MedPath

2-305P3E

Phase 3
Completed
Conditions
Congenital haemophilia with inhibitors
Registration Number
JPRN-jRCT2080225237
Lead Sponsor
KM Biologics Co., Ltd.
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
completed
Sex
All
Target Recruitment
11
Inclusion Criteria

(1) Patients who are expected to complete the observation at week 24 of the preceding KD2-305 phase II/III study
(2) Patients who are considered eligible for the study by the investigator
(3) Patients who or whose legally acceptable representatives have provided written informed consent in hope of continuous administration

Exclusion Criteria

(1) Patients undergoing immune tolerance induction (ITI) treatment
(2) Patients with diseases that develop abnormality in the coagulation/fibrinolytic system other than the target disease of the study or suspected of such
(3) Patients with hypercoagulability or such possibilities
(4) Patients with a history of disseminated intravascular coagulation (DIC) or thromboembolism
(5) Patients with a history of shock or hypersensitivity to protein preparations such as blood derivatives
(6) Patients who have undergone surgical procedure and have not fully recovered when participating in the study or patients who are scheduled to undergo surgery during the study
(7) Patients with acquired immunodeficiency syndrome (AIDS) defining illness
(8) Patients with severe liver disorder or renal disorder
(9) Patients with current serious medical conditions such as malignant tumor or leukaemia who will or are highly likely to undergo chemotherapy or radiotherapy during the study
(10) Patients with hemolytic or blood loss anaemia
(11) Patients who are scheduled to participate in any other clinical studies during the study
(12) Patients who have received HEMLIBRA (R) Subcutaneous Injection within 4 months prior to the eligibility confirmation for the study
(13) Patients who are considered ineligible for the study by the investigator or subinvestigator for any other reason

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
safety<br>Number of cases, number of patients, and incidence rate of adverse events
Secondary Outcome Measures
NameTimeMethod
efficacy<br>1) Annual bleeding rate<br>2) Annual bleeding rate by bleeding site<br>3) Time for treatment
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