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Study of the Mechanisms of Action of Cladribine in Multiple Sclerosis

Not Applicable
Conditions
Multiple Sclerosis
Interventions
Other: biological collection
Registration Number
NCT04821596
Lead Sponsor
University Hospital, Rouen
Brief Summary

The main objective of the project is therefore to study and thus better understand the immunomodulatory / anti-inflammatory effects of cladribine during multiple sclerosis.

Most current and developing therapies targeting the immune system have no effect on the progressive phase of MS, during which neurodegeneration plays a predominant role. As mentioned above, the very promising results of clinical trials with cladribine tablets for the early and progressive phase of the disease have revealed immunomodulatory properties and suggested potential neuroprotective effects.

It therefore plans to further dissect one of these two parameters by designing in vitro studies with peripheral blood mononuclear cells (PBMC) from healthy donors and MS patients.

Detailed Description

Recent clinical trials have reported a remarkable therapeutic efficacy of cladribine tablets not only in the early and recurrent phases of the disease, but also in progressive multiple sclerosis. However, its role on the immune and nervous systems has hardly been studied, although these studies suggest that CoA may exert anti-inflammatory and neuroprotective actions. Thus, the objective is to better understand/describe how cladribine acts during MS and to demonstrate whether CoA: (1) is able to effectively modulate pro-inflammatory immune processes and (2) has powerful neuroprotective properties. Ultimately, it will provide proof of concept that cladribine can be used not only in the early but also in the progressive phase of MS.

To address this hypothesis, the goal is to study the beneficial immunomodulatory/anti-inflammatory effects of cladribine on multiple sclerosis.

The main objective of this project is therefore to study and thus better understand the immunomodulatory / anti-inflammatory effects of cladribine during multiple sclerosis.

Most current and developing therapies targeting the immune system have no effect on the progressive phase of MS, during which neurodegeneration plays a predominant role. As mentioned above, the very promising results of clinical trials with cladribine tablets for the early and progressive phase of the disease have revealed immunomodulatory properties and suggested potential neuroprotective effects.

It therefore plans to further dissect one of these two parameters by designing in vitro studies with peripheral blood mononuclear cells (PBMC) from healthy donors and MS patients.

Recruitment & Eligibility

Status
UNKNOWN
Sex
All
Target Recruitment
75
Inclusion Criteria
  • Major Multiple Sclerosis (MS) Patients
  • RR MS patients without treatment (early stage disease) Or RR MS patients treated with first-line compounds (IFNβ, glatiramer acetate, teriflunomide and dimethyl fumarate, ...).

Or RR MS patients treated with second-line compounds (natalizumab and fingolimod, ...) RR MS patients treated with third-line compounds (alemtuzumab, ...) Or Patients with progressive MS

  • Patients who have read and understood the information letter and signed the consent form
  • Person affiliated to a social security system
Exclusion Criteria
  • Patients under 18 years of age or over 65 years of age,
  • Patients who have benefited from immunosuppressive treatments for other autoimmune or cancerous pathologies,
  • Patients receiving treatments for multiple sclerosis and participating in phase 2, 3 or 4 protocols will be excluded.
  • Patients who have been treated for less than 1 year with cladribine, daclizumab, ocrelizumab, rituximab will be excluded.
  • Patients who have received mitoxantrone or a stem cell transplant,
  • Regulatory Criteria :
  • Person deprived of liberty by an administrative or judicial decision
  • Person placed under legal protection, sub-tutorship or curatorship

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Multiple Sclerosis Patientsbiological collectionMultiple Sclerosis Patients usually followed by Dr. Bourre as part of his consultation at the Rouen University Hospital will be offered the opportunity to participate in this study if they meet the selection criteria.
Primary Outcome Measures
NameTimeMethod
Description of cladribine's effects on immune system of multiple sclerosis patientsThrough study completion, of 1 year

Analysis of T cell response by flow cytometry

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (1)

Rouen University Hospital

🇫🇷

Rouen, France

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