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Evaluation of the complications of injecting a combination of two types of muscle-derived and adipose-derived stem cells in patients with fascioscapulohumeral dystrophy

Phase 1
Conditions
Facioscapulohumeral dystrophy.
Scapulohumeral muscular dystrophy
G71.02
Registration Number
IRCT20080728001031N25
Lead Sponsor
Royan Institute
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Complete
Sex
All
Target Recruitment
15
Inclusion Criteria

Facial muscles weakness including Frontalis, Orbicularis oculi, Orbicularis Oris
Having the FSHD phenotype including involvement of the biceps and triceps muscles
Confirmation of FSHD by genetic testing
Age: 15-50 years old

Exclusion Criteria

Comorbidities such as heart and respiratory disease and diabetes
Having a connective tissue or rheumatologic disease or a history of malignancy
Inability to sign consent
Advanced disease

Study & Design

Study Type
interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Percentage of people with side effects including hematoma, myalgia and mass at the injection site, decreased level of consciousness, nausea and vomiting, headache, diplopia, urinary and fecal impairments, shortness of breath, increase or decrease in blood pressure. Timepoint: 24 hours after injection - 1 month after injection - 2 months after injection - 4 months after injection - 6 months after injection - 12 months after injection. Method of measurement: Clinical examination and the side-effects questionnaire.
Secondary Outcome Measures
NameTimeMethod
Disease progression by measuring CPK. Timepoint: 24 hours after injection 1 month after injection 2 months after injection_ 4 months after injection_ 6 months after injection_ 12 months after injection. Method of measurement: Blood test.;Disease progression by measuring LDH. Timepoint: 24 hours after injection 1 month after injection 2 months after injection_ 4 months after injection_ 6 months after injection_ 12 months after injection. Method of measurement: Blood test.
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