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Study of Ribociclib With Everolimus + Exemestane in HR+ HER2- Locally Advanced/Metastatic Breast Cancer Post Progression on CDK 4/6 Inhibitor.

Phase 1
Completed
Conditions
Breast Cancer
Interventions
Registration Number
NCT02732119
Lead Sponsor
Novartis Pharmaceuticals
Brief Summary

The purpose of this study is determine if the triplet combination of ribociclib, everolimus and exemastane is safe and effective in the treatment of locally advanced/metastatic breast cancer following treatment with a CDK 4/6 inhibitor

Detailed Description

This trial had two phases. The purpose of Phase I dose escalation and dose de-escalation was to determine the maximum tolerated doses (MTDs) and/or identify the recommended Phase II dose (RP2D) of the combination treatment of ribociclib+ everolimus + exemestane. The dosing was continuous in adult men and postmenopausal women with HR+ HER2-negative advanced breast cancer which was resistant to the non-steroidal aromatase inhibitors, fulvestrant or tamoxifen.

The purpose of the phase II portion of this trial was to evaluate the anti-tumor activity of exemestane, everolimus and ribociclib combination therapy following progression on a CDK 4/6 inhibitor.

The planned duration of the study was 30 months.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
104
Inclusion Criteria
  • Adult men and women
  • Patient has a confirmed diagnosis of estrogen-receptor positive and/or progesterone receptor positive breast cancer by local laboratory and has HER2-negative breast cancer
  • Patient must have either measurable disease by RECIST 1.1 or bone lesions in absence of measurable disease.
  • ECOG Performance Status 0 - 1
  • Disease refractory to either, AI, tamoxifen or fulvestrant
  • Previously treated on any CDK 4/6 inhibitor.
  • Patient has adequate bone marrow and organ function.
Exclusion Criteria
  • Patient with symptomatic visceral disease or any disease burden that makes the patient ineligible for endocrine therapy per the investigator's best judgment.
  • Patient has received more than one line of chemotherapy for advanced disease.
  • Previous treatment with mTOR inhibitors, or exemestane for advanced disease.
  • Progressed on more than one CDK 4/6 inhibitor
  • Patient with CNS involvement unless they are at least 4 weeks from prior therapy completion.
  • Clinically significant, uncontrolled heart disease and/or recent cardiac events.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Cohort CExemestaneRibociclib (200 mg daily), everolimus (5 mg daily) and exemestane (25 mg daily) taken orally
Cohort ARibociclibRibociclib (250 mg daily), everolimus (2.5 mg daily) and exemestane (25 mg daily) taken orally for 28 days. If no DLTs occurred, progressed to Cohort B
Cohort CRibociclibRibociclib (200 mg daily), everolimus (5 mg daily) and exemestane (25 mg daily) taken orally
Cohort CEverolimusRibociclib (200 mg daily), everolimus (5 mg daily) and exemestane (25 mg daily) taken orally
Group 2EverolimusRibociclib (200 mg daily), everolimus (5 mg daily) and exemestane (25 mg daily) taken orally
Group 2ExemestaneRibociclib (200 mg daily), everolimus (5 mg daily) and exemestane (25 mg daily) taken orally
Cohort AEverolimusRibociclib (250 mg daily), everolimus (2.5 mg daily) and exemestane (25 mg daily) taken orally for 28 days. If no DLTs occurred, progressed to Cohort B
Cohort AExemestaneRibociclib (250 mg daily), everolimus (2.5 mg daily) and exemestane (25 mg daily) taken orally for 28 days. If no DLTs occurred, progressed to Cohort B
Cohort BRibociclibRibociclib (300 mg daily), everolimus (2.5 mg daily) and exemestane (25 mg daily) taken orally
Cohort BEverolimusRibociclib (300 mg daily), everolimus (2.5 mg daily) and exemestane (25 mg daily) taken orally
Cohort BExemestaneRibociclib (300 mg daily), everolimus (2.5 mg daily) and exemestane (25 mg daily) taken orally
Group 1RibociclibRibociclib (300 mg daily), everolimus (2.5 mg daily) and exemestane (25 mg daily) taken orally
Group 1EverolimusRibociclib (300 mg daily), everolimus (2.5 mg daily) and exemestane (25 mg daily) taken orally
Group 2RibociclibRibociclib (200 mg daily), everolimus (5 mg daily) and exemestane (25 mg daily) taken orally
Group 1ExemestaneRibociclib (300 mg daily), everolimus (2.5 mg daily) and exemestane (25 mg daily) taken orally
Primary Outcome Measures
NameTimeMethod
Participants With Dose Limiting Toxicities by Preferred Term in Cycle 1 (28 Days) - in Phase IBaseline up to 28 days

A dose-limiting toxicity (DLT) is defined as an adverse event or abnormal laboratory value assessed as having a reasonably possible relationship to the study medication(s) and is unrelated to disease, disease progression, inter-current illness, or concomitant medications that occurs within the first 28 days of treatment (cycle 1) and meets any of the criteria defined in the protocol. National Cancer Institute Common Terminology Criteria for Adverse events (NCI CTCAE) version 4.03 will be used for all grading.

Clinical Benefit Rate as Per Central Review by Group- Phase IIFrom baseline up to 24 weeks

Clinical Benefit Rate (CBR) is defined as the percentage of participants with a complete response (CR) or partial response (PR) or with stable disease (SD) as per Response Evaluation Criteria in Solid Tumors (RECIST) V1.1 or Non-Complete Response or Non-Progressive Disease (NCRNPD) during first 24 weeks of first dose. CR=disappearance of all non-nodal target lesions, PR=at least a 30% decrease in the sum of diameter of all target lesions, SD=neither sufficient shrinkage to qualify for PR or CR nor an increase in lesions which would qualify for progressive disease (PD), PD=at least a 20% increase in the sum of diameter of all target lesions.

The hypothesis was to be rejected if the lower limit of the 95% Confidence Interval for Clinical Benefit Rate (CBR) was greater than 10%.

Best Overall Responses (BOR) Summary Table as Per Central Review by Group - Phase IIBaseline up to 24 weeks and at 24 weeks

Complete response (CR) or partial response (PR), or stable disease (SD) at 24 weeks as per Response Evaluation Criteria in Solid Tumors (RECIST) v1.1 or Non-CR Non-PD (NCRNPD) at Week 24.

Secondary Outcome Measures
NameTimeMethod
Clinical Benefit Rate as Per Central Review by Dose Cohort - Phase IBaseline up to 24 weeks and at week 24

Clinical Benefit Rate (CBR) is defined as the percentage of patients with a complete response (CR) or partial response (PR) or with stable disease (SD) at 24 weeks as per Response Evaluation Criteria in Solid Tumors (RECIST) V1.1 or Non-Complete Response Non-Progressive Disease (NCRNPD) up to Week 24 and at Week 24.

Summary of Progression-free Survival (PFS) (Months), as Per Central Review by Group - Phase IIBaseline up to approximately 32 months

Progression is defined as \<= 12 weeks after randomization/ start of treatment (and not qualifying for CR, PR or SD).

Overall Survival (OS) by Group - Phase IIBaseline up to approximately 32 months

Overall survival is the time from date of first treatment to the date of death due to any cause. If a patient is not known to have died, survival will be censored at the last date of contact.

Duration of Overall Response (DOR) by Group - Phase IIBaseline up to approximately 16 months

Patients whose best response is complete response (CR) or partial response (PR). The start date is the date of first documented response (CR or PR) and the end date is the date of first documented progression or death due to underlying cancer.

Time to Definitive Deterioration of ECOG Performance Status in One Category of the Score by Group - Phase IIBaseline up to approximately 8 months

Time to definitive deterioration of ECOG performance status in one category of score is defined as the time from the date of randomization to the date of event, which is defined as at least one score lower than the baseline.

Everolimus Pharmacokinetic Plasma Concentrations - Phase IICycle 1,2: Day 1 and 15 - pre-dose, 2 and 4 hour post dose, Cycle 3 , Day 1 - pre-dose

Plasma concentrations; below limit of quantitation values set to zero

Everolimus Pharmacokinetic Plasma Concentrations by Cohort - Phase ICycle 1,2: Day 1 and 15 - pre-dose, 2 and 4 hour post dose, Cycle 3 , Day 1 - pre-dose

Plasma concentrations; below limit of quantitation values set to zero

Best Overall Responses (BOR) Summary Table as Per Central Review by Cohort - Phase IFrom baseline up to 24 weeks

Complete response (CR) or partial response (PR), or stable disease (SD)as per Response Evaluation Criteria in Solid Tumors (RECIST) v1.1 or Non-CR Non-PD (NCRNPD)

Trial Locations

Locations (25)

Florida Cancer Specialists FL Cancer Specialists

🇺🇸

Fort Myers, Florida, United States

St. Luke's Cancer Institute Regulatory

🇺🇸

Kansas City, Missouri, United States

Research Medical Center HCA Midwest Division

🇺🇸

Kansas City, Missouri, United States

Florida Cancer Research Institute Dept of Oncology

🇺🇸

Davie, Florida, United States

Yale University School of Medicine Smilow Cancer Hospital

🇺🇸

New Haven, Connecticut, United States

Highlands Oncology Group

🇺🇸

Fayetteville, Arkansas, United States

Washington University School of Medicine Washington U School of Medicin

🇺🇸

Saint Louis, Missouri, United States

UF Health Cancer Center at Orlando Health UF Health (4)

🇺🇸

Orlando, Florida, United States

University of Kansas Cancer Center Univ of KS CC Medical Pavilion

🇺🇸

Westwood, Kansas, United States

Penn State Hershey Cancer Institute

🇺🇸

Hershey, Pennsylvania, United States

Northwest Medical Specialties Dept of Onc

🇺🇸

Tacoma, Washington, United States

Central Coast Medical Oncology Corporation Onc Dept

🇺🇸

Santa Maria, California, United States

Saint Barnabas Medical Center

🇺🇸

Livingston, New Jersey, United States

Florida Cancer Specialists-North

🇺🇸

Saint Petersburg, Florida, United States

UCLA Department of Medicine UCLA Hematology/Oncology

🇺🇸

Los Angeles, California, United States

University of California San Francisco Comprehensive Cancer Center

🇺🇸

San Francisco, California, United States

Atlanta Cancer Center

🇺🇸

Atlanta, Georgia, United States

Massachusetts General Hospital Mass Gen Hos Cancer Center

🇺🇸

Boston, Massachusetts, United States

Henry Ford Health System

🇺🇸

Detroit, Michigan, United States

University of Pennsylvania Medical Center Abramson Cancer Ctr of the Uni

🇺🇸

Philadelphia, Pennsylvania, United States

Sarah Cannon Research Institute Sarah Cannon Research Insti

🇺🇸

Nashville, Tennessee, United States

MD Anderson Cancer Center/University of Texas MDACC

🇺🇸

Houston, Texas, United States

Huntsman Cancer Institute Huntsman Cancer Insti

🇺🇸

Salt Lake City, Utah, United States

Ironwood Cancer and Research Centers Ironwood Cancer

🇺🇸

Chandler, Arizona, United States

Oncology Consultants Oncology Consultants

🇺🇸

Houston, Texas, United States

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