visit only occurred if the child did not end the study by a complete visit such as at Months 24, 36 or 48. Results are presented only for percentage of girls with regression or stabilisation of Tanner breast pubertal stage (n=34). Since only one boy was included in the study, results for this outcome measure were listed only and no statistical analysis was performed. Please also note additional post-hoc analysis for regression or stabilisation of Tanner breast pubertal stage which applied the variable Last Visit on Treatment instead of Final Visit.

Secondary Outcome Measures
NameTimeMethod
Percentage of Patients With a Suppressed Luteinizing Hormone (LH) Response to Gonadotropin-Releasing Hormone (GnRH) TestMonths -6, 0 and 36

A suppressed LH response to the GnRH test was defined as a stimulated peak of LH ≤3 international units per litre (IU/L). Percentage of patients who had a suppressed LH response to the GnRH test is reported. It should be noted that almost no hormonal data was collected after Baseline; all data analysed is presented.

Levels of Oestradiol in Girls or Testosterone in Boys Both Measured by Radioimmunoassay (RIA)Months -6, 0, 12, 36 and Final Visit (up to 63 months)

Mean levels of oestradiol in girls or testosterone in boys are reported. It should be noted that almost no hormonal data was collected after Baseline; all data analysed is presented.

Percentage of Patients With a Suppressed Follicle Stimulating Hormone (FSH) Response to GnRH TestMonths -6, 0 and 36

A suppressed FSH response to the GnRH test was defined as a stimulated peak of FSH ≤3 IU/L. Percentage of patients who had a suppressed FSH response to the GnRH test is reported. It should be noted that almost no hormonal data was collected after Baseline; all data analysed is presented.

Body Mass Index (BMI) for Chronological Age VariationMonths -6, 0, 12, 24, 36, 48 and Final Visit (up to 63 months)

Mean changes of BMI from Pretreatment and from Baseline are reported. It should be noted that only limited patient data was collected after Baseline; all data analysed is presented.

BMI Standard Deviation (SD) Score for Chronological Age VariationMonths -6, 0, 12, 24, 36, 48 and Final Visit (up to 63 months)

Mean changes of BMI SD score from Pretreatment and from Baseline are reported. SD score is a standard term used in growth studies and represents standard deviations calculated as the patient value minus the mean divided by the SD. SD scores vary depending on the age and sex of the child. It should be noted that only limited patient data was collected after Baseline; all data analysed is presented.

Auxological Parameters Variations: Height SD ScoreMonths -6, 0, 12, 24, 36, 48 and Final Visit (up to 63 months)

Mean changes of height SD score from Pretreatment and from Baseline are reported. SD score is a standard term used in growth studies and represents standard deviations calculated as the patient value minus the mean divided by the SD. SD scores vary depending on the age and sex of the child. It should be noted that only limited patient data was collected after Baseline; all data analysed is presented.

Auxological Parameters Variations: Growth Velocity SD ScoreMonths -6, 0, 12, 24, 36, 48 and Final Visit (up to 63 months)

Mean changes of growth velocity SD score from Pretreatment and from Baseline are reported. SD score is a standard term used in growth studies and represents standard deviations calculated as the patient value minus the mean divided by the SD. SD scores vary depending on the age and sex of the child. It should be noted that only limited patient data was collected after Baseline; all data analysed is presented.

Auxological Parameters Variations: Weight VariationMonths -6, 0, 12, 24, 36, 48 and Final Visit (up to 63 months)

Mean changes of weight from Pretreatment and from Baseline are reported. It should be noted that only limited patient data was collected after Baseline; all data analysed is presented.

Predicted Adult Height SD ScoreMonths -6, 0, 12 and Final Visit (up to 63 months)

Mean change of predicted adult height SD score from Pretreatment and from Baseline are reported. SD score is a standard term used in growth studies and represents standard deviations calculated as the patient value minus the mean divided by the SD. SD scores vary depending on the age and sex of the child. It should be noted that only limited patient data was collected after Baseline; all data analysed is presented. Also note that data for this endpoint was analysed for girls only.

Bone Age MaturationMonths -6, 0 and Final Visit (up to 63 months)

Mean change in difference between bone age and chronological age from Pretreatment and from Baseline are reported. It should be noted that only limited patient data was collected after Baseline; all data analysed is presented.

Percentage of Girls With a Uterine Length < 36 Millimetres (mm)Months -6, 0, 12, 24, 36 and Final Visit (up to 63 months)

Percentage of girls who had a uterine length \< 36 mm are reported. It should be noted that only limited patient data was collected after Baseline; all data analysed is presented.

Percentage of Children With a Stabilisation or Regression of Tanner Pubic Hair Pubertal Stage at the End of the Study (Final Visit), Compared to Pretreatment (Month -6) and Baseline (Month 0)Months 12, 24, 36, 48 and Final Visit (if applicable; up to 63 months)

Pubic hair was measured by the Tanner method on a scale of 1 to 6. A low grade (i.e. 1) corresponds to a pre-pubertal stage and a high grade (i.e. 5 or 6) to an adult stage. Percentage of patients who had stabilisation or regression (no change in grade or a reduced grade) of Tanner pubic hair pubertal stage is reported. Study treatment was to last until the end of the therapeutic period; visits for Months 36 and 48 were optional because if the girl was already 11 and the boy already 13, they would have finished the study at a prior visit. The Final Visit was to occur only if the child did not end the study by a complete visit such as at Months 24, 36 or 48. Please also note the additional post-hoc analysis for percentage of children with a stabilisation or regression of Tanner pubic hair pubertal stage which applied the variable Last Visit on Treatment instead of Final Visit.

Trial Locations

Locations (10)

Hôpital des Enfants

🇫🇷

Toulouse, France

Hôpital Hôtel Dieu (CHU)

🇫🇷

Angers, France

Hôpital Flaubert

🇫🇷

Le Havre, France

Hôpital Archet II

🇫🇷

Nice, France

American Memorial Hospital

🇫🇷

Reims, France

Hôpital Charles Nicolle

🇫🇷

Rouen, France

Hôpital Hautepierre

🇫🇷

Strasbourg, France

Hôpital de la Gespe

🇫🇷

Tarbes, France

Medical Centre

🇫🇷

Bordeaux, France

Hôpital Robert Debré

🇫🇷

Paris, France

© Copyright 2025. All Rights Reserved by MedPath