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A Study of Pentosan Polysulfate Sodium and the Development of Pigmentary Maculopathy and Pigmentary Retinopathy

Completed
Conditions
Pigmentary Retinopathy
Pigmentary Maculopathy
Interstitial Cystitis
Registration Number
NCT05179460
Lead Sponsor
Janssen Research & Development, LLC
Brief Summary

The purpose of this study is to evaluate incidence and prevalence rates of the study endpoints (pigmentary maculopathy \[PM\]/ pigmentary retinopathy \[PR\]/Any, PM/PR/ pentosan polysulfate sodium \[PPS\], and PM/PR/Non-PPS) in relation to PPS exposure, and in participants with interstitial cystitis (IC) but not exposed to PPS; changes in visual acuity (VA) over time; participant treatment journey leading to PPS treatment, and potential risk factors associated with the occurrence of PM/PR/PPS.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
2
Inclusion Criteria
  • Participants must have at least 6 months baseline information prior to index date (this may apply to the relevant databases, if the study participants are identified and the outcomes are ascertained via multiple linked data source) For the pentosan polysulfate sodium (PPS) Cohort
  • Participants must have records in both the intelligent research in sight (IRIS) database and the closed claims portion of the Komodo claims database and have at least one record of PPS dispensing For the interstitial cystitis (IC) Cohort not exposed to PPS
  • Participants must have records in both the IRIS database and the closed claims portion of the claims database; have at least one diagnosis of IC; and have no record of PPS dispensing
Exclusion Criteria
  • Evaluated based on the Komodo database. Participants will be excluded from the study if they have no information on age or sex (or both)

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Overall Cohort: Prevalence Rate of PM/PR/Any CasesData analysed retrospectively from 01-Jan-2015 to 31-Mar-2021 will be examined

Prevalence rate is defined as number of prevalent cases per number of target cohort assessed (example, number of participants exposed to PPS).

Overall Cohort: Number of PM/PR/PPS Cases Among the PM/PR/Any CasesData analysed retrospectively from 01-Jan-2015 to 31-Mar-2021 will be examined

Number of PM/PR/PPS cases among the PM/PR/any cases will be reported.

Clean Cohort: Prevalence Rate of PM/PR/PPSData analysed retrospectively from 22-May-2018 to 31-Mar-2021 will be examined

Prevalence rate is defined as number of prevalent cases per number of target cohort assessed (example, number of participants exposed to PPS).

Clean Cohort: Incidence Rate of PM/PR/PPSData analysed retrospectively from 22-May-2018 to 31-Mar-2021 will be examined

Incidence rate is defined as number of incident cases per number of all participants at risk (that is, number of all participants exposed to PPS). Incidence rate is calculated by using formula: incidence rate (per 100 person-years)= number of incidence cases divided by number of person-years time at risk.

Clean Cohort: Incidence Rate of Pigmentary Maculopathy (PM)/ Pigmentary Retinopathy (PR)/Any CasesData analysed retrospectively from 22-May-2018 to 31-Mar-2021 will be examined

Incidence rate is defined as number of incident cases per number of all participants at risk (that is, number of all participants exposed to pentosan polysulfate sodium \[PPS\]). Incidence rate is calculated by using formula: incidence rate (per 100 person-years)= number of incidence cases divided by number of person-years time at risk.

Overall Cohort: Incidence Rate of PM/PR/PPSData analysed retrospectively from 01-Jan-2015 to 31-Mar-2021 will be examined

Incidence rate is defined as number of incident cases per number of all participants at risk (that is, number of all participants exposed to pentosan polysulfate sodium \[PPS\]). Incidence rate is calculated by using formula: incidence rate (per 100 person-years)= number of incidence cases divided by number of person-years time at risk.

Clean Cohort: Incidence Rate of PM/PR/Non-PPSData analysed retrospectively from 22-May-2018 to 31-Mar-2021 will be examined

Incidence rate is defined as number of incident cases per number of all participants at risk (that is, number of all participants not exposed to PPS). Incidence rate is calculated by using formula: incidence rate (per 100 person-years)= number of incidence cases divided by number of person-years time at risk.

Clean Cohort: Prevalence Rate of PM/PR/Any CasesData analysed retrospectively from 22-May-2018 to 31-Mar-2021 will be examined

Prevalence rate is defined as number of prevalent cases per number of target cohort assessed (example, number of participants exposed to PPS).

Overall Cohort: Incidence Rate of PM/PR/Any CasesData analysed retrospectively from 01-Jan-2015 to 31-Mar-2021 will be examined

Incidence rate is defined as number of incident cases per number of all participants at risk (that is, number of all participants exposed to pentosan polysulfate sodium \[PPS\]). Incidence rate is calculated by using formula: incidence rate (per 100 person-years)= number of incidence cases divided by number of person-years time at risk.

Overall Cohort: Change in VA in Relation to PM/PR/Non-PPSData analysed retrospectively from 01-Jan-2015 to 31-Mar-2021 will be examined

Change in VA in relation to study endpoint (PM/PR/Non-PPS) will be reported. It will be assessed based on the following categories: a) No change (refers to \<1 line of worsening or improvement, considered not clinically meaningful); b) 1 to \<3 lines of worsening; c) \>= 3 lines of worsening; d) 1 to \<3 lines of improvement; e) \>= 3 lines of improvement.

Clean Cohort: Prevalence Rate of PM/PR/Non-PPSData analysed retrospectively from 22-May-2018 to 31-Mar-2021 will be examined

Prevalence rate is defined as number of prevalent cases per number of target cohort assessed (example, number of participants not exposed to PPS).

Clean Cohort: Change in Visual Acuity (VA) in Relation to PPS DoseData analysed retrospectively from 22-May-2018 to 31-Mar-2021 will be examined

Change in VA in relation to PPS dose will be reported. It will be assessed based on the following categories: a) No change (refers to less than \[\<\] 1 line of worsening or improvement, considered not clinically meaningful); b) 1 to \<3 lines of worsening; c) greater than or equal to (\>=) 3 lines of worsening; d) 1 to \<3 lines of improvement; e) \>= 3 lines of improvement.

Clean Cohort: Change in VA in Relation to PM/PR/Any CasesData analysed retrospectively from 22-May-2018 to 31-Mar-2021 will be examined

Change in VA in relation to study endpoint (PM/PR/Any) will be reported. It will be assessed based on the following categories: a) No change (refers to \<1 line of worsening or improvement, considered not clinically meaningful); b) 1 to \<3 lines of worsening; c) \>= 3 lines of worsening; d) 1 to \<3 lines of improvement; e) \>= 3 lines of improvement.

IC Cohort: Change in VA Based on Time Between the First and Last VA Measurement in Matched CohortsData analysed retrospectively from 01-Jan-2015 to 31-Mar-2021 will be examined

Change in VA based on time between the first and last VA measurement in matched cohorts among participants exposed to PPS and without exposure to PPS will be reported. It will be assessed based on the following categories: a) No change (refers to \<1 line of worsening or improvement, considered not clinically meaningful); b) 1 to \<3 lines of worsening; c) \>= 3 lines of worsening; d) 1 to \<3 lines of improvement; e) \>= 3 lines of improvement.

Overall Cohort: Prevalence Rate of PM/PR/PPSData analysed retrospectively from 01-Jan-2015 to 31-Mar-2021 will be examined

Prevalence rate is defined as number of prevalent cases per number of target cohort assessed (example, number of participants exposed to PPS).

Clean Cohorts: Change in VA in Relation to PM/PR/Non-PPSData analysed retrospectively from 22-May-2018 to 31-Mar-2021 will be examined

Change in VA in relation to study endpoint (PM/PR/Non-PPS) will be reported. It will be assessed based on the following categories: a) No change (refers to \<1 line of worsening or improvement, considered not clinically meaningful); b) 1 to \<3 lines of worsening; c) \>= 3 lines of worsening; d) 1 to \<3 lines of improvement; e) \>= 3 lines of improvement.

Overall Cohort: Change in VA in Relation to PM/PR/Any CasesData analysed retrospectively from 01-Jan-2015 to 31-Mar-2021 will be examined

Change in VA in relation to study endpoint (PM/PR/Any) will be reported. It will be assessed based on the following categories: a) No change (refers to \<1 line of worsening or improvement, considered not clinically meaningful); b) 1 to \<3 lines of worsening; c) \>= 3 lines of worsening; d) 1 to \<3 lines of improvement; e) \>= 3 lines of improvement.

Clean Cohort: Change in VA in Relation to PM/PR/PPSData analysed retrospectively from 22-May-2018 to 31-Mar-2021 will be examined

Change in VA in relation to study endpoint (PM/PR/PPS) will be reported. It will be assessed based on the following categories: a) No change (refers to \<1 line of worsening or improvement, considered not clinically meaningful); b) 1 to \<3 lines of worsening; c) \>= 3 lines of worsening; d) 1 to \<3 lines of improvement; e) \>= 3 lines of improvement.

Overall Cohort: Change in Visual Acuity (VA) in Relation to PPS DoseData analysed retrospectively from 01-Jan-2015 to 31-Mar-2021 will be examined

Change in VA in relation to PPS dose will be reported. It will be assessed based on the following categories: a) No change (refers to less than \[\<\] 1 line of worsening or improvement, considered not clinically meaningful); b) 1 to \<3 lines of worsening; c) greater than or equal to (\>=) 3 lines of worsening; d) 1 to \<3 lines of improvement; e) \>= 3 lines of improvement.

Overall Cohort: Change in VA in Relation to PM/PR/PPSData analysed retrospectively from 01-Jan-2015 to 31-Mar-2021 will be examined

Change in VA in relation to study endpoint (PM/PR/PPS) will be reported. It will be assessed based on the following categories: a) No change (refers to \<1 line of worsening or improvement, considered not clinically meaningful); b) 1 to \<3 lines of worsening; c) \>= 3 lines of worsening; d) 1 to \<3 lines of improvement; e) \>= 3 lines of improvement.

IC Cohort: Change in VA in Relation to PM/PR/Any CasesData analysed retrospectively from 01-Jan-2015 to 31-Mar-2021 will be examined

Change in VA in relation to study endpoint (PM/PR/Any) will be reported. It will be assessed based on the following categories: a) No change (refers to \<1 line of worsening or improvement, considered not clinically meaningful); b) 1 to \<3 lines of worsening; c) \>= 3 lines of worsening; d) 1 to \<3 lines of improvement; e) \>= 3 lines of improvement.

IC Cohort: Change in VA Based on AgeData analysed retrospectively from 01-Jan-2015 to 31-Mar-2021 will be examined

Change in VA based on age among participants exposed to PPS and without exposure to PPS will be reported. It will be assessed based on the following categories: a) No change (refers to \<1 line of worsening or improvement, considered not clinically meaningful); b) 1 to \<3 lines of worsening; c) \>= 3 lines of worsening; d) 1 to \<3 lines of improvement; e) \>= 3 lines of improvement.

IC Cohort: Change in VA Based on SexData analysed retrospectively from 01-Jan-2015 to 31-Mar-2021 will be examined

Change in VA based on sex among participants exposed to PPS and without exposure to PPS will be reported. It will be assessed based on the following categories: a) No change (refers to \<1 line of worsening or improvement, considered not clinically meaningful); b) 1 to \<3 lines of worsening; c) \>= 3 lines of worsening; d) 1 to \<3 lines of improvement; e) \>= 3 lines of improvement.

Interstitial Cystitis (IC) Cohort: Incidence Rate of PM/PR/Any Cases Among the Participants with IC and No-Exposure to PPSData analysed retrospectively from 01-Jan-2015 to 31-Mar-2021 will be examined

Incidence rate is defined as number of incident cases per number of all participants at risk (that is, number of all participants not exposed to PPS). Incidence rate is calculated by using formula: incidence rate (per 100 person-years)= number of incidence cases per number of person-years time at risk.

Secondary Outcome Measures
NameTimeMethod
Demographic characteristics of Cohorts: RaceBaseline

Demographic characteristics of cohorts (race including Asian, black or African American, other, White or Caucasian) will be reported.

Demographic characteristics of Cohorts: AgeBaseline

Demographic characteristics of cohorts (age) will be reported.

Demographic characteristics of Cohorts: SexBaseline

Demographic characteristics of cohorts (sex) will be reported.

Demographic characteristics of Cohorts: EthnicityBaseline

Demographic characteristics of cohorts (ethnicity including Hispanic and non-Hispanic) will be reported.

Number of Participants with ComorbiditiesBaseline

Number of participants with general comorbidities (diabetes, hypertension, hypercholesterolemia, vaginitis, urinary tract infection \[UTI\], detrusor instability, urge incontinence, and overactive bladder, autoimmune disease, Malignant tumor(s) of head and neck \[plus documentation of radiation therapy\] and Radiation cystitis) and ocular comorbidities (diabetic retinopathy, diabetic macular edema, optic neuropathy, glaucoma, glaucoma-related procedure, cataract \[diagnosis\], cataract \[procedure\]) will be reported.

Number of Participants who had Provider CharacteristicsBaseline

Number of participants who had provider characteristics (treating provider specialty \[retina specialist, non-retina specialist, general ophthalmologist, optometrist\]; rural or non-rural location of index practice \[rural/non-rural; United States Department of Agriculture Economic research service 2010 classification\]) will be reported.

Overall Cohort: Distribution of International Classification of Diseases (ICD)-9/10 CodesData analysed retrospectively from 01-Jan-2015 to 31-Mar-2021 will be examined

ICD-9/10 codes are compared among the participants who are exposed to PPS will be reported.

Participant's Journey to PPSData analysed retrospectively from 01-Jan-2015 to 31-Mar-2021 will be examined

Participant's journey to PPS is defined as the sequence of medications and other interventions the participant received before and after receiving PPS.

Trial Locations

Locations (1)

Janssen R&D, LLC

🇺🇸

Titusville, New Jersey, United States

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