MedPath

Study to Assess the Efficacy and Safety of Simtuzumab (GS-6624) in Adults With Idiopathic Pulmonary Fibrosis (IPF)

Phase 2
Terminated
Conditions
Idiopathic Pulmonary Fibrosis
Interventions
Registration Number
NCT01769196
Lead Sponsor
Gilead Sciences
Brief Summary

The primary objectives of this study are to determine the effect of simtuzumab (GS-6624) on progression-free survival (PFS) as determined by either a categorical decline in forced vital capacity (FVC) or all-cause mortality, in all participants enrolled or in a subset of participants who are classified as lysyl oxidase-like-2 (LOXL2) high based on a prespecified level in serum at baseline.

Detailed Description

Not available

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
544
Inclusion Criteria
  • Male or female subjects from 45 to 85 years of age
  • Definite IPF within 3 years prior to screening
  • Be able to walk at least 50 meters

Key

Exclusion Criteria
  • Significant diseases other than IPF

  • Obstructive lung disease

  • Aortic aneurysm greater than or equal to 3.5 cm in diameter

  • Treatment with immunosuppressive, cytotoxic, or antifibrotic drugs < 28 days prior to randomization are not permitted.

    • N-acetylcysteine is permitted provided the individual has been on a stable dose for > 4 weeks prior to screening
    • Concomitant use of pirfenidone or nintedanib must be in accordance with the approved prescribing instructions in the country where the site is located
  • Individuals actively listed for lung transplant are excluded. However individuals at transplant centers with long waiting times (greater than 1 year) may be permitted to enter the study after discussion with Medical Monitor.

Note: Other protocol defined Inclusion/Exclusion criteria may apply.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Simtuzumab PlaceboSimtuzumab placeboParticipants will receive simtuzumab placebo for up to 254 weeks.
SimtuzumabSimtuzumabParticipants will receive simtuzumab for up to 254 weeks.
Primary Outcome Measures
NameTimeMethod
Progression Free SurvivalUp to 148 weeks

Progression free survival (PFS) was defined as the categorical decrease in forced vital capacity (FVC) % predicted (≥ 10% relative decrease in FVC and ≥ 5% absolute decrease in FVC from baseline) with confirmation at a consecutive visit at least 2 weeks later using the same criteria.

PFS Among the Participants With sLOXL2 ≥ 50th PercentileUp to 148 weeks
PFS Among the Participants With sLOXL2 ≥ 75th PercentileUp to 148 weeks
Secondary Outcome Measures
NameTimeMethod
Overall Survival (OS)Up to 151 weeks

Overall survival was defined as the time from randomization date to death that occurred prior to the last dose date plus 30 days.

Overall Survival Among the Participants With sLOXL2 ≥ 50th PercentileUp to 151 weeks
Overall Survival Among the Participants With sLOXL2 ≥ 75th PercentileUp to 151 weeks
Relative Change From Baseline in FVC % PredictedWeeks 54, 106, and 130

* FVC was defined as the volume of air (liters) that can forcibly be blown out after taking a full breath. FVC % predicted was defined as FVC % of the participant divided by the average FVC % in the population for any person of similar age, sex, and body composition.

* Adjusted means were from mixed model repeated measures (MMRM) model with baseline FVC % predicted, sLOXL2 level, concomitant pirfenidone/nintedanib use (never vs. ever), treatment, visit, and treatment-by-visit interaction terms, including all data up to Week 130

* The relative change was calculated as 100% \* ( value at later time point minus value at baseline ) / value at baseline, with lower values indicating a decrease and higher values indicating an increase.

Definite Acute Exacerbations of IPF Among Adjudicated Respiratory HospitalizationsUp to 148 weeks
Number of Adjudicated Respiratory Hospitalizations (ARP) Among Total HospitalizationsUp to 148 weeks
Number of Participants Experiencing Adjudicated Respiratory Deaths Among Those With Adjudicated DeathUp to 148 weeks
Absolute Change From Baseline in 6 Minute Walk Distance (6MWD)Weeks 58, 106, and 130

* Adjusted means were from MMRM model with baseline 6MWD, FVC % predicted, sLOXL2 level, concomitant pirfenidone/nintedanib use (never vs. ever), treatment, visit, and treatment-by-visit interaction terms, including all data up to Week 130.

* The absolute change was calculated as value at later time point minus value at baseline, with lower values indicating a decrease and higher values indicating an increase.

Absolute Change From Baseline in St. George's Respiratory Questionnaire (SGRQ) ScoreWeek 58, 106, and 130

* The SGRQ is a disease-specific questionnaire designed to measure impact on overall health, daily life, and perceived well-being in patients with obstructive airways disease. Patients respond to questions about symptoms (frequency \& severity) and impact components (social functioning and psychological disturbances resulting from airways disease). Scores range from 0 to 100, with higher scores indicating more limitations.

* The absolute change was calculated as value at later time point minus value at baseline, with lower values indicating a decrease and higher values indicating an increase.

Trial Locations

Locations (174)

Sarasota Memorial Hospital

🇺🇸

Sarasota, Florida, United States

University of Maryland

🇺🇸

Baltimore, Maryland, United States

University of Chicago

🇺🇸

Chicago, Illinois, United States

Cleveland Clinic

🇺🇸

Cleveland, Ohio, United States

Ohio State University

🇺🇸

Columbus, Ohio, United States

University Hospital of South Manchester NHS Foundation Trust

🇬🇧

Manchester, England, United Kingdom

HEGP

🇫🇷

Paris Cedex 15, Ile-de-france, France

Universitätsklinikum Leipzig

🇩🇪

Leipzig, Sachsen, Germany

University of Miami

🇺🇸

Miami, Florida, United States

Baylor College of Medicine

🇺🇸

Houston, Texas, United States

University of Cincinnati Medical Center

🇺🇸

Cincinnati, Ohio, United States

University of Cincinnati

🇺🇸

Cincinnati, Ohio, United States

Cliniques Universitaires UCL de Mont-Godinne

🇧🇪

Yvoir, Namur, Belgium

Royal Perth Hospital

🇦🇺

Perth, Western Australia, Australia

University of Florida

🇺🇸

Jacksonville, Florida, United States

Brigham and Women's Hospital

🇺🇸

Boston, Massachusetts, United States

Arizona Pulmonary Specialists, Ltd.

🇺🇸

Scottsdale, Arizona, United States

The University of Arizona

🇺🇸

Tucson, Arizona, United States

Albany Medical College

🇺🇸

Albany, New York, United States

Beth Israel Deaconess Medical Center

🇺🇸

Boston, Massachusetts, United States

University of Washington

🇺🇸

Seattle, Washington, United States

Weill Cornell Medical College

🇺🇸

New York, New York, United States

Hôpitaux Universitaires de Strasbourg

🇫🇷

Strasbourg, Alsace, France

Instytut Gruzlicy i Chorób Pluc

🇵🇱

Warszawa, Mazowieckie, Poland

Tulane University School of Medicine

🇺🇸

New Orleans, Louisiana, United States

The Alfred Hospital

🇦🇺

Melbourne, Victoria, Australia

Jamaica Hospital Medical Center

🇺🇸

Jamaica, New York, United States

Massachusetts General Hospital

🇺🇸

Boston, Massachusetts, United States

Medical University of South Carolina

🇺🇸

Charleston, South Carolina, United States

Robert Wood Johnson Medical School

🇺🇸

New Brunswick, New Jersey, United States

Institut Universitaire de Cardiologie et de Pneumologie de Québec

🇨🇦

Quebec City, Quebec, Canada

Dartmouth Hitchcock Medical Center

🇺🇸

Lebanon, New Hampshire, United States

Samodzielny Publiczny Szpital Kliniczny nr 3 w Zabrzu Slaskiego Uniwersytetu Medycznego w Katowicach

🇵🇱

Zabrze, Slaskie, Poland

Pulmonary and Allergy Associates, PA

🇺🇸

Summit, New Jersey, United States

Hospital Universitario Central de Asturias

🇪🇸

Oviedo, Asturias, Spain

Kantonsspital St. Gallen

🇨🇭

St. Gallen, Sankt Gallen, Switzerland

Vancouver General Hospital

🇨🇦

Vancouver, British Columbia, Canada

Rabin Medical Center

🇮🇱

Petach Tikvah, Israel

Kelowna Respiratory and Allergy Clinic

🇨🇦

Kelowna, British Columbia, Canada

Universitair Ziekenhuis Leuven

🇧🇪

Leuven, Flemish Brabant, Belgium

Southmead Hospital

🇬🇧

Bristol, England, United Kingdom

Northern General Hospital

🇬🇧

Sheffield, England, United Kingdom

Southampton General Hospital

🇬🇧

Southampton, England, United Kingdom

University of Alabama at Birmingham

🇺🇸

Birmingham, Alabama, United States

National Jewish Health

🇺🇸

Denver, Colorado, United States

The Oregon Clinic, PC

🇺🇸

Portland, Oregon, United States

Saint Joseph's Hospital and Medical Center

🇺🇸

Phoenix, Arizona, United States

University of California San Francisco

🇺🇸

San Francisco, California, United States

Henry Ford Hospital

🇺🇸

Detroit, Michigan, United States

University of Minnesota Medical Center

🇺🇸

Minneapolis, Minnesota, United States

Vanderbilt University Medical Center

🇺🇸

Nashville, Tennessee, United States

University of Utah

🇺🇸

Salt Lake City, Utah, United States

Mayo Clinic

🇺🇸

Rochester, Minnesota, United States

Tampa General Hospital

🇺🇸

Tampa, Florida, United States

Froedtert Hospital and Medical College of Wisconsin

🇺🇸

Milwaukee, Wisconsin, United States

University Health Network

🇨🇦

Toronto, Ontario, Canada

Mayo Clinic Arizona

🇺🇸

Scottsdale, Arizona, United States

Southeastern Lung Care

🇺🇸

Decatur, Georgia, United States

Tufts University School of Medicine

🇺🇸

Boston, Massachusetts, United States

Sansum Clinic

🇺🇸

Santa Barbara, California, United States

Loess Hills Clinical Research Center

🇺🇸

Council Bluffs, Iowa, United States

Rush University Medical Center

🇺🇸

Chicago, Illinois, United States

Saint Luke's Midwest Pulmonary Consultants

🇺🇸

Kansas City, Missouri, United States

CardioPulmonary Associates

🇺🇸

Chesterfield, Missouri, United States

Washington University School of Medicine

🇺🇸

Saint Louis, Missouri, United States

Columbia University

🇺🇸

New York, New York, United States

Saint Vincents Hospital

🇦🇺

Darlinghurst, New South Wales, Australia

Prince Charles Hospital

🇦🇺

Chermside, Queensland, Australia

University of Rochester

🇺🇸

Rochester, New York, United States

Miami Valley Hospital

🇺🇸

Dayton, Ohio, United States

University of Pennsylvania

🇺🇸

Philadelphia, Pennsylvania, United States

University of Pittsburgh Presbyterian - Montefiore

🇺🇸

Pittsburgh, Pennsylvania, United States

Temple University Hospital, Temple Lung Center

🇺🇸

Philadelphia, Pennsylvania, United States

Concord Repatriation General Hospital

🇦🇺

Concord, New South Wales, Australia

Sir Charles Gairdner Hospital

🇦🇺

Nedlands, Western Australia, Australia

Providence Everett Medical Center

🇺🇸

Everett, Washington, United States

Royal Brisbane and Women's Hospital

🇦🇺

Herston, Queensland, Australia

Mater Adult Hospital

🇦🇺

Brisbane, Queensland, Australia

ULB Erasme

🇧🇪

Anderlecht, Brussels, Belgium

Royal Adelaide Hospital

🇦🇺

Adelaide, South Australia, Australia

Saint Joseph's Healthcare

🇨🇦

Hamilton, Ontario, Canada

University of British Columbia

🇨🇦

Vancouver, British Columbia, Canada

Centre Hospitalier de L'Université de Montréal Hôtel-Dieu

🇨🇦

Montreal, Quebec, Canada

Krajská nemocnice Liberec a.s.

🇨🇿

Liberec, Severocesky Kraj, Czechia

Hôpital Albert Calmette

🇫🇷

Lille cedex, Nord Pas-de-calais, France

Masarykova nemocnice v Ústí nad Labem o.z.

🇨🇿

Ústí nad Labem, Severocesky Kraj, Czechia

Hôpital Larrey, CHU de Toulouse, Service de Pneumologie

🇫🇷

Toulouse cedex 9, Midi-pyrenees, France

Centre Hospitalier Universitaire Hôpital Nord

🇫🇷

Marseille Cedex 20, Provence Alpes Cote D'azur, France

Fakultní nemocnice Brno

🇨🇿

Brno, Jihormoravsky Kraj, Czechia

Chaim Sheba Medical Center

🇮🇱

Tel Hashomer, Tel Aviv, Israel

Centre Hospitalier Régional et Universitaire - Hôpital Bretonneau

🇫🇷

Tours Cedex 9, Centre, France

Centre Hospitalier Universitaire Hôpital Avicenne

🇫🇷

Bobigny Cedex, Ile-de-france, France

Hôpital Louis Pradel

🇫🇷

Bron, Rhone-aples, France

Nemocnice Jihlava

🇨🇿

Jihlava, Jihormoravsky Kraj, Czechia

Thomayerova nemocnice

🇨🇿

Prague 4 - Krc, Czechia

Ospedale "G.B.Morgagni - L. Pierantoni"

🇮🇹

Forlì, Forli-cesena, Italy

San Giuseppe Hospital, Dept. of Internal Medicine

🇮🇹

Milano, Italy

Hôpital Arnaud de Villeneuve

🇫🇷

Montpellier cedex 5, Languedoc-roussillon, France

Fakultní Nemocnice Ostrava

🇨🇿

Ostrava - Poruba, Severomoravsky Kraj, Czechia

Centre Hospitalier Universitaire de Rennes, Hôpital Pontchaillou

🇫🇷

Rennes cedex 9, Bretagne, France

Fondazione PTV - Policlinico Tor Vergata

🇮🇹

Roma, Italy

Soon Chun Hyang University Hospital Bucheon

🇰🇷

Bucheon-si, Gyeonggi-do, Korea, Republic of

Hadassah-Hebrew University Medical Center

🇮🇱

Jerusalem, Israel

Meir Medical Center

🇮🇱

Kfar Saba, Israel

Policlinico Universitario di Catania

🇮🇹

Catania, Italy

Azienda Ospedaliero-Universitaria Policlinico di Modena

🇮🇹

Modena, Italy

Helios Klinikum Emil von Behring, Lungenklinik Heckeshorn

🇩🇪

Berlin, Germany

Soroka University Medical Center

🇮🇱

Beer Sheva, Beersheba, Israel

Tel Aviv Sourasky Medical Center

🇮🇱

Tel Aviv, Israel

Azienda Ospedaliera San Gerardo di Monza

🇮🇹

Monza, Monza E Brianza, Italy

Università degli studi Federico II di Napoli

🇮🇹

Napoli, Italy

Seoul National University Hospital

🇰🇷

Seoul, Korea, Republic of

Gachon University Gil Medical Center

🇰🇷

Incheon, Gyeonggi-Do, Korea, Republic of

Uniwersyteckie Centrum Kliniczne

🇵🇱

Gdansk, Pomorskie, Poland

Korea University Anam Hospital

🇰🇷

Seoul, Korea, Republic of

Asan Medical Center

🇰🇷

Seoul, Korea, Republic of

10 Wojskowy Szpital Kliniczny z Poliklinika SP ZOZ w Bydgoszczy

🇵🇱

Bydgoszcz, Kujawsko-pomorskie, Poland

Hospital de la Santa Creu i Sant Pau

🇪🇸

Barcelona, Spain

Hospital Universitario Virgen del Rocio

🇪🇸

Sevilla, Spain

Hospital Universitario La Princesa

🇪🇸

Madrid, Spain

Samodzielny Publiczny ZOZ, Uniwersytecki Szpital Kliniczny nr 1 im. Norberta Barlickiego

🇵🇱

Lódz, Lodzkie, Poland

Hospital Quirón Madrid

🇪🇸

Pozuelo de Alarcón, Madrid, Spain

Hospital Universitario Vall d'Hebron

🇪🇸

Barcelona, Spain

Centre Hospitalier Universitaire Vaudois Lausanne (CHUV)

🇨🇭

Lausanne, Vaud, Switzerland

Universitätsspital Basel

🇨🇭

Basel, Switzerland

Glenfield Hospital

🇬🇧

Leicester, England, United Kingdom

Nottingham City Hospital

🇬🇧

Nottingham, England, United Kingdom

Seoul National University Bundang Hospital

🇰🇷

Seongnam-si, Gyeonggi-do, Korea, Republic of

Ruhrlandklinik

🇩🇪

Mannheim, Baden-wuerttemberg, Germany

Universität Freiburg, Klinikum, Abt für Pneumologie

🇩🇪

Freiburg, Baden-wuerttemberg, Germany

Philipps-Universität und Universitätsklinikum Gießen und Marburg GmbH

🇩🇪

Giessen, Hessen, Germany

Klinikum Großhadern der Ludwig-Maximilians-Universität München

🇩🇪

München, Bayern, Germany

Medizinische Hochschule Hannover

🇩🇪

Hanover, Niedersachsen, Germany

Lungenfachklinik Immenhausen

🇩🇪

Immenhausen, Hessen, Germany

Fachkrankenhaus Coswig

🇩🇪

Coswig, Sachsen, Germany

Emory University Hospital

🇺🇸

Atlanta, Georgia, United States

Cleveland Clinic Florida

🇺🇸

Weston, Florida, United States

Loyola University Medical Center

🇺🇸

Maywood, Illinois, United States

Duke University Medical Center

🇺🇸

Durham, North Carolina, United States

North Shore University Hospital

🇺🇸

New Hyde Park, New York, United States

University of California Davis Medical Center

🇺🇸

Sacramento, California, United States

Northwestern University

🇺🇸

Chicago, Illinois, United States

Kentuckiana Pulmonary Associates

🇺🇸

Louisville, Kentucky, United States

Yale University School of Medicine

🇺🇸

New Haven, Connecticut, United States

University of Louisville

🇺🇸

Louisville, Kentucky, United States

David Geffen School of Medicine at University of California, Los Angeles

🇺🇸

Los Angeles, California, United States

Stanford University Medical Center

🇺🇸

Stanford, California, United States

Mayo Clinic Florida

🇺🇸

Jacksonville, Florida, United States

Bay Area Chest Physicians

🇺🇸

Clearwater, Florida, United States

University of Iowa Hospitals and Clinics

🇺🇸

Iowa City, Iowa, United States

Mount Sinai School of Medicine

🇺🇸

New York, New York, United States

Royal Prince Alfred Hospital

🇦🇺

Camperdown, New South Wales, Australia

Thomas Jefferson University Hospital

🇺🇸

Philadelphia, Pennsylvania, United States

Fakultní nemocnice Plzen

🇨🇿

Plzen, Zapadocesky Kraj, Czechia

Centre Hospitalier Universitaire Grenoble Hopital Michalon

🇫🇷

Grenoble Cedex 9, Rhone-Alpes, France

Hôpital Bichat-Claude Bernard

🇫🇷

Paris, Ile-de-france, France

Centre Hospitalier Universitaire de Nice-Hôpital Pasteur

🇫🇷

Nice CEDEX 1, Poitou-charentes, France

Thoraxklinik am Universitätsklinikum Heidelberg

🇩🇪

Heidelberg, Baden-wuerttemberg, Germany

Samsung Medical Center

🇰🇷

Seoul, Gyeonggi-do, Korea, Republic of

Istituto Mediterraneo Trapianti e Terapia Alta Specializzazione (ISMETT)

🇮🇹

Palermo, Italy

Azienda Ospedaliera Universitaria Senese Policlinico Le Scotte

🇮🇹

Siena, Italy

Birmingham Heartlands Hospital

🇬🇧

Birmingham, England, United Kingdom

Inova Fairfax Hospital

🇺🇸

Falls Church, Virginia, United States

University of California San Diego

🇺🇸

La Jolla, California, United States

Saint James's University Hospital

🇬🇧

Leeds, England, United Kingdom

Hospital Clinic de Barcelona

🇪🇸

Barcelona, Spain

Papworth Hospital

🇬🇧

Cambridge, England, United Kingdom

Royal Devon and Exeter Hospital

🇬🇧

Exeter, England, United Kingdom

Aintree University Hospitals NHS Foundation Trust

🇬🇧

Liverpool, England, United Kingdom

Churchill Hospital

🇬🇧

Oxford, England, United Kingdom

Royal Infirmary of Edinburgh

🇬🇧

Edinburgh, Scotland, United Kingdom

Glasgow Royal Infirmary

🇬🇧

Glasgow, Scotland, United Kingdom

Royal Brompton Hospital

🇬🇧

London, England, United Kingdom

Castle Hill Hospital

🇬🇧

Cottingham, England, United Kingdom

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