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Pazopanib as treatment for advanced gastrointestinal stromal tumors not any longer responding to standard treatment with the drugs imatinib or sunitinib - A study without comparator as placebo or another drug, performed at many sites and sponsored by the Scandinavian Sarcoma Group

Phase 1
Conditions
Gatrointestinal stromal tumor (GIST)
Therapeutic area: Diseases [C] - Cancer [C04]
Registration Number
EUCTR2011-004404-37-DE
Lead Sponsor
Scandinavian Sarcoma Group
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
ot Recruiting
Sex
All
Target Recruitment
72
Inclusion Criteria

a) metastatic and/or locally advanced GIST
b) measurable disease as defined by RECIST
c) progressive disease after both imatinib and sunitinib treatment, and also after nilotinib if this drug ha been given
d) no other tyrosin kinase inhibitors given than imatinib, sunitinib, and nilotinib
e) age at least 18 years
f) WHO performance status 0-2
g) resolution of toxic side effects from earlier treatment
h) sufficient organ functions as defined in the protocol
i) acceptence to use adequate contraception throughout the study period for women with childbearing potential
j) written informed consent
Are the trial subjects under 18? no
Number of subjects for this age range:
F.1.2 Adults (18-64 years) yes
F.1.2.1 Number of subjects for this age range 30
F.1.3 Elderly (>=65 years) yes
F.1.3.1 Number of subjects for this age range 42

Exclusion Criteria

a) prior malignancy if claiming active treatment or otherwise is judged to be of significance for the study treatment
b) clinically significant gastrointestinal bleeding
c) uncontrolled infection of significance
d) major surgery or trauma within 28 days priot to the start of study treatment
e) active bleeding or bleeding diathesis
f) uncontrolled hypertension
g) endobronchial lesions or lesions infiltrating major pulmonary vessels
h) medical, psychiatric or other condition that could interfere with safety or compliance
i) pregnancy or lactation

Study & Design

Study Type
Interventional clinical trial of medicinal product
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Objective: Secondary objectives<br>1. Overall response rate (ORR) defined as the fraction of patients ever achieving CR or PR during protocol treatment<br>2. Progression free survival (PFS) defined as the time from start of pazopanib to progressive disease according to RECIST version 1.1<br>12 of treatment<br>3. Toxicity defined as adverse events and abnormal laboratory test results<br><br>Subgroup analysis<br>1. DCR in relation to mutational status of primary tumor sample<br>2. DCR in relation to plasma concentration of pazopanib at week;Primary end point(s): Disease control rate (DCR=CR+PR+SD) at 12 weeks from start of pazopanib treatment according to RECIST version 1.1;Timepoint(s) of evaluation of this end point: 12 weeks from start of treatment;Main Objective: Calculate the disease control rate (DCR)=complete remission (CR)+partial remission (PR) + stable disease (SD) at 12 weeks
Secondary Outcome Measures
NameTimeMethod
Secondary end point(s): Secondary objectives<br>1. Overall response rate (ORR) defined as the fraction of patients ever achieving CR or PR during protocol treatment<br>2. Progression free survival (PFS) defined as the time from start of pazopanib to progressive disease according to RECIST version 1.1<br>12 of treatment<br>3. Toxicity defined as adverse events and abnormal laboratory test results<br><br>Subgroup analysis<br>1. DCR in relation to mutational status of primary tumor sample<br>2. DCR in relation to plasma concentration of pazopanib at week;Timepoint(s) of evaluation of this end point: Secondary objectives<br>For 1, 2, and 3 above - continously during protocol treatment; for 5 also including 30 days after end of treatment<br><br>Subgroup analysis<br>For 1 and 2 - at week 12 of treatment
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