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Phase 1 Study of BPN14770 in Participants With Hepatic Impairment and Healthy Controls

Phase 1
Not yet recruiting
Conditions
Hepatic Impairment
Interventions
Registration Number
NCT07018492
Lead Sponsor
Shionogi
Brief Summary

The primary purpose of this study is to assess the pharmacokinetics (PK) of BPN14770 after a single oral administration of BPN14770 in participants with mild, moderate, and severe liver impairment compared with control participants with normal hepatic function.

Detailed Description

Not available

Recruitment & Eligibility

Status
NOT_YET_RECRUITING
Sex
All
Target Recruitment
32
Inclusion Criteria
  • Considered to be healthy (for healthy participants) or medically stable (for participants with hepatic impairment), as determined by medical evaluation.

  • Body weight ≥ 50 kilograms (kg) and body mass index (BMI) within the range ≥ 18.5 to < 40.0 kilograms per square meter (kg/m^2).

  • A diagnosis of clinically stable hepatic disease for at least 1 month prior to the screening visit, confirmed by medical history or previous confirmation of hepatic cirrhosis by liver biopsy or medical imaging technique.

  • Mild, moderate, and severe hepatic impairment based on the Child-Pugh classification score at the screening visit and Day ˗1 to determine eligibility:

    • Mild (Class A) hepatic impairment (Child-Pugh classification score 5 to 6)
    • Moderate (Class B) hepatic impairment (Child-Pugh classification score 7 to 9)
    • Severe (Class C) hepatic impairment (Child-Pugh classification score 10 to 15)
  • Healthy Participants matched to each participant with moderate hepatic impairment with respect to sex, age (± 10 years), and BMI (± 10%)

Key

Exclusion Criteria
  • History or presence of/significant history of or current cardiovascular, respiratory, hepatic, gastrointestinal, endocrinological, hematological, or neurological disorders capable of significantly altering the absorption, metabolism, or elimination of drugs; constituting a risk when taking the study intervention; or interfering with the interpretation of data, in the judgment of the investigator.

  • Blood loss or blood donation that exceeds 500 milliliters (mL) within 56 days prior to or at the screening visit or donation of any amount of blood from the screening visit until admission to the clinical research unit (CRU).

  • Healthy participants:

    • Clinical laboratory values outside the reference range during the screening period or on Day ˗1 and considered clinically significant by the investigator
    • Alanine aminotransferase or aspartate aminotransferase > 1.5 * the upper limit of normal (ULN) or bilirubin ≥ 1.0 * the ULN.
  • Participants with hepatic impairment:

    • Participant with clinically significant laboratory values in the opinion of the investigator or outside the acceptable ranges or limits during the screening period.

Note: Other protocol defined Inclusion/Exclusion criteria may apply.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Group 1: Mild HIBPN14770Participants with mild hepatic impairment who have a Child Pugh classification system score of Class A will receive a single oral dose of BPN14770 capsule on Day 1.
Group 2: Moderate HIBPN14770Participants with moderate hepatic impairment who have a Child Pugh classification system score of Class B will receive a single oral dose of BPN14770 capsule on Day 1.
Group 3: Severe HIBPN14770Participants with severe hepatic impairment who have a Child Pugh classification system score of Class C will receive a single oral dose of BPN14770 capsule on Day 1.
Group 4: Normal Hepatic FunctionBPN14770Participants with normal hepatic function will receive a single oral dose of BPN14770 capsule on Day 1.
Primary Outcome Measures
NameTimeMethod
Area Under the Plasma Concentration Time Curve Extrapolated from Time 0 to Infinity (AUCinf) of BPN14770Predose up to 240 hours postdose
Maximum Observed Plasma Concentration (Cmax) of BPN14770Predose up to 240 hours postdose
Time Maximum Observed Plasma Concentration (Tmax) of BPN14770Predose up to 240 hours postdose
Secondary Outcome Measures
NameTimeMethod
Number of Participants With Treatment Emergent Adverse Events (TEAEs)Up to 15 days postdose

Trial Locations

Locations (3)

Division of Clinical Pharmacology, University of Miami

🇺🇸

Miami, Florida, United States

Orlando Clinical Research Center

🇺🇸

Orlando, Florida, United States

American Research Corporation dba Texas Liver Institute

🇺🇸

San Antonio, Texas, United States

Division of Clinical Pharmacology, University of Miami
🇺🇸Miami, Florida, United States
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